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2. Delivery of AAV2/9-microdystrophin genes incorporating helix 1 of the coiled-coil motif in the C-terminal domain of dystrophin improves muscle pathology and restores the level of α1-syntrophin and α-dystrobrevin in skeletal muscles of mdx mice. Koo T; Malerba A; Athanasopoulos T; Trollet C; Boldrin L; Ferry A; Popplewell L; Foster H; Foster K; Dickson G Hum Gene Ther; 2011 Nov; 22(11):1379-88. PubMed ID: 21453126 [TBL] [Abstract][Full Text] [Related]
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8. Mdx mice inducibly expressing dystrophin provide insights into the potential of gene therapy for duchenne muscular dystrophy. Ahmad A; Brinson M; Hodges BL; Chamberlain JS; Amalfitano A Hum Mol Genet; 2000 Oct; 9(17):2507-15. PubMed ID: 11030755 [TBL] [Abstract][Full Text] [Related]
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