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50. Hematopoietic stem cell gene therapy for the multisystemic lysosomal storage disorder cystinosis. Harrison F; Yeagy BA; Rocca CJ; Kohn DB; Salomon DR; Cherqui S Mol Ther; 2013 Feb; 21(2):433-44. PubMed ID: 23089735 [TBL] [Abstract][Full Text] [Related]
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