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2. Local dystrophin restoration with antisense oligonucleotide PRO051. van Deutekom JC; Janson AA; Ginjaar IB; Frankhuizen WS; Aartsma-Rus A; Bremmer-Bout M; den Dunnen JT; Koop K; van der Kooi AJ; Goemans NM; de Kimpe SJ; Ekhart PF; Venneker EH; Platenburg GJ; Verschuuren JJ; van Ommen GJ N Engl J Med; 2007 Dec; 357(26):2677-86. PubMed ID: 18160687 [TBL] [Abstract][Full Text] [Related]
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18. Development of antisense-mediated exon skipping as a treatment for duchenne muscular dystrophy. Heemskerk H; de Winter CL; van Ommen GJ; van Deutekom JC; Aartsma-Rus A Ann N Y Acad Sci; 2009 Sep; 1175():71-9. PubMed ID: 19796079 [TBL] [Abstract][Full Text] [Related]