345 related articles for article (PubMed ID: 16819550)
1. rAAV6-microdystrophin preserves muscle function and extends lifespan in severely dystrophic mice.
Gregorevic P; Allen JM; Minami E; Blankinship MJ; Haraguchi M; Meuse L; Finn E; Adams ME; Froehner SC; Murry CE; Chamberlain JS
Nat Med; 2006 Jul; 12(7):787-9. PubMed ID: 16819550
[TBL] [Abstract][Full Text] [Related]
2. Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy.
Le Guiner C; Servais L; Montus M; Larcher T; Fraysse B; Moullec S; Allais M; François V; Dutilleul M; Malerba A; Koo T; Thibaut JL; Matot B; Devaux M; Le Duff J; Deschamps JY; Barthelemy I; Blot S; Testault I; Wahbi K; Ederhy S; Martin S; Veron P; Georger C; Athanasopoulos T; Masurier C; Mingozzi F; Carlier P; Gjata B; Hogrel JY; Adjali O; Mavilio F; Voit T; Moullier P; Dickson G
Nat Commun; 2017 Jul; 8():16105. PubMed ID: 28742067
[TBL] [Abstract][Full Text] [Related]
3. C-terminal-truncated microdystrophin recruits dystrobrevin and syntrophin to the dystrophin-associated glycoprotein complex and reduces muscular dystrophy in symptomatic utrophin/dystrophin double-knockout mice.
Yue Y; Liu M; Duan D
Mol Ther; 2006 Jul; 14(1):79-87. PubMed ID: 16563874
[TBL] [Abstract][Full Text] [Related]
4. Codon and mRNA sequence optimization of microdystrophin transgenes improves expression and physiological outcome in dystrophic mdx mice following AAV2/8 gene transfer.
Foster H; Sharp PS; Athanasopoulos T; Trollet C; Graham IR; Foster K; Wells DJ; Dickson G
Mol Ther; 2008 Nov; 16(11):1825-32. PubMed ID: 18766174
[TBL] [Abstract][Full Text] [Related]
5. Delivery of AAV2/9-microdystrophin genes incorporating helix 1 of the coiled-coil motif in the C-terminal domain of dystrophin improves muscle pathology and restores the level of α1-syntrophin and α-dystrobrevin in skeletal muscles of mdx mice.
Koo T; Malerba A; Athanasopoulos T; Trollet C; Boldrin L; Ferry A; Popplewell L; Foster H; Foster K; Dickson G
Hum Gene Ther; 2011 Nov; 22(11):1379-88. PubMed ID: 21453126
[TBL] [Abstract][Full Text] [Related]
6. Triple trans-splicing adeno-associated virus vectors capable of transferring the coding sequence for full-length dystrophin protein into dystrophic mice.
Koo T; Popplewell L; Athanasopoulos T; Dickson G
Hum Gene Ther; 2014 Feb; 25(2):98-108. PubMed ID: 24191945
[TBL] [Abstract][Full Text] [Related]
7. Intra-amniotic rAAV-mediated microdystrophin gene transfer improves canine X-linked muscular dystrophy and may induce immune tolerance.
Hayashita-Kinoh H; Yugeta N; Okada H; Nitahara-Kasahara Y; Chiyo T; Okada T; Takeda S
Mol Ther; 2015 Apr; 23(4):627-37. PubMed ID: 25586688
[TBL] [Abstract][Full Text] [Related]
8. Microutrophin delivery through rAAV6 increases lifespan and improves muscle function in dystrophic dystrophin/utrophin-deficient mice.
Odom GL; Gregorevic P; Allen JM; Finn E; Chamberlain JS
Mol Ther; 2008 Sep; 16(9):1539-45. PubMed ID: 18665159
[TBL] [Abstract][Full Text] [Related]
9. rAAV6-microdystrophin rescues aberrant Golgi complex organization in mdx skeletal muscles.
Percival JM; Gregorevic P; Odom GL; Banks GB; Chamberlain JS; Froehner SC
Traffic; 2007 Oct; 8(10):1424-39. PubMed ID: 17714427
[TBL] [Abstract][Full Text] [Related]
10. Herpes simplex virus VP22 enhances adenovirus-mediated microdystrophin gene transfer to skeletal muscles in dystrophin-deficient (mdx) mice.
Xiong F; Xiao S; Peng F; Zheng H; Yu M; Ruan Y; Li W; Shang Y; Zhao C; Zhou W; Chen H; Chamberlain JS; Fang L; Zhang C
Hum Gene Ther; 2007 Jun; 18(6):490-501. PubMed ID: 17550336
[TBL] [Abstract][Full Text] [Related]
11. Injection of a recombinant AAV serotype 2 into canine skeletal muscles evokes strong immune responses against transgene products.
Yuasa K; Yoshimura M; Urasawa N; Ohshima S; Howell JM; Nakamura A; Hijikata T; Miyagoe-Suzuki Y; Takeda S
Gene Ther; 2007 Sep; 14(17):1249-60. PubMed ID: 17581597
[TBL] [Abstract][Full Text] [Related]
12. Muscle function recovery in golden retriever muscular dystrophy after AAV1-U7 exon skipping.
Vulin A; Barthélémy I; Goyenvalle A; Thibaud JL; Beley C; Griffith G; Benchaouir R; le Hir M; Unterfinger Y; Lorain S; Dreyfus P; Voit T; Carlier P; Blot S; Garcia L
Mol Ther; 2012 Nov; 20(11):2120-33. PubMed ID: 22968479
[TBL] [Abstract][Full Text] [Related]
13. Phenotypic improvement of dystrophic muscles by rAAV/microdystrophin vectors is augmented by Igf1 codelivery.
Abmayr S; Gregorevic P; Allen JM; Chamberlain JS
Mol Ther; 2005 Sep; 12(3):441-50. PubMed ID: 16099410
[TBL] [Abstract][Full Text] [Related]
14. Dystrophin Gene-Editing Stability Is Dependent on Dystrophin Levels in Skeletal but Not Cardiac Muscles.
Bengtsson NE; Tasfaout H; Hauschka SD; Chamberlain JS
Mol Ther; 2021 Mar; 29(3):1070-1085. PubMed ID: 33160075
[TBL] [Abstract][Full Text] [Related]
15. Rescue of dystrophic muscle through U7 snRNA-mediated exon skipping.
Goyenvalle A; Vulin A; Fougerousse F; Leturcq F; Kaplan JC; Garcia L; Danos O
Science; 2004 Dec; 306(5702):1796-9. PubMed ID: 15528407
[TBL] [Abstract][Full Text] [Related]
16. AAV vector-mediated microdystrophin expression in a relatively small percentage of mdx myofibers improved the mdx phenotype.
Yoshimura M; Sakamoto M; Ikemoto M; Mochizuki Y; Yuasa K; Miyagoe-Suzuki Y; Takeda S
Mol Ther; 2004 Nov; 10(5):821-8. PubMed ID: 15509500
[TBL] [Abstract][Full Text] [Related]
17. Micro-Dystrophin Gene Therapy Goes Systemic in Duchenne Muscular Dystrophy Patients.
Duan D
Hum Gene Ther; 2018 Jul; 29(7):733-736. PubMed ID: 29463117
[TBL] [Abstract][Full Text] [Related]
18. Codon optimization of the microdystrophin gene for Duchene muscular dystrophy gene therapy.
Athanasopoulos T; Foster H; Foster K; Dickson G
Methods Mol Biol; 2011; 709():21-37. PubMed ID: 21194019
[TBL] [Abstract][Full Text] [Related]
19. Recombinant adeno-associated viral (rAAV) vectors as therapeutic tools for Duchenne muscular dystrophy (DMD).
Athanasopoulos T; Graham IR; Foster H; Dickson G
Gene Ther; 2004 Oct; 11 Suppl 1():S109-21. PubMed ID: 15454965
[TBL] [Abstract][Full Text] [Related]
20. Genetic correction of dystrophin deficiency and skeletal muscle remodeling in adult MDX mouse via transplantation of retroviral producer cells.
Fassati A; Wells DJ; Sgro Serpente PA; Walsh FS; Brown SC; Strong PN; Dickson G
J Clin Invest; 1997 Aug; 100(3):620-8. PubMed ID: 9239410
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]
