277 related articles for article (PubMed ID: 11273777)
1. Intracranial injection of recombinant adeno-associated virus improves cognitive function in a murine model of mucopolysaccharidosis type VII.
Frisella WA; O'Connor LH; Vogler CA; Roberts M; Walkley S; Levy B; Daly TM; Sands MS
Mol Ther; 2001 Mar; 3(3):351-8. PubMed ID: 11273777
[TBL] [Abstract][Full Text] [Related]
2. Brain transplantation of genetically modified bone marrow stromal cells corrects CNS pathology and cognitive function in MPS VII mice.
Sakurai K; Iizuka S; Shen JS; Meng XL; Mori T; Umezawa A; Ohashi T; Eto Y
Gene Ther; 2004 Oct; 11(19):1475-81. PubMed ID: 15295619
[TBL] [Abstract][Full Text] [Related]
3. Prevention of systemic clinical disease in MPS VII mice following AAV-mediated neonatal gene transfer.
Daly TM; Ohlemiller KK; Roberts MS; Vogler CA; Sands MS
Gene Ther; 2001 Sep; 8(17):1291-8. PubMed ID: 11571565
[TBL] [Abstract][Full Text] [Related]
4. Treatment of lysosomal storage disease in MPS VII mice using a recombinant adeno-associated virus.
Watson GL; Sayles JN; Chen C; Elliger SS; Elliger CA; Raju NR; Kurtzman GJ; Podsakoff GM
Gene Ther; 1998 Dec; 5(12):1642-9. PubMed ID: 10023443
[TBL] [Abstract][Full Text] [Related]
5. Significantly increased expression of beta-glucuronidase in the central nervous system of mucopolysaccharidosis type VII mice from the latency-associated transcript promoter in a nonpathogenic herpes simplex virus type 1 vector.
Zhu J; Kang W; Wolfe JH; Fraser NW
Mol Ther; 2000 Jul; 2(1):82-94. PubMed ID: 10899831
[TBL] [Abstract][Full Text] [Related]
6. Long-term and significant correction of brain lesions in adult mucopolysaccharidosis type VII mice using recombinant AAV vectors.
Bosch A; Perret E; Desmaris N; Heard JM
Mol Ther; 2000 Jan; 1(1):63-70. PubMed ID: 10933913
[TBL] [Abstract][Full Text] [Related]
7. High level expression and export of beta-glucuronidase from murine mucopolysaccharidosis VII cells corrected by a double-copy retrovirus vector.
Wolfe JH; Kyle JW; Sands MS; Sly WS; Markowitz DG; Parente MK
Gene Ther; 1995 Jan; 2(1):70-8. PubMed ID: 7712336
[TBL] [Abstract][Full Text] [Related]
8. Sustained production of beta-glucuronidase from localized sites after AAV vector gene transfer results in widespread distribution of enzyme and reversal of lysosomal storage lesions in a large volume of brain in mucopolysaccharidosis VII mice.
Skorupa AF; Fisher KJ; Wilson JM; Parente MK; Wolfe JH
Exp Neurol; 1999 Nov; 160(1):17-27. PubMed ID: 10630187
[TBL] [Abstract][Full Text] [Related]
9. Neonatal intramuscular injection with recombinant adeno-associated virus results in prolonged beta-glucuronidase expression in situ and correction of liver pathology in mucopolysaccharidosis type VII mice.
Daly TM; Okuyama T; Vogler C; Haskins ME; Muzyczka N; Sands MS
Hum Gene Ther; 1999 Jan; 10(1):85-94. PubMed ID: 10022533
[TBL] [Abstract][Full Text] [Related]
10. Engraftment of genetically engineered amniotic epithelial cells corrects lysosomal storage in multiple areas of the brain in mucopolysaccharidosis type VII mice.
Kosuga M; Sasaki K; Tanabe A; Li XK; Okawa H; Ogino I; Okuda O; Arai H; Sakuragawa N; Kamata Y; Azuma N; Suzuki S; Yamada M; Okuyama T
Mol Ther; 2001 Feb; 3(2):139-48. PubMed ID: 11237670
[TBL] [Abstract][Full Text] [Related]
11. Systemic hyperosmolality improves beta-glucuronidase distribution and pathology in murine MPS VII brain following intraventricular gene transfer.
Ghodsi A; Stein C; Derksen T; Martins I; Anderson RD; Davidson BL
Exp Neurol; 1999 Nov; 160(1):109-16. PubMed ID: 10630195
[TBL] [Abstract][Full Text] [Related]
12. Cross-correction of beta-glucuronidase deficiency by retroviral vector-mediated gene transfer.
Taylor RM; Wolfe JH
Exp Cell Res; 1994 Oct; 214(2):606-13. PubMed ID: 7925654
[TBL] [Abstract][Full Text] [Related]
13. Histopathological and behavioral improvement of murine mucopolysaccharidosis type VII by intracerebral transplantation of neural stem cells.
Fukuhara Y; Li XK; Kitazawa Y; Inagaki M; Matsuoka K; Kosuga M; Kosaki R; Shimazaki T; Endo H; Umezawa A; Okano H; Takahashi T; Okuyama T
Mol Ther; 2006 Mar; 13(3):548-55. PubMed ID: 16316785
[TBL] [Abstract][Full Text] [Related]
14. Widespread biochemical correction of murine mucopolysaccharidosis type VII pathology by liver hydrodynamic plasmid delivery.
Richard M; Arfi A; Seguin J; Gandolphe C; Scherman D
Gene Ther; 2009 Jun; 16(6):746-56. PubMed ID: 19357715
[TBL] [Abstract][Full Text] [Related]
15. In vivo treatment of hemophilia A and mucopolysaccharidosis type VII using nonprimate lentiviral vectors.
Stein CS; Kang Y; Sauter SL; Townsend K; Staber P; Derksen TA; Martins I; Qian J; Davidson BL; McCray PB
Mol Ther; 2001 Jun; 3(6):850-6. PubMed ID: 11407898
[TBL] [Abstract][Full Text] [Related]
16. Accumulation of abnormal amounts of glycosaminoglycans in murine mucopolysaccharidosis type VII neural progenitor cells does not alter the growth rate or efficiency of differentiation into neurons.
Heuer GG; Skorupa AF; Prasad Alur RK; Jiang K; Wolfe JH
Mol Cell Neurosci; 2001 Jan; 17(1):167-78. PubMed ID: 11161477
[TBL] [Abstract][Full Text] [Related]
17. Genetic correction of the fetal brain increases the lifespan of mice with the severe multisystemic disease mucopolysaccharidosis type VII.
Karolewski BA; Wolfe JH
Mol Ther; 2006 Jul; 14(1):14-24. PubMed ID: 16624622
[TBL] [Abstract][Full Text] [Related]
18. Long-term normalization in the central nervous system, ocular manifestations, and skeletal deformities by a single systemic adenovirus injection into neonatal mice with mucopolysaccharidosis VII.
Kamata Y; Tanabe A; Kanaji A; Kosuga M; Fukuhara Y; Li XK; Suzuki S; Yamada M; Azuma N; Okuyama T
Gene Ther; 2003 Mar; 10(5):406-14. PubMed ID: 12601395
[TBL] [Abstract][Full Text] [Related]
19. Elimination of lysosomal storage in brains of MPS VII mice treated by intrathecal administration of an adeno-associated virus vector.
Elliger SS; Elliger CA; Aguilar CP; Raju NR; Watson GL
Gene Ther; 1999 Jun; 6(6):1175-8. PubMed ID: 10455422
[TBL] [Abstract][Full Text] [Related]
20. Brain transplantation of genetically engineered human neural stem cells globally corrects brain lesions in the mucopolysaccharidosis type VII mouse.
Meng XL; Shen JS; Ohashi T; Maeda H; Kim SU; Eto Y
J Neurosci Res; 2003 Oct; 74(2):266-77. PubMed ID: 14515356
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]
