These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.
3. Recent Advances in Gene Therapy for Hemophilia: Projecting the Perspectives. Chernyi N; Gavrilova D; Saruhanyan M; Oloruntimehin ES; Karabelsky A; Bezsonov E; Malogolovkin A Biomolecules; 2024 Jul; 14(7):. PubMed ID: 39062568 [TBL] [Abstract][Full Text] [Related]
4. Gene therapy for hemophilia: are viral vectors really feasible? Walsh C J Thromb Haemost; 2003 Feb; 1(2):218-9. PubMed ID: 12871491 [No Abstract] [Full Text] [Related]
5. Hemophilia A and hemophilia B: focus on arthropathy and variables affecting bleeding severity and prophylaxis. Escobar M; Sallah S J Thromb Haemost; 2013 Aug; 11(8):1449-53. PubMed ID: 23763284 [TBL] [Abstract][Full Text] [Related]
6. [Advances in AAV-CRISPR/Cas9-Mediated Hemophilia A Gene Therapy --Review]. Fang S; Wang G; Yang LH Zhongguo Shi Yan Xue Ye Xue Za Zhi; 2023 Dec; 31(6):1890-1893. PubMed ID: 38071078 [TBL] [Abstract][Full Text] [Related]
9. Advances in the treatment of bleeding disorders. Peyvandi F; Garagiola I; Biguzzi E J Thromb Haemost; 2016 Nov; 14(11):2095-2106. PubMed ID: 27590165 [TBL] [Abstract][Full Text] [Related]
10. Canine models of inherited bleeding disorders in the development of coagulation assays, novel protein replacement and gene therapies. Nichols TC; Hough C; Agersø H; Ezban M; Lillicrap D J Thromb Haemost; 2016 May; 14(5):894-905. PubMed ID: 26924758 [TBL] [Abstract][Full Text] [Related]
11. Gene therapy for immune tolerance induction in hemophilia with inhibitors. Arruda VR; Samelson-Jones BJ J Thromb Haemost; 2016 Jun; 14(6):1121-34. PubMed ID: 27061380 [TBL] [Abstract][Full Text] [Related]
13. Gene transfer for hemophilia: can therapeutic efficacy in large animals be safely translated to patients? High K J Thromb Haemost; 2005 Aug; 3(8):1682-91. PubMed ID: 16102034 [TBL] [Abstract][Full Text] [Related]
14. Gene therapy for hemophilia, a clinical viewpoint. Chou SC; Hsu YC; Lin SW J Formos Med Assoc; 2023 Nov; 122(11):1101-1110. PubMed ID: 37210312 [TBL] [Abstract][Full Text] [Related]
15. Evaluating Gene Therapy as a Potential Paradigm Shift in Treating Severe Hemophilia. Thornburg CD; Simmons DH; von Drygalski A BioDrugs; 2023 Sep; 37(5):595-606. PubMed ID: 37490225 [TBL] [Abstract][Full Text] [Related]
17. Sensitivity of whole blood clotting time and activated partial thromboplastin time for factor IX: relevance to gene therapy and determination of post-transfusion elimination time of canine factor IX in hemophilia B dogs. Nichols TC; Franck HW; Franck CT; De Friess N; Raymer RA; Merricks EP J Thromb Haemost; 2012 Mar; 10(3):474-6. PubMed ID: 22482117 [No Abstract] [Full Text] [Related]
18. Activated factor X targeted stored in platelets as an effective gene therapy strategy for both hemophilia A and B. Wang D; Shao X; Wang Q; Pan X; Dai Y; Yao S; Yin T; Wang Z; Zhu J; Xi X; Chen Z; Chen S; Zhang G Clin Transl Med; 2021 Mar; 11(3):e375. PubMed ID: 33783994 [TBL] [Abstract][Full Text] [Related]
19. The complex, confusing and poorly understood immune responses to AAV-mediated gene transfer in haemophilia-Is more or less immunosuppression required? Tuddenham EGD; Foster GR J Viral Hepat; 2024 Apr; 31 Suppl 1():21-25. PubMed ID: 38606938 [TBL] [Abstract][Full Text] [Related]
20. [Recent advances in the replacement therapy for Hemophilia]. Hou PX; Yang RC Zhonghua Xue Ye Xue Za Zhi; 2023 Dec; 44(12):1052-1056. PubMed ID: 38503535 [No Abstract] [Full Text] [Related] [Next] [New Search]