225 related articles for article (PubMed ID: 10444282)
21. Bone marrow mesenchymal cells for haemophilia A gene therapy using retroviral vectors with modified long-terminal repeats.
Van Damme A; Chuah MK; Dell'accio F; De Bari C; Luyten F; Collen D; VandenDriessche T
Haemophilia; 2003 Jan; 9(1):94-103. PubMed ID: 12558785
[TBL] [Abstract][Full Text] [Related]
22. Heterogeneity of the immune response to adenovirus-mediated factor VIII gene therapy in different inbred hemophilic mouse strains.
Rawle FE; Shi CX; Brown B; McKinven A; Tinlin S; Graham FL; Hough C; Lillicrap D
J Gene Med; 2004 Dec; 6(12):1358-68. PubMed ID: 15493040
[TBL] [Abstract][Full Text] [Related]
23. Helper-dependent adenoviral gene therapy mediates long-term correction of the clotting defect in the canine hemophilia A model.
McCORMACK WM; Seiler MP; Bertin TK; Ubhayakar K; Palmer DJ; Ng P; Nichols TC; Lee B
J Thromb Haemost; 2006 Jun; 4(6):1218-1225. PubMed ID: 16706963
[TBL] [Abstract][Full Text] [Related]
24. Characteristics of Minimally Oversized Adeno-Associated Virus Vectors Encoding Human Factor VIII Generated Using Producer Cell Lines and Triple Transfection.
Nambiar B; Cornell Sookdeo C; Berthelette P; Jackson R; Piraino S; Burnham B; Nass S; Souza D; O'Riordan CR; Vincent KA; Cheng SH; Armentano D; Kyostio-Moore S
Hum Gene Ther Methods; 2017 Feb; 28(1):23-38. PubMed ID: 28166648
[TBL] [Abstract][Full Text] [Related]
25. Development and application of a minimal-adenoviral vector system for gene therapy of hemophilia A.
Zhang WW; Josephs SF; Zhou J; Fang X; Alemany R; Balagué C; Dai Y; Ayares D; Prokopenko E; Lou YC; Sethi E; Hubert-Leslie D; Kennedy M; Ruiz L; Rockow-Magnone S
Thromb Haemost; 1999 Aug; 82(2):562-71. PubMed ID: 10605752
[TBL] [Abstract][Full Text] [Related]
26. Haemophilia A gene therapy.
Connelly S; Kaleko M
Haemophilia; 1998 Jul; 4(4):380-8. PubMed ID: 9873758
[TBL] [Abstract][Full Text] [Related]
27. Total correction of hemophilia A mice with canine FVIII using an AAV 8 serotype.
Sarkar R; Tetreault R; Gao G; Wang L; Bell P; Chandler R; Wilson JM; Kazazian HH
Blood; 2004 Feb; 103(4):1253-60. PubMed ID: 14551134
[TBL] [Abstract][Full Text] [Related]
28. Phenotypic correction of a mouse model of hemophilia A using AAV2 vectors encoding the heavy and light chains of FVIII.
Scallan CD; Liu T; Parker AE; Patarroyo-White SL; Chen H; Jiang H; Vargas J; Nagy D; Powell SK; Wright JF; Sarkar R; Kazazian HH; McClelland A; Couto LB
Blood; 2003 Dec; 102(12):3919-26. PubMed ID: 12893764
[TBL] [Abstract][Full Text] [Related]
29. Gene Therapy with BMN 270 Results in Therapeutic Levels of FVIII in Mice and Primates and Normalization of Bleeding in Hemophilic Mice.
Bunting S; Zhang L; Xie L; Bullens S; Mahimkar R; Fong S; Sandza K; Harmon D; Yates B; Handyside B; Sihn CR; Galicia N; Tsuruda L; O'Neill CA; Bagri A; Colosi P; Long S; Vehar G; Carter B
Mol Ther; 2018 Feb; 26(2):496-509. PubMed ID: 29292164
[TBL] [Abstract][Full Text] [Related]
30. Adenoviral vector-mediated expression of physiologic levels of human factor VIII in nonhuman primates.
Brann T; Kayda D; Lyons RM; Shirley P; Roy S; Kaleko M; Smith T
Hum Gene Ther; 1999 Dec; 10(18):2999-3011. PubMed ID: 10609660
[TBL] [Abstract][Full Text] [Related]
31. Complete correction of hemophilia A with adeno-associated viral vectors containing a full-size expression cassette.
Lu H; Chen L; Wang J; Huack B; Sarkar R; Zhou S; Xu R; Ding Q; Wang X; Wang H; Xiao W
Hum Gene Ther; 2008 Jun; 19(6):648-54. PubMed ID: 18500941
[TBL] [Abstract][Full Text] [Related]
32. Sustained phenotypic correction of murine hemophilia A by in vivo gene therapy.
Connelly S; Andrews JL; Gallo AM; Kayda DB; Qian J; Hoyer L; Kadan MJ; Gorziglia MI; Trapnell BC; McClelland A; Kaleko M
Blood; 1998 May; 91(9):3273-81. PubMed ID: 9558383
[TBL] [Abstract][Full Text] [Related]
33. High-level tissue-specific expression of functional human factor VIII in mice.
Connelly S; Gardner JM; McClelland A; Kaleko M
Hum Gene Ther; 1996 Jan; 7(2):183-95. PubMed ID: 8788169
[TBL] [Abstract][Full Text] [Related]
34. Long-term efficacy of adeno-associated virus serotypes 8 and 9 in hemophilia a dogs and mice.
Sarkar R; Mucci M; Addya S; Tetreault R; Bellinger DA; Nichols TC; Kazazian HH
Hum Gene Ther; 2006 Apr; 17(4):427-39. PubMed ID: 16610930
[TBL] [Abstract][Full Text] [Related]
35. Multiyear therapeutic benefit of AAV serotypes 2, 6, and 8 delivering factor VIII to hemophilia A mice and dogs.
Jiang H; Lillicrap D; Patarroyo-White S; Liu T; Qian X; Scallan CD; Powell S; Keller T; McMurray M; Labelle A; Nagy D; Vargas JA; Zhou S; Couto LB; Pierce GF
Blood; 2006 Jul; 108(1):107-15. PubMed ID: 16522813
[TBL] [Abstract][Full Text] [Related]
36. Codon optimization of human factor VIII cDNAs leads to high-level expression.
Ward NJ; Buckley SM; Waddington SN; Vandendriessche T; Chuah MK; Nathwani AC; McIntosh J; Tuddenham EG; Kinnon C; Thrasher AJ; McVey JH
Blood; 2011 Jan; 117(3):798-807. PubMed ID: 21041718
[TBL] [Abstract][Full Text] [Related]
37. Long-term expression of human coagulation factor VIII and correction of hemophilia A after in vivo retroviral gene transfer in factor VIII-deficient mice.
VandenDriessche T; Vanslembrouck V; Goovaerts I; Zwinnen H; Vanderhaeghen ML; Collen D; Chuah MK
Proc Natl Acad Sci U S A; 1999 Aug; 96(18):10379-84. PubMed ID: 10468616
[TBL] [Abstract][Full Text] [Related]
38. Expression of therapeutic levels of factor VIII in hemophilia A mice using a novel adeno/adeno-associated hybrid virus.
Gnatenko DV; Wu Y; Jesty J; Damon AL; Hearing P; Bahou WF
Thromb Haemost; 2004 Aug; 92(2):317-27. PubMed ID: 15269828
[TBL] [Abstract][Full Text] [Related]
39. Phenotype correction of hemophilia A mice with adeno-associated virus vectors carrying the B domain-deleted canine factor VIII gene.
Ishiwata A; Mimuro J; Kashiwakura Y; Niimura M; Takano K; Ohmori T; Madoiwa S; Mizukami H; Okada T; Naka H; Yoshioka A; Ozawa K; Sakata Y
Thromb Res; 2006; 118(5):627-35. PubMed ID: 16371232
[TBL] [Abstract][Full Text] [Related]
40. Ex vivo gene therapy for hemophilia A that enhances safe delivery and sustained in vivo factor VIII expression from lentivirally engineered endothelial progenitors.
Matsui H; Shibata M; Brown B; Labelle A; Hegadorn C; Andrews C; Hebbel RP; Galipeau J; Hough C; Lillicrap D
Stem Cells; 2007 Oct; 25(10):2660-9. PubMed ID: 17615271
[TBL] [Abstract][Full Text] [Related]
[Previous] [Next] [New Search]