These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.


BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

200 related articles for article (PubMed ID: 15649123)

  • 1. Treatment of the mouse model of mucopolysaccharidosis type IIIB with lentiviral-NAGLU vector.
    Di Natale P; Di Domenico C; Gargiulo N; Castaldo S; Gonzalez Y Reyero E; Mithbaokar P; De Felice M; Follenzi A; Naldini L; Villani GR
    Biochem J; 2005 Jun; 388(Pt 2):639-46. PubMed ID: 15649123
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Macrophage enzyme and reduced inflammation drive brain correction of mucopolysaccharidosis IIIB by stem cell gene therapy.
    Holley RJ; Ellison SM; Fil D; O'Leary C; McDermott J; Senthivel N; Langford-Smith AWW; Wilkinson FL; D'Souza Z; Parker H; Liao A; Rowlston S; Gleitz HFE; Kan SH; Dickson PI; Bigger BW
    Brain; 2018 Jan; 141(1):99-116. PubMed ID: 29186350
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Improved behavior and neuropathology in the mouse model of Sanfilippo type IIIB disease after adeno-associated virus-mediated gene transfer in the striatum.
    Cressant A; Desmaris N; Verot L; Bréjot T; Froissart R; Vanier MT; Maire I; Heard JM
    J Neurosci; 2004 Nov; 24(45):10229-39. PubMed ID: 15537895
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Correction of mucopolysaccharidosis type IIIb fibroblasts by lentiviral vector-mediated gene transfer.
    Villani GR; Follenzi A; Vanacore B; Di Domenico C; Naldini L; Di Natale P
    Biochem J; 2002 Jun; 364(Pt 3):747-53. PubMed ID: 12049639
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Gene therapy for a mucopolysaccharidosis type I murine model with lentiviral-IDUA vector.
    Di Domenico C; Villani GR; Di Napoli D; Reyero EG; Lombardo A; Naldini L; Di Natale P
    Hum Gene Ther; 2005 Jan; 16(1):81-90. PubMed ID: 15703491
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Retrovirally transduced bone marrow has a therapeutic effect on brain in the mouse model of mucopolysaccharidosis IIIB.
    Zheng Y; Ryazantsev S; Ohmi K; Zhao HZ; Rozengurt N; Kohn DB; Neufeld EF
    Mol Genet Metab; 2004 Aug; 82(4):286-95. PubMed ID: 15308126
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Intracranial gene delivery of LV-NAGLU vector corrects neuropathology in murine MPS IIIB.
    Di Domenico C; Villani GR; Di Napoli D; Nusco E; Calì G; Nitsch L; Di Natale P
    Am J Med Genet A; 2009 Jun; 149A(6):1209-18. PubMed ID: 19449420
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Biochemical evaluation of intracerebroventricular rhNAGLU-IGF2 enzyme replacement therapy in neonatal mice with Sanfilippo B syndrome.
    Kan SH; Elsharkawi I; Le SQ; Prill H; Mangini L; Cooper JD; Lawrence R; Sands MS; Crawford BE; Dickson PI
    Mol Genet Metab; 2021 Jun; 133(2):185-192. PubMed ID: 33839004
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Restoration of central nervous system alpha-N-acetylglucosaminidase activity and therapeutic benefits in mucopolysaccharidosis IIIB mice by a single intracisternal recombinant adeno-associated viral type 2 vector delivery.
    Fu H; DiRosario J; Kang L; Muenzer J; McCarty DM
    J Gene Med; 2010 Jul; 12(7):624-33. PubMed ID: 20603889
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Short-term enzyme replacement in the murine model of Sanfilippo syndrome type B.
    Yu WH; Zhao KW; Ryazantsev S; Rozengurt N; Neufeld EF
    Mol Genet Metab; 2000 Dec; 71(4):573-80. PubMed ID: 11136549
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Disease correction by combined neonatal intracranial AAV and systemic lentiviral gene therapy in Sanfilippo Syndrome type B mice.
    Heldermon CD; Qin EY; Ohlemiller KK; Herzog ED; Brown JR; Vogler C; Hou W; Orrock JL; Crawford BE; Sands MS
    Gene Ther; 2013 Sep; 20(9):913-21. PubMed ID: 23535899
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Neurological correction of lysosomal storage in a mucopolysaccharidosis IIIB mouse model by adeno-associated virus-mediated gene delivery.
    Fu H; Samulski RJ; McCown TJ; Picornell YJ; Fletcher D; Muenzer J
    Mol Ther; 2002 Jan; 5(1):42-9. PubMed ID: 11786044
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Cell-Mediated Immunity to NAGLU Transgene Following Intracerebral Gene Therapy in Children With Mucopolysaccharidosis Type IIIB Syndrome.
    Gougeon ML; Poirier-Beaudouin B; Ausseil J; Zérah M; Artaud C; Heard JM; Deiva K; Tardieu M
    Front Immunol; 2021; 12():655478. PubMed ID: 34040605
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Disease correction in mucopolysaccharidosis type IIIB mice by intraparenchymal or cisternal delivery of a capsid modified AAV8 codon-optimized NAGLU vector.
    Rouse CJ; Hawkins K; Kabbej N; Dalugdug J; Kunta A; Kim MJ; Someya S; Herbst Z; Gelb M; Dinelli I; Butterworth E; Falk DJ; Rosenkrantz E; Elmohd H; Khaledi H; Mowafy S; Ashby F; Heldermon CD
    Hum Mol Genet; 2023 Jan; 32(3):417-430. PubMed ID: 35997776
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Processing of mutant N-acetyl-α-glucosaminidase in mucopolysaccharidosis type IIIB fibroblasts cultured at low temperature.
    Meijer OLM; Te Brinke H; Ofman R; IJlst L; Wijburg FA; van Vlies N
    Mol Genet Metab; 2017 Sep; 122(1-2):100-106. PubMed ID: 28751108
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Near-Complete Correction of Profound Metabolomic Impairments Corresponding to Functional Benefit in MPS IIIB Mice after IV rAAV9-hNAGLU Gene Delivery.
    Fu H; Meadows AS; Ware T; Mohney RP; McCarty DM
    Mol Ther; 2017 Mar; 25(3):792-802. PubMed ID: 28143737
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Mouse model of Sanfilippo syndrome type B produced by targeted disruption of the gene encoding alpha-N-acetylglucosaminidase.
    Li HH; Yu WH; Rozengurt N; Zhao HZ; Lyons KM; Anagnostaras S; Fanselow MS; Suzuki K; Vanier MT; Neufeld EF
    Proc Natl Acad Sci U S A; 1999 Dec; 96(25):14505-10. PubMed ID: 10588735
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Serum MIP-1 alpha level: a biomarker for the follow-up of lentiviral therapy in mucopolysaccharidosis IIIB mice.
    Di Natale P; Di Domenico C; Di Napoli D
    J Inherit Metab Dis; 2010 Apr; 33(2):159-65. PubMed ID: 20162365
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Molecular defects in Sanfilippo syndrome type B (mucopolysaccharidosis IIIB).
    Beesley CE; Jackson M; Young EP; Vellodi A; Winchester BG
    J Inherit Metab Dis; 2005; 28(5):759-67. PubMed ID: 16151907
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Molecular basis of mucopolysaccharidosis type IIIB in emu (Dromaius novaehollandiae): an avian model of Sanfilippo syndrome type B.
    Aronovich EL; Johnston JM; Wang P; Giger U; Whitley CB
    Genomics; 2001 Jun; 74(3):299-305. PubMed ID: 11414757
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 10.