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4. Restoration of dystrophin expression in mdx muscle cells by chimeraplast-mediated exon skipping. Bertoni C; Lau C; Rando TA Hum Mol Genet; 2003 May; 12(10):1087-99. PubMed ID: 12719373 [TBL] [Abstract][Full Text] [Related]
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11. Cell and gene therapy in Duchenne muscular dystrophy. Morgan JE Hum Gene Ther; 1994 Feb; 5(2):165-73. PubMed ID: 7514447 [TBL] [Abstract][Full Text] [Related]
12. CD45 fraction bone marrow cells as potential delivery vehicles for genetically corrected dystrophin loci. Kapsa RM; Wong SH; Bertoncello I; Quigley AF; Williams B; Sells K; Marotta R; Kita M; Simmons P; Byrne E; Kornberg AJ Neuromuscul Disord; 2002 Oct; 12 Suppl 1():S61-6. PubMed ID: 12206798 [TBL] [Abstract][Full Text] [Related]
13. Electrotransfer of naked DNA in the skeletal muscles of animal models of muscular dystrophies. Vilquin JT; Kennel PF; Paturneau-Jouas M; Chapdelaine P; Boissel N; Delaère P; Tremblay JP; Scherman D; Fiszman MY; Schwartz K Gene Ther; 2001 Jul; 8(14):1097-107. PubMed ID: 11526457 [TBL] [Abstract][Full Text] [Related]
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19. Cardiac Protection after Systemic Transplant of Dystrophin Expressing Chimeric (DEC) Cells to the mdx Mouse Model of Duchenne Muscular Dystrophy. Siemionow M; Malik M; Langa P; Cwykiel J; Brodowska S; Heydemann A Stem Cell Rev Rep; 2019 Dec; 15(6):827-841. PubMed ID: 31612351 [TBL] [Abstract][Full Text] [Related]
20. Efficient adenovirus-mediated transfer of a human minidystrophin gene to skeletal muscle of mdx mice. Ragot T; Vincent N; Chafey P; Vigne E; Gilgenkrantz H; Couton D; Cartaud J; Briand P; Kaplan JC; Perricaudet M Nature; 1993 Feb; 361(6413):647-50. PubMed ID: 8437625 [TBL] [Abstract][Full Text] [Related] [Next] [New Search]