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6. Evolving Gene Therapy in Primary Immunodeficiency. Thrasher AJ; Williams DA Mol Ther; 2017 May; 25(5):1132-1141. PubMed ID: 28366768 [TBL] [Abstract][Full Text] [Related]
7. Treatment of patients with severe combined immunodeficiency due to adenosine deaminase (ADA) deficiency by autologous transplantation of genetically modified bone marrow cells. Hoogerbrugge PM; Vossen JM; v Beusechem VW; Valerio D Hum Gene Ther; 1992 Oct; 3(5):553-8. PubMed ID: 1420454 [No Abstract] [Full Text] [Related]
8. Efficacy of gene therapy for SCID is being confirmed. Cavazzana-Calvo M; Fischer A Lancet; 2004 Dec 18-31; 364(9452):2155-6. PubMed ID: 15610783 [No Abstract] [Full Text] [Related]
9. A Journey in the Development of Gene Therapy for Inherited Disorders of the Bone Marrow. Kohn D; Wilson JM Hum Gene Ther Clin Dev; 2015 Dec; 26(4):203-7. PubMed ID: 26684443 [No Abstract] [Full Text] [Related]
10. Towards a rAAV-based gene therapy for ADA-SCID: from ADA deficiency to current and future treatment strategies. Silver JN; Flotte TR Pharmacogenomics; 2008 Jul; 9(7):947-68. PubMed ID: 18597656 [TBL] [Abstract][Full Text] [Related]
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12. [Transplantation of genetically modified cells in the treatment of children with SCID: great hopes and recent disappointments]. Smogorzewska EM; Weinberg KI; Kohn DB Med Wieku Rozwoj; 2003; 7(1):27-34. PubMed ID: 13130167 [TBL] [Abstract][Full Text] [Related]
13. Gene therapy for severe combined immunodeficiencies and beyond. Fischer A; Hacein-Bey-Abina S J Exp Med; 2020 Jan; 217(2):. PubMed ID: 31826240 [TBL] [Abstract][Full Text] [Related]
14. Development of gene therapy for immunodeficiency: adenosine deaminase deficiency. Blaese RM Pediatr Res; 1993 Jan; 33(1 Suppl):S49-53; discussion S53-5. PubMed ID: 8433875 [TBL] [Abstract][Full Text] [Related]
15. Bone marrow transplantation and alternatives for adenosine deaminase deficiency. Gaspar HB Immunol Allergy Clin North Am; 2010 May; 30(2):221-36. PubMed ID: 20493398 [TBL] [Abstract][Full Text] [Related]
16. ADA-SCID Gene Therapy Endorsed By European Medicines Agency For Marketing Authorization. Ylä-Herttuala S Mol Ther; 2016 Jun; 24(6):1013-1014. PubMed ID: 27324442 [No Abstract] [Full Text] [Related]
18. Success for gene therapy: render unto Caesar that which is Caesar's. Qiao J; Diaz RM; Vile RG Genome Biol; 2004; 5(8):237. PubMed ID: 15287968 [TBL] [Abstract][Full Text] [Related]
19. Gene therapy for severe combined immunodeficiency: are we there yet? Cavazzana-Calvo M; Fischer A J Clin Invest; 2007 Jun; 117(6):1456-65. PubMed ID: 17549248 [TBL] [Abstract][Full Text] [Related]