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5. Case of leukaemia associated with X-linked severe combined immunodeficiency gene therapy trial in London. Board of the European Society of Gene and Cell Therapy Hum Gene Ther; 2008 Jan; 19(1):3-4. PubMed ID: 18380015 [No Abstract] [Full Text] [Related]
7. Toward Clinical Translation of New Gene Targeting Technologies for Correcting Inherited Mutations and Empowering Adoptive Immunotherapy of Cancer (SUPERSIST). Hum Gene Ther Clin Dev; 2015 Jun; 26(2):95-7. PubMed ID: 26086760 [No Abstract] [Full Text] [Related]
8. Trials are halted on gene therapy: child in experiment falls ill--new setback for research. Stolberg SG N Y Times Web; 2002 Oct; ():A1, A25. PubMed ID: 12474837 [No Abstract] [Full Text] [Related]
9. Interleukin-2 receptor gamma chain mutation results in X-linked severe combined immunodeficiency in humans. Cell 73: 147-157. 1993. Noguchi M; Yi H; Rosenblatt HM; Filipovich AH; Adelstein S; Modi WS; McBride OW; Leonard WJ J Immunol; 2008 Nov; 181(9):5817-27. PubMed ID: 18941169 [No Abstract] [Full Text] [Related]
10. Genome editing: a tool for research and therapy: targeted genome editing hits the clinic. Lombardo A; Naldini L Nat Med; 2014 Oct; 20(10):1101-3. PubMed ID: 25295939 [No Abstract] [Full Text] [Related]
12. Analysis of Mutations in the IL2RG Gene in 2 Asian Infants With X-linked Severe Combined Immunodeficiency. Hara Y; Kobayashi N; Maruyama Y; Motobayashi M; Shigemura T; Ohara O; Agematsu K; Koike K J Investig Allergol Clin Immunol; 2015; 25(4):313-5. PubMed ID: 26310054 [No Abstract] [Full Text] [Related]
13. New Gene Therapy Potential Cure for "Bubble Boy Disease": An experimental gene therapy has allowed children with SCID-1X to develop fully functioning immune systems. Am J Med Genet A; 2019 Jul; 179(7):1114-1115. PubMed ID: 31180192 [No Abstract] [Full Text] [Related]
14. A novel IL2RG mutation presenting with atypical T(-)B(+)NK+ phenotype: rapid elucidation of NK cell origin. Estévez OA; Ortega C; Fernández S; Aguado R; Rumbao J; Perez-Navero J; Santamaría M Pediatr Blood Cancer; 2014 Jan; 61(1):178-9. PubMed ID: 23940110 [No Abstract] [Full Text] [Related]
15. LMO2 and IL2RG synergize in thymocytes to mimic the evolution of SCID-X1 gene therapy-associated T-cell leukaemia. Ruggero K; Al-Assar O; Chambers JS; Codrington R; Brend T; Rabbitts TH Leukemia; 2016 Sep; 30(9):1959-62. PubMed ID: 27256700 [No Abstract] [Full Text] [Related]
16. FDA halts 27 gene therapy trials after illness: leukemia-like cases in 2 children in France prompt the action. Pollack A N Y Times Web; 2003 Jan; ():A1, A17. PubMed ID: 12647754 [No Abstract] [Full Text] [Related]
17. Combating oncogene activation associated with retrovirus-mediated gene therapy of X-linked severe combined immunodeficiency. Strauss BE; Costanzi-Strauss E Braz J Med Biol Res; 2007 May; 40(5):601-13. PubMed ID: 17464421 [TBL] [Abstract][Full Text] [Related]
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19. Gene therapy. Seeking the cause of induced leukemias in X-SCID trial. Kaiser J Science; 2003 Jan; 299(5606):495. PubMed ID: 12543948 [No Abstract] [Full Text] [Related]
20. T-cell-replete haploidentical bone marrow transplantation for X-linked severe combined immunodeficiency. Ariffin H; Chew KS; Jawin V; Thavagnanam S Singapore Med J; 2020 May; 61(5):284-285. PubMed ID: 30128577 [No Abstract] [Full Text] [Related] [Next] [New Search]