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5. Stable transgene expression in primitive human CD34+ hematopoietic stem/progenitor cells, using the Sleeping Beauty transposon system. Sumiyoshi T; Holt NG; Hollis RP; Ge S; Cannon PM; Crooks GM; Kohn DB Hum Gene Ther; 2009 Dec; 20(12):1607-26. PubMed ID: 19689196 [TBL] [Abstract][Full Text] [Related]
6. Counterselection and co-delivery of transposon and transposase functions for Sleeping Beauty-mediated transposition in cultured mammalian cells. Converse AD; Belur LR; Gori JL; Liu G; Amaya F; Aguilar-Cordova E; Hackett PB; McIvor RS Biosci Rep; 2004 Dec; 24(6):577-94. PubMed ID: 16158196 [TBL] [Abstract][Full Text] [Related]
7. Phenotypic correction and long-term expression of factor VIII in hemophilic mice by immunotolerization and nonviral gene transfer using the Sleeping Beauty transposon system. Ohlfest JR; Frandsen JL; Fritz S; Lobitz PD; Perkinson SG; Clark KJ; Nelsestuen G; Key NS; McIvor RS; Hackett PB; Largaespada DA Blood; 2005 Apr; 105(7):2691-8. PubMed ID: 15576475 [TBL] [Abstract][Full Text] [Related]
8. Comparison of ventricular and intravenous lentiviral-mediated gene therapy for murine MPS VII. Bielicki J; McIntyre C; Anson DS Mol Genet Metab; 2010 Dec; 101(4):370-82. PubMed ID: 20864369 [TBL] [Abstract][Full Text] [Related]
9. Liver-directed gene therapy using the sleeping beauty transposon system. Belur LR; McIvor RS; Wilber A Methods Mol Biol; 2008; 434():267-76. PubMed ID: 18470650 [TBL] [Abstract][Full Text] [Related]
11. Recombinant adeno-associated virus-mediated correction of lysosomal storage within the central nervous system of the adult mucopolysaccharidosis type VII mouse. Sferra TJ; Qu G; McNeely D; Rennard R; Clark KR; Lo WD; Johnson PR Hum Gene Ther; 2000 Mar; 11(4):507-19. PubMed ID: 10724030 [TBL] [Abstract][Full Text] [Related]
12. Transgene produces massive overexpression of human beta -glucuronidase in mice, lysosomal storage of enzyme, and strain-dependent tumors. Vogler C; Galvin N; Levy B; Grubb J; Jiang J; Zhou XY; Sly WS Proc Natl Acad Sci U S A; 2003 Mar; 100(5):2669-73. PubMed ID: 12591953 [TBL] [Abstract][Full Text] [Related]
13. Neonatal intramuscular injection with recombinant adeno-associated virus results in prolonged beta-glucuronidase expression in situ and correction of liver pathology in mucopolysaccharidosis type VII mice. Daly TM; Okuyama T; Vogler C; Haskins ME; Muzyczka N; Sands MS Hum Gene Ther; 1999 Jan; 10(1):85-94. PubMed ID: 10022533 [TBL] [Abstract][Full Text] [Related]
14. Targeted delivery of in situ PCR-amplified Sleeping Beauty transposon genes to cancer cells with lipid-based nanoparticle-like protocells. Ma K; Fu D; Yu D; Cui C; Wang L; Guo Z; Mao C Biomaterials; 2017 Mar; 121():55-63. PubMed ID: 28081459 [TBL] [Abstract][Full Text] [Related]
15. Helper-Independent Sleeping Beauty transposon-transposase vectors for efficient nonviral gene delivery and persistent gene expression in vivo. Mikkelsen JG; Yant SR; Meuse L; Huang Z; Xu H; Kay MA Mol Ther; 2003 Oct; 8(4):654-65. PubMed ID: 14529839 [TBL] [Abstract][Full Text] [Related]
16. Widespread biochemical correction of murine mucopolysaccharidosis type VII pathology by liver hydrodynamic plasmid delivery. Richard M; Arfi A; Seguin J; Gandolphe C; Scherman D Gene Ther; 2009 Jun; 16(6):746-56. PubMed ID: 19357715 [TBL] [Abstract][Full Text] [Related]
17. Platelets are efficient and protective depots for storage, distribution, and delivery of lysosomal enzyme in mice with Hurler syndrome. Dai M; Han J; El-Amouri SS; Brady RO; Pan D Proc Natl Acad Sci U S A; 2014 Feb; 111(7):2680-5. PubMed ID: 24550296 [TBL] [Abstract][Full Text] [Related]
18. Sleeping Beauty Transposon Vectors in Liver-directed Gene Delivery of LDLR and VLDLR for Gene Therapy of Familial Hypercholesterolemia. Turunen TA; Kurkipuro J; Heikura T; Vuorio T; Hytönen E; Izsvák Z; Ylä-Herttuala S Mol Ther; 2016 Mar; 24(3):620-35. PubMed ID: 26670130 [TBL] [Abstract][Full Text] [Related]
19. Excision of Sleeping Beauty transposons: parameters and applications to gene therapy. Liu G; Aronovich EL; Cui Z; Whitley CB; Hackett PB J Gene Med; 2004 May; 6(5):574-83. PubMed ID: 15133768 [TBL] [Abstract][Full Text] [Related]
20. Sleeping Beauty-baculovirus hybrid vectors for long-term gene expression in the eye. Turunen TA; Laakkonen JP; Alasaarela L; Airenne KJ; Ylä-Herttuala S J Gene Med; 2014; 16(1-2):40-53. PubMed ID: 24464652 [TBL] [Abstract][Full Text] [Related] [Next] [New Search]