BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

317 related articles for article (PubMed ID: 15110316)

  • 1. Neonatal retroviral vector-mediated hepatic gene therapy reduces bone, joint, and cartilage disease in mucopolysaccharidosis VII mice and dogs.
    Mango RL; Xu L; Sands MS; Vogler C; Seiler G; Schwarz T; Haskins ME; Ponder KP
    Mol Genet Metab; 2004 May; 82(1):4-19. PubMed ID: 15110316
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Gene therapy ameliorates cardiovascular disease in dogs with mucopolysaccharidosis VII.
    Sleeper MM; Fornasari B; Ellinwood NM; Weil MA; Melniczek J; O'Malley TM; Sammarco CD; Xu L; Ponder KP; Haskins ME
    Circulation; 2004 Aug; 110(7):815-20. PubMed ID: 15289379
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Expression in blood cells may contribute to biochemical and pathological improvements after neonatal intravenous gene therapy for mucopolysaccharidosis VII in dogs.
    Wang B; O'Malley TM; Xu L; Vite C; Wang P; O'Donnell PA; Ellinwood NM; Haskins ME; Ponder KP
    Mol Genet Metab; 2006 Jan; 87(1):8-21. PubMed ID: 16275036
    [TBL] [Abstract][Full Text] [Related]  

  • 4. The effect of neonatal gene therapy on skeletal manifestations in mucopolysaccharidosis VII dogs after a decade.
    Xing EM; Knox VW; O'Donnell PA; Sikura T; Liu Y; Wu S; Casal ML; Haskins ME; Ponder KP
    Mol Genet Metab; 2013 Jun; 109(2):183-93. PubMed ID: 23628461
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Evaluation of pathological manifestations of disease in mucopolysaccharidosis VII mice after neonatal hepatic gene therapy.
    Xu L; Mango RL; Sands MS; Haskins ME; Ellinwood NM; Ponder KP
    Mol Ther; 2002 Dec; 6(6):745-58. PubMed ID: 12498771
    [TBL] [Abstract][Full Text] [Related]  

  • 6. The effect of Tlr4 and/or C3 deficiency and of neonatal gene therapy on skeletal disease in mucopolysaccharidosis VII mice.
    Xing EM; Wu S; Ponder KP
    Mol Genet Metab; 2015 Feb; 114(2):209-16. PubMed ID: 25559179
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Therapeutic neonatal hepatic gene therapy in mucopolysaccharidosis VII dogs.
    Ponder KP; Melniczek JR; Xu L; Weil MA; O'Malley TM; O'Donnell PA; Knox VW; Aguirre GD; Mazrier H; Ellinwood NM; Sleeper M; Maguire AM; Volk SW; Mango RL; Zweigle J; Wolfe JH; Haskins ME
    Proc Natl Acad Sci U S A; 2002 Oct; 99(20):13102-7. PubMed ID: 12232044
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Transduction of hepatocytes after neonatal delivery of a Moloney murine leukemia virus based retroviral vector results in long-term expression of beta-glucuronidase in mucopolysaccharidosis VII dogs.
    Xu L; Haskins ME; Melniczek JR; Gao C; Weil MA; O'Malley TM; O'Donnell PA; Mazrier H; Ellinwood NM; Zweigle J; Wolfe JH; Ponder KP
    Mol Ther; 2002 Feb; 5(2):141-53. PubMed ID: 11829521
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Effect of neonatal gene therapy on lumbar spine disease in mucopolysaccharidosis VII dogs.
    Smith LJ; Martin JT; O'Donnell P; Wang P; Elliott DM; Haskins ME; Ponder KP
    Mol Genet Metab; 2012 Sep; 107(1-2):145-52. PubMed ID: 22510705
    [TBL] [Abstract][Full Text] [Related]  

  • 10. The effect of neonatal gene therapy with a gamma retroviral vector on cardiac valve disease in mucopolysaccharidosis VII dogs after a decade.
    Bigg PW; Sleeper MM; O'Donnell PA; Liu Y; Wu S; Casal ML; Haskins ME; Ponder KP
    Mol Genet Metab; 2013 Nov; 110(3):311-8. PubMed ID: 23860311
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Neonatal intramuscular injection with recombinant adeno-associated virus results in prolonged beta-glucuronidase expression in situ and correction of liver pathology in mucopolysaccharidosis type VII mice.
    Daly TM; Okuyama T; Vogler C; Haskins ME; Muzyczka N; Sands MS
    Hum Gene Ther; 1999 Jan; 10(1):85-94. PubMed ID: 10022533
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Skeletal response to lentiviral mediated gene therapy in a mouse model of MPS VII.
    Macsai CE; Derrick-Roberts AL; Ding X; Zarrinkalam KH; McIntyre C; Anderson PH; Anson DS; Byers S
    Mol Genet Metab; 2012 Jun; 106(2):202-13. PubMed ID: 22525091
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Murine mucopolysaccharidosis type VII: the impact of therapies on the clinical course and pathology in a murine model of lysosomal storage disease.
    Vogler C; Sands MS; Galvin N; Levy B; Thorpe C; Barker J; Sly WS
    J Inherit Metab Dis; 1998 Aug; 21(5):575-86. PubMed ID: 9728337
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Evaluation of AAV-mediated Gene Therapy for Central Nervous System Disease in Canine Mucopolysaccharidosis VII.
    Gurda BL; De Guilhem De Lataillade A; Bell P; Zhu Y; Yu H; Wang P; Bagel J; Vite CH; Sikora T; Hinderer C; Calcedo R; Yox AD; Steet RA; Ruane T; O'Donnell P; Gao G; Wilson JM; Casal M; Ponder KP; Haskins ME
    Mol Ther; 2016 Feb; 24(2):206-216. PubMed ID: 26447927
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Delivery of a retroviral vector expressing human beta-glucuronidase to the liver and spleen decreases lysosomal storage in mucopolysaccharidosis VII mice.
    Gao C; Sands MS; Haskins ME; Ponder KP
    Mol Ther; 2000 Sep; 2(3):233-44. PubMed ID: 10985954
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Cloning of the canine beta-glucuronidase cDNA, mutation identification in canine MPS VII, and retroviral vector-mediated correction of MPS VII cells.
    Ray J; Bouvet A; DeSanto C; Fyfe JC; Xu D; Wolfe JH; Aguirre GD; Patterson DF; Haskins ME; Henthorn PS
    Genomics; 1998 Mar; 48(2):248-53. PubMed ID: 9521879
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Intracranial injection of recombinant adeno-associated virus improves cognitive function in a murine model of mucopolysaccharidosis type VII.
    Frisella WA; O'Connor LH; Vogler CA; Roberts M; Walkley S; Levy B; Daly TM; Sands MS
    Mol Ther; 2001 Mar; 3(3):351-8. PubMed ID: 11273777
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Radiographic evaluation of bones and joints in mucopolysaccharidosis I and VII dogs after neonatal gene therapy.
    Herati RS; Knox VW; O'Donnell P; D'Angelo M; Haskins ME; Ponder KP
    Mol Genet Metab; 2008 Nov; 95(3):142-51. PubMed ID: 18707908
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Comparison of ventricular and intravenous lentiviral-mediated gene therapy for murine MPS VII.
    Bielicki J; McIntyre C; Anson DS
    Mol Genet Metab; 2010 Dec; 101(4):370-82. PubMed ID: 20864369
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Widespread correction of lysosomal storage following intrahepatic injection of a recombinant adeno-associated virus in the adult MPS VII mouse.
    Sferra TJ; Backstrom K; Wang C; Rennard R; Miller M; Hu Y
    Mol Ther; 2004 Sep; 10(3):478-91. PubMed ID: 15336648
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 16.