These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.
2. Advances toward gene therapy for hemophilia at the millennium. Kaufman RJ Hum Gene Ther; 1999 Sep; 10(13):2091-107. PubMed ID: 10498242 [TBL] [Abstract][Full Text] [Related]
3. AAV-mediated gene transfer for hemophilia. High KA Ann N Y Acad Sci; 2001 Dec; 953():64-74. PubMed ID: 11795424 [TBL] [Abstract][Full Text] [Related]
5. Gene transfer as an approach to treating hemophilia. High KA Circ Res; 2001 Feb; 88(2):137-44. PubMed ID: 11157664 [TBL] [Abstract][Full Text] [Related]
6. Gene therapy for the hemophilias. Walsh CE Curr Opin Pediatr; 2002 Feb; 14(1):12-6. PubMed ID: 11880728 [TBL] [Abstract][Full Text] [Related]
11. Gene therapy progress and prospects: gene therapy for the hemophilias. Walsh CE Gene Ther; 2003 Jun; 10(12):999-1003. PubMed ID: 12776156 [TBL] [Abstract][Full Text] [Related]
12. Recent progress in gene therapy for hemophilia. Chuah MK; Nair N; VandenDriessche T Hum Gene Ther; 2012 Jun; 23(6):557-65. PubMed ID: 22671033 [TBL] [Abstract][Full Text] [Related]
13. Theodore E. Woodward Award. AAV-mediated gene transfer for hemophilia. High KA Trans Am Clin Climatol Assoc; 2003; 114():337-51; discussion 351-2. PubMed ID: 12813929 [TBL] [Abstract][Full Text] [Related]
14. Gene therapy for hemophilia. Nathwani AC Hematology Am Soc Hematol Educ Program; 2019 Dec; 2019(1):1-8. PubMed ID: 31808868 [TBL] [Abstract][Full Text] [Related]
15. What´s new in Gene Therapy of Hemophilia. Rodriguez-Merchan EC Curr Gene Ther; 2018; 18(2):107-114. PubMed ID: 29446741 [TBL] [Abstract][Full Text] [Related]
16. Gene therapy for the hemophilias. Walter J; High KA Adv Vet Med; 1997; 40():119-34. PubMed ID: 9395731 [TBL] [Abstract][Full Text] [Related]
17. Rare bleeding disorders-old diseases in the era of novel options for therapy. Livnat T; Barg AA; Levy-Mendelovich S; Kenet G Blood Cells Mol Dis; 2017 Sep; 67():63-68. PubMed ID: 28222949 [TBL] [Abstract][Full Text] [Related]
18. Management of hemophilias--gene therapy to come? Vajó Z; Sréter L Acta Physiol Hung; 1996; 84(2):191-8. PubMed ID: 9046365 [TBL] [Abstract][Full Text] [Related]