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26. Efficacy of gene therapy for SCID is being confirmed. Cavazzana-Calvo M; Fischer A Lancet; 2004 Dec 18-31; 364(9452):2155-6. PubMed ID: 15610783 [No Abstract] [Full Text] [Related]
27. LMO2 and gene therapy for severe combined immunodeficiency. Stone BD N Engl J Med; 2004 Jun; 350(24):2526-7; author reply 2526-7. PubMed ID: 15195349 [No Abstract] [Full Text] [Related]
28. Enzyme replacement therapy with polyethylene glycol-adenosine deaminase in adenosine deaminase deficiency: overview and case reports of three patients, including two now receiving gene therapy. Hershfield MS; Chaffee S; Sorensen RU Pediatr Res; 1993 Jan; 33(1 Suppl):S42-7; discussion S47-8. PubMed ID: 8433874 [TBL] [Abstract][Full Text] [Related]
32. Gene therapy for severe combined immune deficiency poised for European approval: If green-lighted, Strimvelis would provide additional treatment option for second most common form of disease. Am J Med Genet A; 2016 Aug; 170(8):1955-6. PubMed ID: 27410196 [No Abstract] [Full Text] [Related]
34. PEG-ADA: an alternative to haploidentical bone marrow transplantation and an adjunct to gene therapy for adenosine deaminase deficiency. Hershfield MS Hum Mutat; 1995; 5(2):107-12. PubMed ID: 7749407 [TBL] [Abstract][Full Text] [Related]
35. [Severe combined immunodeficiencies: a case of adenosine-deaminase deficit]. Macellaro P; Savarino A; Cucchi G; Lazzati A; Zuccotti GV Pediatr Med Chir; 2004; 26(3):191-5. PubMed ID: 16366403 [TBL] [Abstract][Full Text] [Related]
36. Gene transfer therapy for heritable disease: cell and expression targeting. Mitani K; Clemens PR; Moseley AB; Caskey CT Philos Trans R Soc Lond B Biol Sci; 1993 Feb; 339(1288):217-24. PubMed ID: 8097051 [TBL] [Abstract][Full Text] [Related]