479 related articles for article (PubMed ID: 16304358)
1. Gene Therapy for beta-thalassemia.
Malik P; Arumugam PI
Hematology Am Soc Hematol Educ Program; 2005; ():45-50. PubMed ID: 16304358
[TBL] [Abstract][Full Text] [Related]
2. Successful correction of the human Cooley's anemia beta-thalassemia major phenotype using a lentiviral vector flanked by the chicken hypersensitive site 4 chromatin insulator.
Malik P; Arumugam PI; Yee JK; Puthenveetil G
Ann N Y Acad Sci; 2005; 1054():238-49. PubMed ID: 16339671
[TBL] [Abstract][Full Text] [Related]
3. Improved human beta-globin expression from self-inactivating lentiviral vectors carrying the chicken hypersensitive site-4 (cHS4) insulator element.
Arumugam PI; Scholes J; Perelman N; Xia P; Yee JK; Malik P
Mol Ther; 2007 Oct; 15(10):1863-71. PubMed ID: 17622240
[TBL] [Abstract][Full Text] [Related]
4. Comparative analysis of FV vectors with human α- or β-globin gene regulatory elements for the correction of β-thalassemia.
Morianos I; Siapati EK; Pongas G; Vassilopoulos G
Gene Ther; 2012 Mar; 19(3):303-11. PubMed ID: 21734726
[TBL] [Abstract][Full Text] [Related]
5. Genetic therapy for beta-thalassemia: from the bench to the bedside.
Arumugam P; Malik P
Hematology Am Soc Hematol Educ Program; 2010; 2010():445-50. PubMed ID: 21239833
[TBL] [Abstract][Full Text] [Related]
6. Permanent and panerythroid correction of murine beta thalassemia by multiple lentiviral integration in hematopoietic stem cells.
Imren S; Payen E; Westerman KA; Pawliuk R; Fabry ME; Eaves CJ; Cavilla B; Wadsworth LD; Beuzard Y; Bouhassira EE; Russell R; London IM; Nagel RL; Leboulch P; Humphries RK
Proc Natl Acad Sci U S A; 2002 Oct; 99(22):14380-5. PubMed ID: 12391330
[TBL] [Abstract][Full Text] [Related]
7. The degree of phenotypic correction of murine beta -thalassemia intermedia following lentiviral-mediated transfer of a human gamma-globin gene is influenced by chromosomal position effects and vector copy number.
Persons DA; Hargrove PW; Allay ER; Hanawa H; Nienhuis AW
Blood; 2003 Mar; 101(6):2175-83. PubMed ID: 12411297
[TBL] [Abstract][Full Text] [Related]
8. Improved Titer and Gene Transfer by Lentiviral Vectors Using Novel, Small β-Globin Locus Control Region Elements.
Morgan RA; Unti MJ; Aleshe B; Brown D; Osborne KS; Koziol C; Ayoub PG; Smith OB; O'Brien R; Tam C; Miyahira E; Ruiz M; Quintos JP; Senadheera S; Hollis RP; Kohn DB
Mol Ther; 2020 Jan; 28(1):328-340. PubMed ID: 31628051
[TBL] [Abstract][Full Text] [Related]
9. Successful correction of the human beta-thalassemia major phenotype using a lentiviral vector.
Puthenveetil G; Scholes J; Carbonell D; Qureshi N; Xia P; Zeng L; Li S; Yu Y; Hiti AL; Yee JK; Malik P
Blood; 2004 Dec; 104(12):3445-53. PubMed ID: 15292064
[TBL] [Abstract][Full Text] [Related]
10. Progress toward the genetic treatment of the beta-thalassemias.
Sadelain M; Lisowski L; Samakoglu S; Rivella S; May C; Riviere I
Ann N Y Acad Sci; 2005; 1054():78-91. PubMed ID: 16339654
[TBL] [Abstract][Full Text] [Related]
11. Extended beta-globin locus control region elements promote consistent therapeutic expression of a gamma-globin lentiviral vector in murine beta-thalassemia.
Hanawa H; Hargrove PW; Kepes S; Srivastava DK; Nienhuis AW; Persons DA
Blood; 2004 Oct; 104(8):2281-90. PubMed ID: 15198957
[TBL] [Abstract][Full Text] [Related]
12. The new self-inactivating lentiviral vector for thalassemia gene therapy combining two HPFH activating elements corrects human thalassemic hematopoietic stem cells.
Papanikolaou E; Georgomanoli M; Stamateris E; Panetsos F; Karagiorga M; Tsaftaridis P; Graphakos S; Anagnou NP
Hum Gene Ther; 2012 Jan; 23(1):15-31. PubMed ID: 21875313
[TBL] [Abstract][Full Text] [Related]
13. Development of virus vectors for gene therapy of beta chain hemoglobinopathies: flanking with a chromatin insulator reduces gamma-globin gene silencing in vivo.
Emery DW; Yannaki E; Tubb J; Nishino T; Li Q; Stamatoyannopoulos G
Blood; 2002 Sep; 100(6):2012-9. PubMed ID: 12200360
[TBL] [Abstract][Full Text] [Related]
14. Hematopoietic stem cell gene transfer for the treatment of hemoglobin disorders.
Persons DA
Hematology Am Soc Hematol Educ Program; 2009; ():690-7. PubMed ID: 20008255
[TBL] [Abstract][Full Text] [Related]
15. Gene Therapy of the β-Hemoglobinopathies by Lentiviral Transfer of the β(A(T87Q))-Globin Gene.
Negre O; Eggimann AV; Beuzard Y; Ribeil JA; Bourget P; Borwornpinyo S; Hongeng S; Hacein-Bey S; Cavazzana M; Leboulch P; Payen E
Hum Gene Ther; 2016 Feb; 27(2):148-65. PubMed ID: 26886832
[TBL] [Abstract][Full Text] [Related]
16. In vivo selection of genetically modified erythroblastic progenitors leads to long-term correction of beta-thalassemia.
Miccio A; Cesari R; Lotti F; Rossi C; Sanvito F; Ponzoni M; Routledge SJ; Chow CM; Antoniou MN; Ferrari G
Proc Natl Acad Sci U S A; 2008 Jul; 105(30):10547-52. PubMed ID: 18650378
[TBL] [Abstract][Full Text] [Related]
17. A phase I/II clinical trial of beta-globin gene therapy for beta-thalassemia.
Bank A; Dorazio R; Leboulch P
Ann N Y Acad Sci; 2005; 1054():308-16. PubMed ID: 16339679
[TBL] [Abstract][Full Text] [Related]
18. Therapeutic hemoglobin levels after gene transfer in β-thalassemia mice and in hematopoietic cells of β-thalassemia and sickle cells disease patients.
Breda L; Casu C; Gardenghi S; Bianchi N; Cartegni L; Narla M; Yazdanbakhsh K; Musso M; Manwani D; Little J; Gardner LB; Kleinert DA; Prus E; Fibach E; Grady RW; Giardina PJ; Gambari R; Rivella S
PLoS One; 2012; 7(3):e32345. PubMed ID: 22479321
[TBL] [Abstract][Full Text] [Related]
19. The beta-globin locus control region versus gene therapy vectors: a struggle for expression.
Ellis J; Pannell D
Clin Genet; 2001 Jan; 59(1):17-24. PubMed ID: 11168020
[TBL] [Abstract][Full Text] [Related]
20. Evaluation of optimal expression cassette in retrovirus vector for beta-thalassemia gene therapy.
Dong WJ; Li B; Liu DP; Zu ZX; Li J; Hao DL; Liu G; Guo ZC; Liang CC
Mol Biotechnol; 2003 Jun; 24(2):127-40. PubMed ID: 12746554
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]