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2. Severe combined immunodeficiencies. Fischer A Immunodefic Rev; 1992; 3(2):83-100. PubMed ID: 1554500 [TBL] [Abstract][Full Text] [Related]
3. Treatment of patients with severe combined immunodeficiency due to adenosine deaminase (ADA) deficiency by autologous transplantation of genetically modified bone marrow cells. Hoogerbrugge PM; Vossen JM; v Beusechem VW; Valerio D Hum Gene Ther; 1992 Oct; 3(5):553-8. PubMed ID: 1420454 [No Abstract] [Full Text] [Related]
4. Maternal T-cell engraftment impedes with diagnosis of a SCID-ADA patient. Lanfranchi A; Lougaris V; Notarangelo LD; Soncini E; Comini M; Beghin A; Bolda F; Montanelli A; Imberti L; Porta F Clin Immunol; 2018 Aug; 193():118-120. PubMed ID: 29355610 [TBL] [Abstract][Full Text] [Related]
5. A new chance for SCID gene therapy. Bordignon C Nat Med; 1998 Jan; 4(1):19-20. PubMed ID: 9427599 [No Abstract] [Full Text] [Related]
6. LMO2 and gene therapy for severe combined immunodeficiency. Stone BD N Engl J Med; 2004 Jun; 350(24):2526-7; author reply 2526-7. PubMed ID: 15195349 [No Abstract] [Full Text] [Related]
8. Amendment to Clinical Research Project. Project 90-C-195. April 1, 1993. Treatment of severe combined immunodeficiency disease (SCID) due to adenosine deaminase deficiency with autologous lymphocytes transduced with a human ADA gene. Dunbar C; Chang L; Mullen C; Ramsey WJ; Carter C; Kohn D; Parkman R; Lenarsky C; Weinberg K; Wara D; Culver KW; Anderson WF; Leitman S; Fleisher T; Klein H; Shearer G; Clerici M; McGarrity G; Bastian J; Hershfield MS Hum Gene Ther; 1999 Feb; 10(3):477-88. PubMed ID: 10048399 [No Abstract] [Full Text] [Related]
9. Advances in the understanding and treatment of human severe combined immunodeficiency. Buckley RH Immunol Res; 2000; 22(2-3):237-51. PubMed ID: 11339359 [TBL] [Abstract][Full Text] [Related]
10. Severe immunodeficiencies: bone marrow transplantation or gene therapy? Mariani SM MedGenMed; 2003 Jun; 5(2):19. PubMed ID: 14603118 [No Abstract] [Full Text] [Related]
11. Evolving Gene Therapy in Primary Immunodeficiency. Thrasher AJ; Williams DA Mol Ther; 2017 May; 25(5):1132-1141. PubMed ID: 28366768 [TBL] [Abstract][Full Text] [Related]
12. Preclinical demonstration of lentiviral vector-mediated correction of immunological and metabolic abnormalities in models of adenosine deaminase deficiency. Carbonaro DA; Zhang L; Jin X; Montiel-Equihua C; Geiger S; Carmo M; Cooper A; Fairbanks L; Kaufman ML; Sebire NJ; Hollis RP; Blundell MP; Senadheera S; Fu PY; Sahaghian A; Chan RY; Wang X; Cornetta K; Thrasher AJ; Kohn DB; Gaspar HB Mol Ther; 2014 Mar; 22(3):607-622. PubMed ID: 24256635 [TBL] [Abstract][Full Text] [Related]
13. Efficacy of gene therapy for SCID is being confirmed. Cavazzana-Calvo M; Fischer A Lancet; 2004 Dec 18-31; 364(9452):2155-6. PubMed ID: 15610783 [No Abstract] [Full Text] [Related]
14. Gene therapy of primary T cell immunodeficiencies. Fischer A; Hacein-Bey-Abina S; Cavazzana-Calvo M Gene; 2013 Aug; 525(2):170-3. PubMed ID: 23583799 [TBL] [Abstract][Full Text] [Related]
15. The different extent of B and T cell immune reconstitution after hematopoietic stem cell transplantation and enzyme replacement therapies in SCID patients with adenosine deaminase deficiency. Serana F; Sottini A; Chiarini M; Zanotti C; Ghidini C; Lanfranchi A; Notarangelo LD; Caimi L; Imberti L J Immunol; 2010 Dec; 185(12):7713-22. PubMed ID: 21057082 [TBL] [Abstract][Full Text] [Related]
16. Influence of severe combined immunodeficiency phenotype on the outcome of HLA non-identical, T-cell-depleted bone marrow transplantation: a retrospective European survey from the European group for bone marrow transplantation and the european society for immunodeficiency. Bertrand Y; Landais P; Friedrich W; Gerritsen B; Morgan G; Fasth A; Cavazzana-Calvo M; Porta F; Cant A; Espanol T; Müller S; Veys P; Vossen J; Haddad E; Fischer A J Pediatr; 1999 Jun; 134(6):740-8. PubMed ID: 10356144 [TBL] [Abstract][Full Text] [Related]
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