480 related articles for article (PubMed ID: 16464640)
1. Sustained FVIII expression and phenotypic correction of hemophilia A in neonatal mice using an endothelial-targeted sleeping beauty transposon.
Liu L; Mah C; Fletcher BS
Mol Ther; 2006 May; 13(5):1006-15. PubMed ID: 16464640
[TBL] [Abstract][Full Text] [Related]
2. Phenotypic correction and long-term expression of factor VIII in hemophilic mice by immunotolerization and nonviral gene transfer using the Sleeping Beauty transposon system.
Ohlfest JR; Frandsen JL; Fritz S; Lobitz PD; Perkinson SG; Clark KJ; Nelsestuen G; Key NS; McIvor RS; Hackett PB; Largaespada DA
Blood; 2005 Apr; 105(7):2691-8. PubMed ID: 15576475
[TBL] [Abstract][Full Text] [Related]
3. Phenotype correction of hemophilia A mice by spliceosome-mediated RNA trans-splicing.
Chao H; Mansfield SG; Bartel RC; Hiriyanna S; Mitchell LG; Garcia-Blanco MA; Walsh CE
Nat Med; 2003 Aug; 9(8):1015-9. PubMed ID: 12847523
[TBL] [Abstract][Full Text] [Related]
4. Heterogeneity of the immune response to adenovirus-mediated factor VIII gene therapy in different inbred hemophilic mouse strains.
Rawle FE; Shi CX; Brown B; McKinven A; Tinlin S; Graham FL; Hough C; Lillicrap D
J Gene Med; 2004 Dec; 6(12):1358-68. PubMed ID: 15493040
[TBL] [Abstract][Full Text] [Related]
5. Indoleamine 2,3-dioxygenase attenuates inhibitor development in gene-therapy-treated hemophilia A mice.
Liu L; Liu H; Mah C; Fletcher BS
Gene Ther; 2009 Jun; 16(6):724-33. PubMed ID: 19262614
[TBL] [Abstract][Full Text] [Related]
6. Sustained expansion and transgene expression of coagulation factor VIII-transduced cord blood-derived endothelial progenitor cells.
Herder C; Tonn T; Oostendorp R; Becker S; Keller U; Peschel C; Grez M; Seifried E
Arterioscler Thromb Vasc Biol; 2003 Dec; 23(12):2266-72. PubMed ID: 14551158
[TBL] [Abstract][Full Text] [Related]
7. Gene therapy for hemophilia A.
Connelly S; Kaleko M
Thromb Haemost; 1997 Jul; 78(1):31-6. PubMed ID: 9198123
[TBL] [Abstract][Full Text] [Related]
8. Phenotype correction of hemophilia A mice with adeno-associated virus vectors carrying the B domain-deleted canine factor VIII gene.
Ishiwata A; Mimuro J; Kashiwakura Y; Niimura M; Takano K; Ohmori T; Madoiwa S; Mizukami H; Okada T; Naka H; Yoshioka A; Ozawa K; Sakata Y
Thromb Res; 2006; 118(5):627-35. PubMed ID: 16371232
[TBL] [Abstract][Full Text] [Related]
9. Recombinant factor VIII expression in hematopoietic cells following lentiviral transduction.
Tiede A; Eder M; von Depka M; Battmer K; Luther S; Kiem HP; Ganser A; Scherr M
Gene Ther; 2003 Oct; 10(22):1917-25. PubMed ID: 14502221
[TBL] [Abstract][Full Text] [Related]
10. Evaluation of an adenoviral vector encoding full-length human factor VIII in hemophiliac mice.
Connelly S; Andrews JL; Gallo-Penn AM; Tagliavacca L; Kaufman RJ; Kaleko M
Thromb Haemost; 1999 Feb; 81(2):234-9. PubMed ID: 10063998
[TBL] [Abstract][Full Text] [Related]
11. Gene therapy strategies for hemophilia: benefits versus risks.
Petrus I; Chuah M; VandenDriessche T
J Gene Med; 2010 Oct; 12(10):797-809. PubMed ID: 20848668
[TBL] [Abstract][Full Text] [Related]
12. [Molecular genetics of hemophilia A].
De Brasi CD; Slavutsky IR; Larripa IB
Medicina (B Aires); 1996; 56(5 Pt 1):509-17. PubMed ID: 9239887
[TBL] [Abstract][Full Text] [Related]
13. FVIII gene delivery by muscle electroporation corrects murine hemophilia A.
Long YC; Jaichandran S; Ho LP; Tien SL; Tan SY; Kon OL
J Gene Med; 2005 Apr; 7(4):494-505. PubMed ID: 15521095
[TBL] [Abstract][Full Text] [Related]
14. Nanocapsule-delivered Sleeping Beauty mediates therapeutic Factor VIII expression in liver sinusoidal endothelial cells of hemophilia A mice.
Kren BT; Unger GM; Sjeklocha L; Trossen AA; Korman V; Diethelm-Okita BM; Reding MT; Steer CJ
J Clin Invest; 2009 Jul; 119(7):2086-99. PubMed ID: 19509468
[TBL] [Abstract][Full Text] [Related]
15. Clinical gene transfer studies for hemophilia A.
Chuah MK; Collen D; VandenDriessche T
Semin Thromb Hemost; 2004 Apr; 30(2):249-56. PubMed ID: 15118936
[TBL] [Abstract][Full Text] [Related]
16. Expression of human coagulation factor VIII in adipocytes transduced with the simian immunodeficiency virus agmTYO1-based vector for hemophilia A gene therapy.
Ogata K; Mimuro J; Kikuchi J; Tabata T; Ueda Y; Naito M; Madoiwa S; Takano K; Hasegawa M; Ozawa K; Sakata Y
Gene Ther; 2004 Feb; 11(3):253-9. PubMed ID: 14737084
[TBL] [Abstract][Full Text] [Related]
17. Hemophilia A--from basic science to clinical practice.
Klinge J; Ananyeva NM; Hauser CA; Saenko EL
Semin Thromb Hemost; 2002 Jun; 28(3):309-22. PubMed ID: 12098093
[TBL] [Abstract][Full Text] [Related]
18. Preclinical animal models for hemophilia gene therapy: predictive value and limitations.
Rawle FE; Lillicrap D
Semin Thromb Hemost; 2004 Apr; 30(2):205-13. PubMed ID: 15118932
[TBL] [Abstract][Full Text] [Related]
19. Gene therapy for hemophilia.
Lynch CM
Curr Opin Mol Ther; 1999 Aug; 1(4):493-9. PubMed ID: 11713765
[TBL] [Abstract][Full Text] [Related]
20. Retroviral modification of mesenchymal stem cells for gene therapy of hemophilia.
Doering CB
Methods Mol Biol; 2008; 433():203-12. PubMed ID: 18679625
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]
