284 related articles for article (PubMed ID: 11828387)
1. Sustained delivery of therapeutic concentrations of human clotting factor IX--a comparison of adenoviral and AAV vectors administered in utero.
Schneider H; Mühle C; Douar AM; Waddington S; Jiang QJ; von der Mark K; Coutelle C; Rascher W
J Gene Med; 2002; 4(1):46-53. PubMed ID: 11828387
[TBL] [Abstract][Full Text] [Related]
2. Recombinant adeno-associated virus-mediated in utero gene transfer gives therapeutic transgene expression in the sheep.
David AL; McIntosh J; Peebles DM; Cook T; Waddington S; Weisz B; Wigley V; Abi-Nader K; Boyd M; Davidoff AM; Nathwani AC
Hum Gene Ther; 2011 Apr; 22(4):419-26. PubMed ID: 20919876
[TBL] [Abstract][Full Text] [Related]
3. Therapeutic plasma concentrations of human factor IX in mice after gene delivery into the amniotic cavity: a model for the prenatal treatment of haemophilia B.
Schneider H; Adebakin S; Themis M; Cook T; Douar AM; Pavirani A; Coutelle C
J Gene Med; 1999; 1(6):424-32. PubMed ID: 10753068
[TBL] [Abstract][Full Text] [Related]
4. Persistent and therapeutic concentrations of human factor IX in mice after hepatic gene transfer of recombinant AAV vectors.
Snyder RO; Miao CH; Patijn GA; Spratt SK; Danos O; Nagy D; Gown AM; Winther B; Meuse L; Cohen LK; Thompson AR; Kay MA
Nat Genet; 1997 Jul; 16(3):270-6. PubMed ID: 9207793
[TBL] [Abstract][Full Text] [Related]
5. Efficient induction of immune tolerance to coagulation factor IX following direct intramuscular gene transfer.
Cohn EF; Zhuo J; Kelly ME; Chao HJ
J Thromb Haemost; 2007 Jun; 5(6):1227-36. PubMed ID: 17362228
[TBL] [Abstract][Full Text] [Related]
6. In utero gene transfer of human factor IX to fetal mice can induce postnatal tolerance of the exogenous clotting factor.
Waddington SN; Buckley SM; Nivsarkar M; Jezzard S; Schneider H; Dahse T; Kemball-Cook G; Miah M; Tucker N; Dallman MJ; Themis M; Coutelle C
Blood; 2003 Feb; 101(4):1359-66. PubMed ID: 12393743
[TBL] [Abstract][Full Text] [Related]
7. Potential limits of AAV-based gene therapy with the use of new transgenes expressing factor IX fusion proteins.
Le Quellec S; Dane A; Enjolras N; McIntosh J; Rosales C; Negrier C; Nathwani A
Haemophilia; 2019 Jan; 25(1):e11-e18. PubMed ID: 30520547
[TBL] [Abstract][Full Text] [Related]
8. In Utero Transfer of Adeno-Associated Viral Vectors Produces Long-Term Factor IX Levels in a Cynomolgus Macaque Model.
Mattar CNZ; Gil-Farina I; Rosales C; Johana N; Tan YYW; McIntosh J; Kaeppel C; Waddington SN; Biswas A; Choolani M; Schmidt M; Nathwani AC; Chan JKY
Mol Ther; 2017 Aug; 25(8):1843-1853. PubMed ID: 28462816
[TBL] [Abstract][Full Text] [Related]
9. Efficient delivery of human clotting factor IX after injection of lentiviral vectors in utero.
Chen XG; Zhu HZ; Gong JL; Li F; Xue JL
Acta Pharmacol Sin; 2004 Jun; 25(6):789-93. PubMed ID: 15169633
[TBL] [Abstract][Full Text] [Related]
10. Muscle as a target for supplementary factor IX gene transfer.
Hoffman BE; Dobrzynski E; Wang L; Hirao L; Mingozzi F; Cao O; Herzog RW
Hum Gene Ther; 2007 Jul; 18(7):603-13. PubMed ID: 17594244
[TBL] [Abstract][Full Text] [Related]
11. Stable human FIX expression after 0.9G intrauterine gene transfer of self-complementary adeno-associated viral vector 5 and 8 in macaques.
Mattar CN; Nathwani AC; Waddington SN; Dighe N; Kaeppel C; Nowrouzi A; Mcintosh J; Johana NB; Ogden B; Fisk NM; Davidoff AM; David A; Peebles D; Valentine MB; Appelt JU; von Kalle C; Schmidt M; Biswas A; Choolani M; Chan JK
Mol Ther; 2011 Nov; 19(11):1950-60. PubMed ID: 21629224
[TBL] [Abstract][Full Text] [Related]
12. Long-term and therapeutic-level hepatic gene expression of human factor IX after naked plasmid transfer in vivo.
Miao CH; Thompson AR; Loeb K; Ye X
Mol Ther; 2001 Jun; 3(6):947-57. PubMed ID: 11407909
[TBL] [Abstract][Full Text] [Related]
13. Ultrasound-guided percutaneous delivery of adenoviral vectors encoding the beta-galactosidase and human factor IX genes to early gestation fetal sheep in utero.
David A; Cook T; Waddington S; Peebles D; Nivsarkar M; Knapton H; Miah M; Dahse T; Noakes D; Schneider H; Rodeck C; Coutelle C; Themis M
Hum Gene Ther; 2003 Mar; 14(4):353-64. PubMed ID: 12659676
[TBL] [Abstract][Full Text] [Related]
14. [Preparation of rAAV2/hFIX and experimentally application to gene therapy for hemophilia B].
Peng JQ; Dong XY; Peng M; Chen L; Tan SP; Yuan H; Chen FP; Xue JL; Wu XB
Zhonghua Xue Ye Xue Za Zhi; 2004 Sep; 25(9):513-8. PubMed ID: 15569526
[TBL] [Abstract][Full Text] [Related]
15. Role of the vector genome and underlying factor IX mutation in immune responses to AAV gene therapy for hemophilia B.
Rogers GL; Martino AT; Zolotukhin I; Ertl HC; Herzog RW
J Transl Med; 2014 Jan; 12():25. PubMed ID: 24460861
[TBL] [Abstract][Full Text] [Related]
16. Direct intramuscular injection with recombinant AAV vectors results in sustained expression in a dog model of hemophilia.
Monahan PE; Samulski RJ; Tazelaar J; Xiao X; Nichols TC; Bellinger DA; Read MS; Walsh CE
Gene Ther; 1998 Jan; 5(1):40-9. PubMed ID: 9536263
[TBL] [Abstract][Full Text] [Related]
17. Preclinical in vivo evaluation of pseudotyped adeno-associated virus vectors for liver gene therapy.
Grimm D; Zhou S; Nakai H; Thomas CE; Storm TA; Fuess S; Matsushita T; Allen J; Surosky R; Lochrie M; Meuse L; McClelland A; Colosi P; Kay MA
Blood; 2003 Oct; 102(7):2412-9. PubMed ID: 12791653
[TBL] [Abstract][Full Text] [Related]
18. No evidence for germ-line transmission following prenatal and early postnatal AAV-mediated gene delivery.
Jakob M; Mühle C; Park J; Weiss S; Waddington S; Schneider H
J Gene Med; 2005 May; 7(5):630-7. PubMed ID: 15693035
[TBL] [Abstract][Full Text] [Related]
19. Gene therapy for hemophilia B mice with scAAV8-LP1-hFIX.
Lu W; Zhou Q; Yang H; Wang H; Gu Y; Shen Q; Xue J; Dong X; Chen J
Front Med; 2016 Jun; 10(2):212-8. PubMed ID: 27052253
[TBL] [Abstract][Full Text] [Related]
20. Persistent expression of hF.IX After tolerance induction by in utero or neonatal administration of AAV-1-F.IX in hemophilia B mice.
Sabatino DE; Mackenzie TC; Peranteau W; Edmonson S; Campagnoli C; Liu YL; Flake AW; High KA
Mol Ther; 2007 Sep; 15(9):1677-85. PubMed ID: 17565352
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]
