These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.
5. Restoration of human dystrophin following transplantation of exon-skipping-engineered DMD patient stem cells into dystrophic mice. Benchaouir R; Meregalli M; Farini A; D'Antona G; Belicchi M; Goyenvalle A; Battistelli M; Bresolin N; Bottinelli R; Garcia L; Torrente Y Cell Stem Cell; 2007 Dec; 1(6):646-57. PubMed ID: 18371406 [TBL] [Abstract][Full Text] [Related]
6. Progress in gene therapy of dystrophic heart disease. Lai Y; Duan D Gene Ther; 2012 Jun; 19(6):678-85. PubMed ID: 22318092 [TBL] [Abstract][Full Text] [Related]
7. Gene transfer studies in animals: what do they really tell us about the prospects for gene therapy in DMD? Wells DJ; Wells KE Neuromuscul Disord; 2002 Oct; 12 Suppl 1():S11-22. PubMed ID: 12206790 [TBL] [Abstract][Full Text] [Related]
8. Splice modification to restore functional dystrophin synthesis in Duchenne muscular dystrophy. Wilton SD; Fletcher S Curr Pharm Des; 2010; 16(8):988-1001. PubMed ID: 20041827 [TBL] [Abstract][Full Text] [Related]
9. Viral vectors for gene transfer of micro-, mini-, or full-length dystrophin. Scott JM; Li S; Harper SQ; Welikson R; Bourque D; DelloRusso C; Hauschka SD; Chamberlain JS Neuromuscul Disord; 2002 Oct; 12 Suppl 1():S23-9. PubMed ID: 12206791 [TBL] [Abstract][Full Text] [Related]
15. Gene therapy for muscular dystrophies: current status and future prospects. Takeda S; Miyagoe-Suzuki Y BioDrugs; 2001; 15(10):635-44. PubMed ID: 11604045 [TBL] [Abstract][Full Text] [Related]
16. Dystrophin-glycoprotein complex: its role in the molecular pathogenesis of muscular dystrophies. Matsumura K; Campbell KP Muscle Nerve; 1994 Jan; 17(1):2-15. PubMed ID: 8264699 [TBL] [Abstract][Full Text] [Related]