These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.


BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

227 related articles for article (PubMed ID: 12206798)

  • 1. CD45 fraction bone marrow cells as potential delivery vehicles for genetically corrected dystrophin loci.
    Kapsa RM; Wong SH; Bertoncello I; Quigley AF; Williams B; Sells K; Marotta R; Kita M; Simmons P; Byrne E; Kornberg AJ
    Neuromuscul Disord; 2002 Oct; 12 Suppl 1():S61-6. PubMed ID: 12206798
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Targeted gene correction in the mdx mouse using short DNA fragments: towards application with bone marrow-derived cells for autologous remodeling of dystrophic muscle.
    Kapsa RM; Quigley AF; Vadolas J; Steeper K; Ioannou PA; Byrne E; Kornberg AJ
    Gene Ther; 2002 Jun; 9(11):695-9. PubMed ID: 12032690
    [TBL] [Abstract][Full Text] [Related]  

  • 3. In vivo and in vitro correction of the mdx dystrophin gene nonsense mutation by short-fragment homologous replacement.
    Kapsa R; Quigley A; Lynch GS; Steeper K; Kornberg AJ; Gregorevic P; Austin L; Byrne E
    Hum Gene Ther; 2001 Apr; 12(6):629-42. PubMed ID: 11426463
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Oligonucleotide-mediated gene therapy for muscular dystrophies.
    Rando TA
    Neuromuscul Disord; 2002 Oct; 12 Suppl 1():S55-60. PubMed ID: 12206797
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Dystrophin gene repair in mdx muscle precursor cells in vitro and in vivo mediated by RNA-DNA chimeric oligonucleotides.
    Bertoni C; Rando TA
    Hum Gene Ther; 2002 Apr; 13(6):707-18. PubMed ID: 11936970
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Restoration of human dystrophin following transplantation of exon-skipping-engineered DMD patient stem cells into dystrophic mice.
    Benchaouir R; Meregalli M; Farini A; D'Antona G; Belicchi M; Goyenvalle A; Battistelli M; Bresolin N; Bottinelli R; Garcia L; Torrente Y
    Cell Stem Cell; 2007 Dec; 1(6):646-57. PubMed ID: 18371406
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Differential effects of dystrophin and utrophin gene transfer in immunocompetent muscular dystrophy (mdx) mice.
    Ebihara S; Guibinga GH; Gilbert R; Nalbantoglu J; Massie B; Karpati G; Petrof BJ
    Physiol Genomics; 2000 Sep; 3(3):133-44. PubMed ID: 11015608
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Enhanced in vivo delivery of antisense oligonucleotides to restore dystrophin expression in adult mdx mouse muscle.
    Wells KE; Fletcher S; Mann CJ; Wilton SD; Wells DJ
    FEBS Lett; 2003 Sep; 552(2-3):145-9. PubMed ID: 14527677
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Screening for antisense modulation of dystrophin pre-mRNA splicing.
    Dickson G; Hill V; Graham IR
    Neuromuscul Disord; 2002 Oct; 12 Suppl 1():S67-70. PubMed ID: 12206799
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Ex vivo gene transfer using adenovirus-mediated full-length dystrophin delivery to dystrophic muscles.
    Floyd SS; Clemens PR; Ontell MR; Kochanek S; Day CS; Yang J; Hauschka SD; Balkir L; Morgan J; Moreland MS; Feero GW; Epperly M; Huard J
    Gene Ther; 1998 Jan; 5(1):19-30. PubMed ID: 9536261
    [TBL] [Abstract][Full Text] [Related]  

  • 11. [Gene therapy for muscular dystrophy].
    Takeda S
    No To Hattatsu; 2004 Mar; 36(2):117-23. PubMed ID: 15031985
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Gene transfer studies in animals: what do they really tell us about the prospects for gene therapy in DMD?
    Wells DJ; Wells KE
    Neuromuscul Disord; 2002 Oct; 12 Suppl 1():S11-22. PubMed ID: 12206790
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Targeted exon skipping as a potential gene correction therapy for Duchenne muscular dystrophy.
    Aartsma-Rus A; Bremmer-Bout M; Janson AA; den Dunnen JT; van Ommen GJ; van Deutekom JC
    Neuromuscul Disord; 2002 Oct; 12 Suppl 1():S71-7. PubMed ID: 12206800
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Dystrophin delivery in dystrophin-deficient DMDmdx skeletal muscle by isogenic muscle-derived stem cell transplantation.
    Ikezawa M; Cao B; Qu Z; Peng H; Xiao X; Pruchnic R; Kimura S; Miike T; Huard J
    Hum Gene Ther; 2003 Nov; 14(16):1535-46. PubMed ID: 14577915
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Electroporation of corrective nucleic acids (CNA) in vivo to promote gene correction in dystrophic muscle.
    Kapsa RM; Wong SH; Quigley AF
    Methods Mol Biol; 2008; 423():405-19. PubMed ID: 18370218
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Cell-lineage regulated myogenesis for dystrophin replacement: a novel therapeutic approach for treatment of muscular dystrophy.
    Kimura E; Han JJ; Li S; Fall B; Ra J; Haraguchi M; Tapscott SJ; Chamberlain JS
    Hum Mol Genet; 2008 Aug; 17(16):2507-17. PubMed ID: 18511457
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Therapeutic gene transfer to dystrophic diaphragm by an adenoviral vector deleted of all viral genes.
    Matecki S; Dudley RW; Divangahi M; Gilbert R; Nalbantoglu J; Karpati G; Petrof BJ
    Am J Physiol Lung Cell Mol Physiol; 2004 Sep; 287(3):L569-76. PubMed ID: 15155269
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Mdx mice inducibly expressing dystrophin provide insights into the potential of gene therapy for duchenne muscular dystrophy.
    Ahmad A; Brinson M; Hodges BL; Chamberlain JS; Amalfitano A
    Hum Mol Genet; 2000 Oct; 9(17):2507-15. PubMed ID: 11030755
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Splice modification to restore functional dystrophin synthesis in Duchenne muscular dystrophy.
    Wilton SD; Fletcher S
    Curr Pharm Des; 2010; 16(8):988-1001. PubMed ID: 20041827
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Morpholino oligomer-mediated exon skipping averts the onset of dystrophic pathology in the mdx mouse.
    Fletcher S; Honeyman K; Fall AM; Harding PL; Johnsen RD; Steinhaus JP; Moulton HM; Iversen PL; Wilton SD
    Mol Ther; 2007 Sep; 15(9):1587-92. PubMed ID: 17579573
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 12.