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6. Insights into the Pathogenesis and Treatment of Krabbe Disease. Bongarzone ER; Escolar ML; Gray SJ; Kafri T; Vite CH; Sands MS Pediatr Endocrinol Rev; 2016 Jun; 13 Suppl 1():689-96. PubMed ID: 27491217 [TBL] [Abstract][Full Text] [Related]
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9. Generation of a mouse with low galactocerebrosidase activity by gene targeting: a new model of globoid cell leukodystrophy (Krabbe disease). Luzi P; Rafi MA; Zaka M; Curtis M; Vanier MT; Wenger DA Mol Genet Metab; 2001 Jul; 73(3):211-23. PubMed ID: 11461188 [TBL] [Abstract][Full Text] [Related]
10. Krabbe disease: New hope for an old disease. Bradbury AM; Bongarzone ER; Sands MS Neurosci Lett; 2021 May; 752():135841. PubMed ID: 33766733 [TBL] [Abstract][Full Text] [Related]
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13. Cloning of the canine GALC cDNA and identification of the mutation causing globoid cell leukodystrophy in West Highland White and Cairn terriers. Victoria T; Rafi MA; Wenger DA Genomics; 1996 May; 33(3):457-62. PubMed ID: 8661004 [TBL] [Abstract][Full Text] [Related]
14. Murine, canine and non-human primate models of Krabbe disease. Wenger DA Mol Med Today; 2000 Nov; 6(11):449-51. PubMed ID: 11074371 [TBL] [Abstract][Full Text] [Related]
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19. Retroviral vector-mediated transfer of the galactocerebrosidase (GALC) cDNA leads to overexpression and transfer of GALC activity to neighboring cells. Rafi MA; Fugaro J; Amini S; Luzi P; de Gala G; Victoria T; Dubell C; Shahinfar M; Wenger DA Biochem Mol Med; 1996 Aug; 58(2):142-50. PubMed ID: 8812733 [TBL] [Abstract][Full Text] [Related]
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