BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

1005 related articles for article (PubMed ID: 10784449)

  • 1. Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease.
    Cavazzana-Calvo M; Hacein-Bey S; de Saint Basile G; Gross F; Yvon E; Nusbaum P; Selz F; Hue C; Certain S; Casanova JL; Bousso P; Deist FL; Fischer A
    Science; 2000 Apr; 288(5466):669-72. PubMed ID: 10784449
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Treatment of an infant with X-linked severe combined immunodeficiency (SCID-X1) by gene therapy in Australia.
    Ginn SL; Curtin JA; Kramer B; Smyth CM; Wong M; Kakakios A; McCowage GB; Watson D; Alexander SI; Latham M; Cunningham SC; Zheng M; Hobson L; Rowe PB; Fischer A; Cavazzana-Calvo M; Hacein-Bey-Abina S; Alexander IE
    Med J Aust; 2005 May; 182(9):458-63. PubMed ID: 15865589
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Sustained correction of X-linked severe combined immunodeficiency by ex vivo gene therapy.
    Hacein-Bey-Abina S; Le Deist F; Carlier F; Bouneaud C; Hue C; De Villartay JP; Thrasher AJ; Wulffraat N; Sorensen R; Dupuis-Girod S; Fischer A; Davies EG; Kuis W; Leiva L; Cavazzana-Calvo M
    N Engl J Med; 2002 Apr; 346(16):1185-93. PubMed ID: 11961146
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Gene therapy of X-linked severe combined immunodeficiency by use of a pseudotyped gammaretroviral vector.
    Gaspar HB; Parsley KL; Howe S; King D; Gilmour KC; Sinclair J; Brouns G; Schmidt M; Von Kalle C; Barington T; Jakobsen MA; Christensen HO; Al Ghonaium A; White HN; Smith JL; Levinsky RJ; Ali RR; Kinnon C; Thrasher AJ
    Lancet; 2004 Dec 18-31; 364(9452):2181-7. PubMed ID: 15610804
    [TBL] [Abstract][Full Text] [Related]  

  • 5. [Gene therapy of X-linked severe combined immunologic deficiency (SCID-X1)].
    Hacein-Bey S; Gross F; Nusbaum P; Yvon E; Fischer A; Cavazzana-Calvo M
    Pathol Biol (Paris); 2001 Feb; 49(1):57-66. PubMed ID: 11265225
    [TBL] [Abstract][Full Text] [Related]  

  • 6. gammac gene transfer in the presence of stem cell factor, FLT-3L, interleukin-7 (IL-7), IL-1, and IL-15 cytokines restores T-cell differentiation from gammac(-) X-linked severe combined immunodeficiency hematopoietic progenitor cells in murine fetal thymic organ cultures.
    Hacein-Bey S; Basile GD; Lemerle J; Fischer A; Cavazzana-Calvo M
    Blood; 1998 Dec; 92(11):4090-7. PubMed ID: 9834214
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Lentiviral Gene Therapy Combined with Low-Dose Busulfan in Infants with SCID-X1.
    Mamcarz E; Zhou S; Lockey T; Abdelsamed H; Cross SJ; Kang G; Ma Z; Condori J; Dowdy J; Triplett B; Li C; Maron G; Aldave Becerra JC; Church JA; Dokmeci E; Love JT; da Matta Ain AC; van der Watt H; Tang X; Janssen W; Ryu BY; De Ravin SS; Weiss MJ; Youngblood B; Long-Boyle JR; Gottschalk S; Meagher MM; Malech HL; Puck JM; Cowan MJ; Sorrentino BP
    N Engl J Med; 2019 Apr; 380(16):1525-1534. PubMed ID: 30995372
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Efficacy of gene therapy for X-linked severe combined immunodeficiency.
    Hacein-Bey-Abina S; Hauer J; Lim A; Picard C; Wang GP; Berry CC; Martinache C; Rieux-Laucat F; Latour S; Belohradsky BH; Leiva L; Sorensen R; Debré M; Casanova JL; Blanche S; Durandy A; Bushman FD; Fischer A; Cavazzana-Calvo M
    N Engl J Med; 2010 Jul; 363(4):355-64. PubMed ID: 20660403
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Gene therapy. The best of times, the worst of times.
    Anderson WF
    Science; 2000 Apr; 288(5466):627-9. PubMed ID: 10799000
    [No Abstract]   [Full Text] [Related]  

  • 10. A modified γ-retrovirus vector for X-linked severe combined immunodeficiency.
    Hacein-Bey-Abina S; Pai SY; Gaspar HB; Armant M; Berry CC; Blanche S; Bleesing J; Blondeau J; de Boer H; Buckland KF; Caccavelli L; Cros G; De Oliveira S; Fernández KS; Guo D; Harris CE; Hopkins G; Lehmann LE; Lim A; London WB; van der Loo JC; Malani N; Male F; Malik P; Marinovic MA; McNicol AM; Moshous D; Neven B; Oleastro M; Picard C; Ritz J; Rivat C; Schambach A; Shaw KL; Sherman EA; Silberstein LE; Six E; Touzot F; Tsytsykova A; Xu-Bayford J; Baum C; Bushman FD; Fischer A; Kohn DB; Filipovich AH; Notarangelo LD; Cavazzana M; Williams DA; Thrasher AJ
    N Engl J Med; 2014 Oct; 371(15):1407-17. PubMed ID: 25295500
    [TBL] [Abstract][Full Text] [Related]  

  • 11. A novel splice-site mutation in the common gamma chain (gammac) gene IL2RG results in X-linked severe combined immunodeficiency with an atypical NK+ phenotype.
    Ginn SL; Smyth C; Wong M; Bennetts B; Rowe PB; Alexander IE
    Hum Mutat; 2004 May; 23(5):522-3. PubMed ID: 15108287
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Gene therapy for severe combined immunodeficiencies.
    Gaspar HB; Thrasher AJ
    Expert Opin Biol Ther; 2005 Sep; 5(9):1175-82. PubMed ID: 16120048
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Role of interleukin-2 (IL-2), IL-7, and IL-15 in natural killer cell differentiation from cord blood hematopoietic progenitor cells and from gamma c transduced severe combined immunodeficiency X1 bone marrow cells.
    Cavazzana-Calvo M; Hacein-Bey S; de Saint Basile G; De Coene C; Selz F; Le Deist F; Fischer A
    Blood; 1996 Nov; 88(10):3901-9. PubMed ID: 8916956
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Retroviral transduction of IL2RG into CD34(+) cells from X-linked severe combined immunodeficiency patients permits human T- and B-cell development in sheep chimeras.
    Tsai EJ; Malech HL; Kirby MR; Hsu AP; Seidel NE; Porada CD; Zanjani ED; Bodine DM; Puck JM
    Blood; 2002 Jul; 100(1):72-9. PubMed ID: 12070011
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Gene therapy of X-linked severe combined immunodeficiency.
    Hacein-Bey-Abina S; Fischer A; Cavazzana-Calvo M
    Int J Hematol; 2002 Nov; 76(4):295-8. PubMed ID: 12463590
    [TBL] [Abstract][Full Text] [Related]  

  • 16. A self-inactivating lentiviral vector for SCID-X1 gene therapy that does not activate LMO2 expression in human T cells.
    Zhou S; Mody D; DeRavin SS; Hauer J; Lu T; Ma Z; Hacein-Bey Abina S; Gray JT; Greene MR; Cavazzana-Calvo M; Malech HL; Sorrentino BP
    Blood; 2010 Aug; 116(6):900-8. PubMed ID: 20457870
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Gene therapy model of X-linked severe combined immunodeficiency using a modified foamy virus vector.
    Horino S; Uchiyama T; So T; Nagashima H; Sun SL; Sato M; Asao A; Haji Y; Sasahara Y; Candotti F; Tsuchiya S; Kure S; Sugamura K; Ishii N
    PLoS One; 2013; 8(8):e71594. PubMed ID: 23990961
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Lentiviral hematopoietic stem cell gene therapy for X-linked severe combined immunodeficiency.
    De Ravin SS; Wu X; Moir S; Anaya-O'Brien S; Kwatemaa N; Littel P; Theobald N; Choi U; Su L; Marquesen M; Hilligoss D; Lee J; Buckner CM; Zarember KA; O'Connor G; McVicar D; Kuhns D; Throm RE; Zhou S; Notarangelo LD; Hanson IC; Cowan MJ; Kang E; Hadigan C; Meagher M; Gray JT; Sorrentino BP; Malech HL; Kardava L
    Sci Transl Med; 2016 Apr; 8(335):335ra57. PubMed ID: 27099176
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Transplantation of X-linked severe combined immunodeficient dogs with CD34+ bone marrow cells.
    Hartnett BJ; Yao D; Suter SE; Ellinwood NM; Henthorn PS; Moore PE; McSweeney PA; Nash RA; Brown JD; Weinberg KI; Felsburg PJ
    Biol Blood Marrow Transplant; 2002; 8(4):188-97. PubMed ID: 12014808
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Lentivirus Mediated Correction of Artemis-Deficient Severe Combined Immunodeficiency.
    Punwani D; Kawahara M; Yu J; Sanford U; Roy S; Patel K; Carbonaro DA; Karlen AD; Khan S; Cornetta K; Rothe M; Schambach A; Kohn DB; Malech HL; McIvor RS; Puck JM; Cowan MJ
    Hum Gene Ther; 2017 Jan; 28(1):112-124. PubMed ID: 27611239
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 51.