BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

405 related articles for article (PubMed ID: 17716993)

  • 1. Restoration of the balanced alpha/beta-globin gene expression in beta654-thalassemia mice using combined RNAi and antisense RNA approach.
    Xie SY; Ren ZR; Zhang JZ; Guo XB; Wang QX; Wang S; Lin D; Gong XL; Li W; Huang SZ; Zeng F; Zeng YT
    Hum Mol Genet; 2007 Nov; 16(21):2616-25. PubMed ID: 17716993
    [TBL] [Abstract][Full Text] [Related]  

  • 2. A novel transgenic mouse model produced from lentiviral germline integration for the study of beta-thalassemia gene therapy.
    Li W; Xie S; Guo X; Gong X; Wang S; Lin D; Zhang J; Ren Z; Huang S; Zeng F; Zeng Y
    Haematologica; 2008 Mar; 93(3):356-62. PubMed ID: 18268280
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Amelioration of beta654-thalassemia in mouse model with the knockdown of aberrantly spliced beta-globin mRNA.
    Xie S; Li W; Ren Z; Zhang J; Guo X; Wang S; Huang S; Zeng F; Zeng YT
    J Genet Genomics; 2008 Oct; 35(10):595-601. PubMed ID: 18937916
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Successful correction of the human Cooley's anemia beta-thalassemia major phenotype using a lentiviral vector flanked by the chicken hypersensitive site 4 chromatin insulator.
    Malik P; Arumugam PI; Yee JK; Puthenveetil G
    Ann N Y Acad Sci; 2005; 1054():238-49. PubMed ID: 16339671
    [TBL] [Abstract][Full Text] [Related]  

  • 5. siRNA-mediated reduction of alpha-globin results in phenotypic improvements in beta-thalassemic cells.
    Voon HP; Wardan H; Vadolas J
    Haematologica; 2008 Aug; 93(8):1238-42. PubMed ID: 18556409
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Beta globin gene inhibition by antisense RNA transcripts.
    Xu L; Ferry AE; Monteiro C; Pace BS
    Gene Ther; 2000 Mar; 7(5):438-44. PubMed ID: 10694826
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Correction of β654-thalassaemia mice using direct intravenous injection of siRNA and antisense RNA vectors.
    Xie SY; Li W; Ren ZR; Huang SZ; Zeng F; Zeng YT
    Int J Hematol; 2011 Mar; 93(3):301-310. PubMed ID: 21369857
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Comparative analysis of FV vectors with human α- or β-globin gene regulatory elements for the correction of β-thalassemia.
    Morianos I; Siapati EK; Pongas G; Vassilopoulos G
    Gene Ther; 2012 Mar; 19(3):303-11. PubMed ID: 21734726
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Reversal of aberrant splicing of beta-thalassemia allele by antisense RNA in vitro and in vivo.
    Zeng Y; Gu X; Chen Y; Gong L; Ren Z; Huang S
    Chin Med J (Engl); 1999 Feb; 112(2):107-11. PubMed ID: 11593572
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Therapeutic haemoglobin synthesis in beta-thalassaemic mice expressing lentivirus-encoded human beta-globin.
    May C; Rivella S; Callegari J; Heller G; Gaensler KM; Luzzatto L; Sadelain M
    Nature; 2000 Jul; 406(6791):82-6. PubMed ID: 10894546
    [TBL] [Abstract][Full Text] [Related]  

  • 11. [Repair of the splicing defect of thalassemic allele beta IVS-2-654 C-->T in cultured human erythroid cells by antisense RNA].
    Gu X; Gong L; Zhang W
    Zhonghua Yi Xue Za Zhi; 1997 Nov; 77(11):815-8. PubMed ID: 9772473
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Recent advances in globin gene transfer for the treatment of beta-thalassemia and sickle cell anemia.
    Sadelain M
    Curr Opin Hematol; 2006 May; 13(3):142-8. PubMed ID: 16567956
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Progress toward the genetic treatment of the beta-thalassemias.
    Sadelain M; Lisowski L; Samakoglu S; Rivella S; May C; Riviere I
    Ann N Y Acad Sci; 2005; 1054():78-91. PubMed ID: 16339654
    [TBL] [Abstract][Full Text] [Related]  

  • 14. [Update on RNA splicing repair: applications to beta thalassemia and other perspectives].
    Labie D; Kaplan JC
    Med Sci (Paris); 2010 Jan; 26(1):38-41. PubMed ID: 20132773
    [No Abstract]   [Full Text] [Related]  

  • 15. Improvement of mouse beta-thalassemia upon erythropoietin delivery by encapsulated myoblasts.
    Dalle B; Payen E; Regulier E; Deglon N; Rouyer-Fessard P; Beuzard Y; Aebischer P
    Gene Ther; 1999 Feb; 6(2):157-61. PubMed ID: 10435099
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Current status of globin gene therapy for the treatment of beta-thalassaemia.
    Lisowski L; Sadelain M
    Br J Haematol; 2008 May; 141(3):335-45. PubMed ID: 18410569
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Anti-beta s-ribozyme reduces beta s mRNA levels in transgenic mice: potential application to the gene therapy of sickle cell anemia.
    Alami R; Gilman JG; Feng YQ; Marmorato A; Rochlin I; Suzuka SM; Fabry ME; Nagel RL; Bouhassira EE
    Blood Cells Mol Dis; 1999 Apr; 25(2):110-9. PubMed ID: 10389593
    [TBL] [Abstract][Full Text] [Related]  

  • 18. A phase I/II clinical trial of beta-globin gene therapy for beta-thalassemia.
    Bank A; Dorazio R; Leboulch P
    Ann N Y Acad Sci; 2005; 1054():308-16. PubMed ID: 16339679
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Exogenous iron increases hemoglobin in beta-thalassemic mice.
    Ginzburg YZ; Rybicki AC; Suzuka SM; Hall CB; Breuer W; Cabantchik ZI; Bouhassira EE; Fabry ME; Nagel RL
    Exp Hematol; 2009 Feb; 37(2):172-83. PubMed ID: 19059700
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Molecular analysis of globin gene expression in different thalassaemia disorders: individual variation of β(E) pre-mRNA splicing determine disease severity.
    Tubsuwan A; Munkongdee T; Jearawiriyapaisarn N; Boonchoy C; Winichagoon P; Fucharoen S; Svasti S
    Br J Haematol; 2011 Sep; 154(5):635-43. PubMed ID: 21732929
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 21.