BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

195 related articles for article (PubMed ID: 17954483)

  • 21. Engraftment of gene-modified umbilical cord blood cells in neonates with adenosine deaminase deficiency.
    Kohn DB; Weinberg KI; Nolta JA; Heiss LN; Lenarsky C; Crooks GM; Hanley ME; Annett G; Brooks JS; el-Khoureiy A
    Nat Med; 1995 Oct; 1(10):1017-23. PubMed ID: 7489356
    [TBL] [Abstract][Full Text] [Related]  

  • 22. Recombinant adeno-associated virus-mediated gene transfer for the potential therapy of adenosine deaminase-deficient severe combined immune deficiency.
    Silver JN; Elder M; Conlon T; Cruz P; Wright AJ; Srivastava A; Flotte TR
    Hum Gene Ther; 2011 Aug; 22(8):935-49. PubMed ID: 21142972
    [TBL] [Abstract][Full Text] [Related]  

  • 23. Gene therapy for hematopoietic and immune disorders.
    Kohn DB
    Bone Marrow Transplant; 1996 Dec; 18 Suppl 3():S55-8. PubMed ID: 8971410
    [TBL] [Abstract][Full Text] [Related]  

  • 24. Update on gene therapy for adenosine deaminase-deficient severe combined immunodeficiency.
    Ferrua F; Brigida I; Aiuti A
    Curr Opin Allergy Clin Immunol; 2010 Dec; 10(6):551-6. PubMed ID: 20966749
    [TBL] [Abstract][Full Text] [Related]  

  • 25. Integration of retroviral vectors induces minor changes in the transcriptional activity of T cells from ADA-SCID patients treated with gene therapy.
    Cassani B; Montini E; Maruggi G; Ambrosi A; Mirolo M; Selleri S; Biral E; Frugnoli I; Hernandez-Trujillo V; Di Serio C; Roncarolo MG; Naldini L; Mavilio F; Aiuti A
    Blood; 2009 Oct; 114(17):3546-56. PubMed ID: 19652199
    [TBL] [Abstract][Full Text] [Related]  

  • 26. Gene transfer to hematopoietic cells--the clinical experience.
    Richter J
    Eur J Haematol; 1997 Aug; 59(2):67-75. PubMed ID: 9293853
    [No Abstract]   [Full Text] [Related]  

  • 27. In vivo T-cell dynamics during immune reconstitution after hematopoietic stem cell gene therapy in adenosine deaminase severe combined immune deficiency.
    Selleri S; Brigida I; Casiraghi M; Scaramuzza S; Cappelli B; Cassani B; Ferrua F; Aker M; Slavin S; Scarselli A; Cancrini C; Marktel S; Grazia Roncarolo M; Aiuti A
    J Allergy Clin Immunol; 2011 Jun; 127(6):1368-75.e8. PubMed ID: 21477850
    [TBL] [Abstract][Full Text] [Related]  

  • 28. Gene therapy for human inherited disorders: techniques and status.
    Hoeben RC; Valerio D; van der Eb AJ; van Ormondt H
    Crit Rev Oncol Hematol; 1992 Jul; 13(1):33-54. PubMed ID: 1333218
    [No Abstract]   [Full Text] [Related]  

  • 29. Amendment to Clinical Research Project. Project 90-C-195. April 1, 1993. Treatment of severe combined immunodeficiency disease (SCID) due to adenosine deaminase deficiency with autologous lymphocytes transduced with a human ADA gene.
    Dunbar C; Chang L; Mullen C; Ramsey WJ; Carter C; Kohn D; Parkman R; Lenarsky C; Weinberg K; Wara D; Culver KW; Anderson WF; Leitman S; Fleisher T; Klein H; Shearer G; Clerici M; McGarrity G; Bastian J; Hershfield MS
    Hum Gene Ther; 1999 Feb; 10(3):477-88. PubMed ID: 10048399
    [No Abstract]   [Full Text] [Related]  

  • 30. [Gene therapy of primary immunodeficiencies. Present and future].
    Serrano F; Laín de Lera T; González MA; García MJ; Abad JL; Bernad A
    Sangre (Barc); 1999 Apr; 44(2):143-53. PubMed ID: 10382324
    [No Abstract]   [Full Text] [Related]  

  • 31. Gene therapy fulfilling its promise.
    Kohn DB; Candotti F
    N Engl J Med; 2009 Jan; 360(5):518-21. PubMed ID: 19179320
    [No Abstract]   [Full Text] [Related]  

  • 32. Gene therapy. The best of times, the worst of times.
    Anderson WF
    Science; 2000 Apr; 288(5466):627-9. PubMed ID: 10799000
    [No Abstract]   [Full Text] [Related]  

  • 33. Gene therapy for severe combined immunodeficiency due to adenosine deaminase deficiency.
    Montiel-Equihua CA; Thrasher AJ; Gaspar HB
    Curr Gene Ther; 2012 Feb; 12(1):57-65. PubMed ID: 22348551
    [TBL] [Abstract][Full Text] [Related]  

  • 34. Successful peripheral T-lymphocyte-directed gene transfer for a patient with severe combined immune deficiency caused by adenosine deaminase deficiency.
    Onodera M; Ariga T; Kawamura N; Kobayashi I; Ohtsu M; Yamada M; Tame A; Furuta H; Okano M; Matsumoto S; Kotani H; McGarrity GJ; Blaese RM; Sakiyama Y
    Blood; 1998 Jan; 91(1):30-6. PubMed ID: 9414266
    [TBL] [Abstract][Full Text] [Related]  

  • 35. Update on the safety and efficacy of retroviral gene therapy for immunodeficiency due to adenosine deaminase deficiency.
    Cicalese MP; Ferrua F; Castagnaro L; Pajno R; Barzaghi F; Giannelli S; Dionisio F; Brigida I; Bonopane M; Casiraghi M; Tabucchi A; Carlucci F; Grunebaum E; Adeli M; Bredius RG; Puck JM; Stepensky P; Tezcan I; Rolfe K; De Boever E; Reinhardt RR; Appleby J; Ciceri F; Roncarolo MG; Aiuti A
    Blood; 2016 Jul; 128(1):45-54. PubMed ID: 27129325
    [TBL] [Abstract][Full Text] [Related]  

  • 36. Twenty-Five Years of Gene Therapy for ADA-SCID: From Bubble Babies to an Approved Drug.
    Ferrua F; Aiuti A
    Hum Gene Ther; 2017 Nov; 28(11):972-981. PubMed ID: 28847159
    [TBL] [Abstract][Full Text] [Related]  

  • 37. Integration profile of retroviral vector in gene therapy treated patients is cell-specific according to gene expression and chromatin conformation of target cell.
    Biasco L; Ambrosi A; Pellin D; Bartholomae C; Brigida I; Roncarolo MG; Di Serio C; von Kalle C; Schmidt M; Aiuti A
    EMBO Mol Med; 2011 Feb; 3(2):89-101. PubMed ID: 21243617
    [TBL] [Abstract][Full Text] [Related]  

  • 38. Evolving Gene Therapy in Primary Immunodeficiency.
    Thrasher AJ; Williams DA
    Mol Ther; 2017 May; 25(5):1132-1141. PubMed ID: 28366768
    [TBL] [Abstract][Full Text] [Related]  

  • 39. Outcomes in two Japanese adenosine deaminase-deficiency patients treated by stem cell gene therapy with no cytoreductive conditioning.
    Otsu M; Yamada M; Nakajima S; Kida M; Maeyama Y; Hatano N; Toita N; Takezaki S; Okura Y; Kobayashi R; Matsumoto Y; Tatsuzawa O; Tsuchida F; Kato S; Kitagawa M; Mineno J; Hershfield MS; Bali P; Candotti F; Onodera M; Kawamura N; Sakiyama Y; Ariga T
    J Clin Immunol; 2015 May; 35(4):384-98. PubMed ID: 25875699
    [TBL] [Abstract][Full Text] [Related]  

  • 40. Steps toward gene therapy: 1. The initial trials.
    Blaese RM
    Hosp Pract (1995); 1995 Nov; 30(11):33-40. PubMed ID: 8557801
    [TBL] [Abstract][Full Text] [Related]  

    [Previous]   [Next]    [New Search]
    of 10.