253 related articles for article (PubMed ID: 15640693)
21. Gene therapy of severe combined immunodeficiencies.
Cavazzana-Calvo M; Hacein-Bey S; Yates F; de Villartay JP; Le Deist F; Fischer A
J Gene Med; 2001; 3(3):201-6. PubMed ID: 11437325
[TBL] [Abstract][Full Text] [Related]
22. Gene therapy for adenosine deaminase deficiency.
Aiuti A; Ficara F; Cattaneo F; Bordignon C; Roncarolo MG
Curr Opin Allergy Clin Immunol; 2003 Dec; 3(6):461-6. PubMed ID: 14612670
[TBL] [Abstract][Full Text] [Related]
23. [Transplantation of genetically modified cells in the treatment of children with SCID: great hopes and recent disappointments].
Smogorzewska EM; Weinberg KI; Kohn DB
Med Wieku Rozwoj; 2003; 7(1):27-34. PubMed ID: 13130167
[TBL] [Abstract][Full Text] [Related]
24. Gene therapy for immune disorders: good news tempered by bad news.
Puck JM; Malech HL
J Allergy Clin Immunol; 2006 Apr; 117(4):865-9. PubMed ID: 16630946
[TBL] [Abstract][Full Text] [Related]
25. Gene therapy for severe combined immunodeficiencies.
Gaspar HB; Thrasher AJ
Expert Opin Biol Ther; 2005 Sep; 5(9):1175-82. PubMed ID: 16120048
[TBL] [Abstract][Full Text] [Related]
26. Treatment of severe combined immunodeficiency disease (SCID) due to adenosine deaminase deficiency with CD34+ selected autologous peripheral blood cells transduced with a human ADA gene. Amendment to clinical research project, Project 90-C-195, January 10, 1992.
Blaese RM; Culver KW; Chang L; Anderson WF; Mullen C; Nienhuis A; Carter C; Dunbar C; Leitman S; Berger M
Hum Gene Ther; 1993 Aug; 4(4):521-7. PubMed ID: 7691188
[TBL] [Abstract][Full Text] [Related]
27. [Gene therapy for hereditary immunodeficiencies].
Fischer A; de Saint-Basile G; Disanto JP; Hacein-Bey S; Sharara L; Cavazzana-Calvo M
C R Seances Soc Biol Fil; 1996; 190(1):77-93. PubMed ID: 8881271
[TBL] [Abstract][Full Text] [Related]
28. Gene therapy for inherited immunodeficiencies.
Howe S; Thrasher AJ
Curr Hematol Rep; 2003 Jul; 2(4):328-34. PubMed ID: 12901330
[TBL] [Abstract][Full Text] [Related]
29. Gene Therapy for Adenosine Deaminase Deficiency: A Comprehensive Evaluation of Short- and Medium-Term Safety.
Cicalese MP; Ferrua F; Castagnaro L; Rolfe K; De Boever E; Reinhardt RR; Appleby J; Roncarolo MG; Aiuti A
Mol Ther; 2018 Mar; 26(3):917-931. PubMed ID: 29433935
[TBL] [Abstract][Full Text] [Related]
30. In vivo T-cell dynamics during immune reconstitution after hematopoietic stem cell gene therapy in adenosine deaminase severe combined immune deficiency.
Selleri S; Brigida I; Casiraghi M; Scaramuzza S; Cappelli B; Cassani B; Ferrua F; Aker M; Slavin S; Scarselli A; Cancrini C; Marktel S; Grazia Roncarolo M; Aiuti A
J Allergy Clin Immunol; 2011 Jun; 127(6):1368-75.e8. PubMed ID: 21477850
[TBL] [Abstract][Full Text] [Related]
31. Gene therapy for primary immunodeficiencies: Part 1.
Cavazzana-Calvo M; Fischer A; Hacein-Bey-Abina S; Aiuti A
Curr Opin Immunol; 2012 Oct; 24(5):580-4. PubMed ID: 22981681
[TBL] [Abstract][Full Text] [Related]
32. Gene therapy for primary immunodeficiencies.
Thrasher AJ
Immunol Allergy Clin North Am; 2008 May; 28(2):457-71, xi. PubMed ID: 18424342
[TBL] [Abstract][Full Text] [Related]
33. [Substitution therapy with hematopoietic progenitors in the primary immunodeficiencies].
Español T
Allergol Immunopathol (Madr); 2001; 29(3):118-21. PubMed ID: 11434885
[TBL] [Abstract][Full Text] [Related]
34. Gene therapy for severe combined immunodeficiencies and beyond.
Fischer A; Hacein-Bey-Abina S
J Exp Med; 2020 Jan; 217(2):. PubMed ID: 31826240
[TBL] [Abstract][Full Text] [Related]
35. Primary T-cell immunodeficiencies.
Fischer A
Curr Opin Immunol; 1993 Aug; 5(4):569-78. PubMed ID: 8216933
[TBL] [Abstract][Full Text] [Related]
36. Gene Therapy for the Treatment of Primary Immune Deficiencies.
Kuo CY; Kohn DB
Curr Allergy Asthma Rep; 2016 May; 16(5):39. PubMed ID: 27056559
[TBL] [Abstract][Full Text] [Related]
37. [Gene therapy of primary immunodeficiencies. Present and future].
Serrano F; Laín de Lera T; González MA; García MJ; Abad JL; Bernad A
Sangre (Barc); 1999 Apr; 44(2):143-53. PubMed ID: 10382324
[No Abstract] [Full Text] [Related]
38. Progress in primary immunodeficiency.
Matsumoto S; Sakiyama Y; Ariga T; Gallagher R; Taguchi Y
Immunol Today; 1992 Jan; 13(1):4-5. PubMed ID: 1739431
[TBL] [Abstract][Full Text] [Related]
39. Gene therapy of lymphoid primary immunodeficiencies.
Fischer A
Curr Opin Pediatr; 2000 Dec; 12(6):557-62. PubMed ID: 11106275
[TBL] [Abstract][Full Text] [Related]
40. Long-term and real-world safety and efficacy of retroviral gene therapy for adenosine deaminase deficiency.
Migliavacca M; Barzaghi F; Fossati C; Rancoita PMV; Gabaldo M; Dionisio F; Giannelli S; Salerio FA; Ferrua F; Tucci F; Calbi V; Gallo V; Recupero S; Consiglieri G; Pajno R; Sambuco M; Priolo A; Ferri C; Garella V; Monti I; Silvani P; Darin S; Casiraghi M; Corti A; Zancan S; Levi M; Cesana D; Carlucci F; Pituch-Noworolska A; AbdElaziz D; Baumann U; Finocchi A; Cancrini C; Ladogana S; Meinhardt A; Meyts I; Montin D; Notarangelo LD; Porta F; Pasquet M; Speckmann C; Stepensky P; Tommasini A; Rabusin M; Karakas Z; Galicchio M; Leonardi L; Duse M; Guner SN; Di Serio C; Ciceri F; Bernardo ME; Aiuti A; Cicalese MP
Nat Med; 2024 Feb; 30(2):488-497. PubMed ID: 38355973
[TBL] [Abstract][Full Text] [Related]
[Previous] [Next] [New Search]