BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

123 related articles for article (PubMed ID: 15259445)

  • 1. Laronidase opens door to treat other rare disorders.
    Morrow T
    Manag Care; 2004 Jun; 13(6):52-3. PubMed ID: 15259445
    [No Abstract]   [Full Text] [Related]  

  • 2. First treatment for rare enzyme disorder.
    FDA Consum; 2003; 37(4):6. PubMed ID: 12971332
    [No Abstract]   [Full Text] [Related]  

  • 3. Alpha-L-iduronidase (laronidase; aldurazyme).
    Med Lett Drugs Ther; 2003 Oct; 45(1168):88. PubMed ID: 14576624
    [No Abstract]   [Full Text] [Related]  

  • 4. Long-term efficacy and safety of laronidase in the treatment of mucopolysaccharidosis I.
    Clarke LA; Wraith JE; Beck M; Kolodny EH; Pastores GM; Muenzer J; Rapoport DM; Berger KI; Sidman M; Kakkis ED; Cox GF
    Pediatrics; 2009 Jan; 123(1):229-40. PubMed ID: 19117887
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Enzyme replacement therapy with laronidase (Aldurazyme(®)) for treating mucopolysaccharidosis type I.
    Jameson E; Jones S; Remmington T
    Cochrane Database Syst Rev; 2016 Apr; 4():CD009354. PubMed ID: 27033167
    [TBL] [Abstract][Full Text] [Related]  

  • 6. [Hurler syndrome. Early diagnosis and successful enzyme replacement therapy: a new therapeutic approach. Case report].
    Dupont C; El Hachem C; Harchaoui S; Ribault V; Amiour M; Guillot M; Maire I; Froissart R; Guffon-Fouilhoux N
    Arch Pediatr; 2008 Jan; 15(1):45-9. PubMed ID: 18162380
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Enzyme replacement therapy for mucopolysaccharidosis I: a randomized, double-blinded, placebo-controlled, multinational study of recombinant human alpha-L-iduronidase (laronidase).
    Wraith JE; Clarke LA; Beck M; Kolodny EH; Pastores GM; Muenzer J; Rapoport DM; Berger KI; Swiedler SJ; Kakkis ED; Braakman T; Chadbourne E; Walton-Bowen K; Cox GF
    J Pediatr; 2004 May; 144(5):581-8. PubMed ID: 15126990
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Enzyme replacement therapy in patients who have mucopolysaccharidosis I and are younger than 5 years: results of a multinational study of recombinant human alpha-L-iduronidase (laronidase).
    Wraith JE; Beck M; Lane R; van der Ploeg A; Shapiro E; Xue Y; Kakkis ED; Guffon N
    Pediatrics; 2007 Jul; 120(1):e37-46. PubMed ID: 17606547
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Impact of 144 weeks of laronidase therapy on body functions, endurance and general well-being in a Hurler-Scheie patient.
    Soutar RL; Mercer J; Wraith JE
    J Inherit Metab Dis; 2006 Aug; 29(4):590. PubMed ID: 16830264
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Mucopolysaccharidosis I under enzyme replacement therapy with laronidase--a mortality case with autopsy report.
    Lin HY; Lin SP; Chuang CK; Chen MR; Chen BF; Wraith JE
    J Inherit Metab Dis; 2005; 28(6):1146-8. PubMed ID: 16435211
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Combined enzyme replacement and haematopoietic stem cell transplantation in Hurler syndrome.
    Bijarnia S; Shaw P; Vimpani A; Smith R; Pacey V; O'Grady H; Christodoulou J; Sillence D
    J Paediatr Child Health; 2009; 45(7-8):469-72. PubMed ID: 19712183
    [TBL] [Abstract][Full Text] [Related]  

  • 12. [Laronidase for treating post-surgical respiratory failure in a patient with type I mucopolysaccharidosis].
    Vélez-Díaz-Pallarés M; Sánchez Cuervo M; Martínez-Pardo Casanova M; Bermejo Vicedo T
    Farm Hosp; 2012; 36(1):55-6. PubMed ID: 21641259
    [No Abstract]   [Full Text] [Related]  

  • 13. Effect of discontinuing of laronidase in a patient with mucopolysaccharidosis type I.
    Anbu AT; Mercer J; Wraith JE
    J Inherit Metab Dis; 2006 Feb; 29(1):230-1. PubMed ID: 16601901
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Alternative laronidase dose regimen for patients with mucopolysaccharidosis I: a multinational, retrospective, chart review case series.
    Horovitz DD; Acosta AX; Giugliani R; Hlavatá A; Hlavatá K; Tchan MC; Lopes Barth A; Cardoso L; Embiruçu de Araújo Leão EK; Esposito AC; Kyosen SO; De Souza CF; Martins AM
    Orphanet J Rare Dis; 2016 Apr; 11(1):51. PubMed ID: 27129473
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Enzyme replacement therapy in feline mucopolysaccharidosis I.
    Kakkis ED; Schuchman E; He X; Wan Q; Kania S; Wiemelt S; Hasson CW; O'Malley T; Weil MA; Aguirre GA; Brown DE; Haskins ME
    Mol Genet Metab; 2001 Mar; 72(3):199-208. PubMed ID: 11243725
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Ethical issues related to the access to orphan drugs in Brazil: the case of mucopolysaccharidosis type I.
    Boy R; Schwartz IV; Krug BC; Santana-da-Silva LC; Steiner CE; Acosta AX; Ribeiro EM; Galera MF; Leivas PG; Braz M
    J Med Ethics; 2011 Apr; 37(4):233-9. PubMed ID: 21266385
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Decreased corneal opacity and improved vision in a patient with mucopolysaccharidosis I (Hurler-Scheie) treated with enzyme replacement therapy (laronidase, Aldurazyme).
    Cáceres-Marzal C; García-Reymundo M; Solana J; de Arévalo B; Vaquerizo J; Galán E
    Am J Med Genet A; 2008 Jul; 146A(13):1768-70. PubMed ID: 18546328
    [No Abstract]   [Full Text] [Related]  

  • 18. Laronidase.
    BioDrugs; 2002; 16(4):316-8. PubMed ID: 12196045
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Treatment of respiratory system (not just lung!) abnormalities in Mucopolysaccharidosis I.
    Allen JL
    J Pediatr; 2004 May; 144(5):561-2. PubMed ID: 15126984
    [No Abstract]   [Full Text] [Related]  

  • 20. Laronidase for cardiopulmonary disease in Hurler syndrome 12 years after bone marrow transplantation.
    Valayannopoulos V; de Blic J; Mahlaoui N; Stos B; Jaubert F; Bonnet D; Fischer A; de Lonlay P
    Pediatrics; 2010 Nov; 126(5):e1242-7. PubMed ID: 20974778
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 7.