259 related articles for article (PubMed ID: 16871228)
21. Increasing sulfatide synthesis in myelin-forming cells of arylsulfatase A-deficient mice causes demyelination and neurological symptoms reminiscent of human metachromatic leukodystrophy.
Ramakrishnan H; Hedayati KK; Lüllmann-Rauch R; Wessig C; Fewou SN; Maier H; Goebel HH; Gieselmann V; Eckhardt M
J Neurosci; 2007 Aug; 27(35):9482-90. PubMed ID: 17728461
[TBL] [Abstract][Full Text] [Related]
22. Telencephalic histopathology and changes in behavioural and neural plasticity in a murine model for metachromatic leukodystrophy.
Faldini E; Stroobants S; Lüllmann-Rauch R; Eckhardt M; Gieselmann V; Balschun D; D'Hooge R
Behav Brain Res; 2011 Sep; 222(2):309-14. PubMed ID: 21459117
[TBL] [Abstract][Full Text] [Related]
23. Generation of Human Induced Pluripotent Stem Cell-Derived Bona Fide Neural Stem Cells for Ex Vivo Gene Therapy of Metachromatic Leukodystrophy.
Meneghini V; Frati G; Sala D; De Cicco S; Luciani M; Cavazzin C; Paulis M; Mentzen W; Morena F; Giannelli S; Sanvito F; Villa A; Bulfone A; Broccoli V; Martino S; Gritti A
Stem Cells Transl Med; 2017 Feb; 6(2):352-368. PubMed ID: 28191778
[TBL] [Abstract][Full Text] [Related]
24. Modest phenotypic improvements in ASA-deficient mice with only one UDP-galactose:ceramide-galactosyltransferase gene.
Franken S; Wittke D; Mansson JE; D'Hooge R; De Deyn PP; Lüllmann-Rauch R; Matzner U; Gieselmann V
Lipids Health Dis; 2006 Aug; 5():21. PubMed ID: 16893448
[TBL] [Abstract][Full Text] [Related]
25. Multipotential neural precursors transplanted into the metachromatic leukodystrophy brain fail to generate oligodendrocytes but contribute to limit brain dysfunction.
Givogri MI; Bottai D; Zhu HL; Fasano S; Lamorte G; Brambilla R; Vescovi A; Wrabetz L; Bongarzone E
Dev Neurosci; 2008; 30(5):340-57. PubMed ID: 18667806
[TBL] [Abstract][Full Text] [Related]
26. Retroviral gene transfer and sustained expression of human arylsulfatase A.
Learish R; Ohashi T; Robbins PA; Bahnson A; Boggs SS; Patrene K; Schwartz BE; Gieselmann V; Barranger JA
Gene Ther; 1996 Apr; 3(4):343-9. PubMed ID: 8732166
[TBL] [Abstract][Full Text] [Related]
27. Non-inhibitory antibodies impede lysosomal storage reduction during enzyme replacement therapy of a lysosomal storage disease.
Matzner U; Matthes F; Weigelt C; Andersson C; Eistrup C; Fogh J; Gieselmann V
J Mol Med (Berl); 2008 Apr; 86(4):433-42. PubMed ID: 18360747
[TBL] [Abstract][Full Text] [Related]
28. Oligodendroglial progenitor cell therapy limits central neurological deficits in mice with metachromatic leukodystrophy.
Givogri MI; Galbiati F; Fasano S; Amadio S; Perani L; Superchi D; Morana P; Del Carro U; Marchesini S; Brambilla R; Wrabetz L; Bongarzone E
J Neurosci; 2006 Mar; 26(12):3109-19. PubMed ID: 16554462
[TBL] [Abstract][Full Text] [Related]
29. Genetics of metachromatic leukodystrophy.
Gieselmann V; Kreysing J; von Figura K
Gene Ther; 1994; 1 Suppl 1():S87. PubMed ID: 8542433
[TBL] [Abstract][Full Text] [Related]
30. Coexpression of formylglycine-generating enzyme is essential for synthesis and secretion of functional arylsulfatase A in a mouse model of metachromatic leukodystrophy.
Takakusaki Y; Hisayasu S; Hirai Y; Shimada T
Hum Gene Ther; 2005 Aug; 16(8):929-36. PubMed ID: 16076251
[TBL] [Abstract][Full Text] [Related]
31. Deletion of fatty acid amide hydrolase reduces lyso-sulfatide levels but exacerbates metachromatic leukodystrophy in mice.
Yaghootfam C; Gehrig B; Sylvester M; Gieselmann V; Matzner U
J Biol Chem; 2021 Sep; 297(3):101064. PubMed ID: 34375644
[TBL] [Abstract][Full Text] [Related]
32. Intracerebroventricular enzyme infusion corrects central nervous system pathology and dysfunction in a mouse model of metachromatic leukodystrophy.
Stroobants S; Gerlach D; Matthes F; Hartmann D; Fogh J; Gieselmann V; D'Hooge R; Matzner U
Hum Mol Genet; 2011 Jul; 20(14):2760-9. PubMed ID: 21515587
[TBL] [Abstract][Full Text] [Related]
33. Sulfatide storage in neurons causes hyperexcitability and axonal degeneration in a mouse model of metachromatic leukodystrophy.
Eckhardt M; Hedayati KK; Pitsch J; Lüllmann-Rauch R; Beck H; Fewou SN; Gieselmann V
J Neurosci; 2007 Aug; 27(34):9009-21. PubMed ID: 17715338
[TBL] [Abstract][Full Text] [Related]
34. Transduction of fibroblasts and CD34+ progenitors using a selectable retroviral vector containing cDNAs encoding arylsulfatase A and CD24.
Tsutsudaasano A; Migita M; Takahashi K; Shimada T
J Hum Genet; 2000; 45(1):18-23. PubMed ID: 10697958
[TBL] [Abstract][Full Text] [Related]
35. AAV1 mediated co-expression of formylglycine-generating enzyme and arylsulfatase a efficiently corrects sulfatide storage in a mouse model of metachromatic leukodystrophy.
Kurai T; Hisayasu S; Kitagawa R; Migita M; Suzuki H; Hirai Y; Shimada T
Mol Ther; 2007 Jan; 15(1):38-43. PubMed ID: 17164773
[TBL] [Abstract][Full Text] [Related]
36. Early signs of neurolipidosis-related behavioural alterations in a murine model of metachromatic leukodystrophy.
Stroobants S; Leroy T; Eckhardt M; Aerts JM; Berckmans D; D'Hooge R
Behav Brain Res; 2008 Jun; 189(2):306-16. PubMed ID: 18336930
[TBL] [Abstract][Full Text] [Related]
37. Embryonic stem cell-derived glial precursors as a vehicle for sulfamidase production in the MPS-IIIA mouse brain.
Robinson AJ; Zhao G; Rathjen J; Rathjen PD; Hutchinson RG; Eyre HJ; Hemsley KM; Hopwood JJ
Cell Transplant; 2010; 19(8):985-98. PubMed ID: 20350350
[TBL] [Abstract][Full Text] [Related]
38. Engineering embryonic stem cell derived glia for adenosine delivery.
Fedele DE; Koch P; Scheurer L; Simpson EM; Möhler H; Brüstle O; Boison D
Neurosci Lett; 2004 Nov; 370(2-3):160-5. PubMed ID: 15488315
[TBL] [Abstract][Full Text] [Related]
39. Enzyme replacement in the CSF to treat metachromatic leukodystrophy in mouse model using single intracerebroventricular injection of self-complementary AAV1 vector.
Hironaka K; Yamazaki Y; Hirai Y; Yamamoto M; Miyake N; Miyake K; Okada T; Morita A; Shimada T
Sci Rep; 2015 Aug; 5():13104. PubMed ID: 26283284
[TBL] [Abstract][Full Text] [Related]
40. Long-term correction of biochemical and neurological abnormalities in MLD mice model by neonatal systemic injection of an AAV serotype 9 vector.
Miyake N; Miyake K; Asakawa N; Yamamoto M; Shimada T
Gene Ther; 2014 Apr; 21(4):427-33. PubMed ID: 24572788
[TBL] [Abstract][Full Text] [Related]
[Previous] [Next] [New Search]