These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.


BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

287 related articles for article (PubMed ID: 18650378)

  • 41. A phase I/II clinical trial of beta-globin gene therapy for beta-thalassemia.
    Bank A; Dorazio R; Leboulch P
    Ann N Y Acad Sci; 2005; 1054():308-16. PubMed ID: 16339679
    [TBL] [Abstract][Full Text] [Related]  

  • 42. Restoration of β-Globin Expression with Optimally Designed Lentiviral Vector for β-Thalassemia Treatment in Chinese Patients.
    Ouyang W; Dong G; Zhao W; Li J; Zhou Z; Yang G; Liu R; Li Y; Zhang Q; Du X; Sun H; Gu Y; Lai Y; Liu S; Liu C
    Hum Gene Ther; 2021 May; 32(9-10):481-494. PubMed ID: 33256481
    [TBL] [Abstract][Full Text] [Related]  

  • 43. Preclinical evaluation of efficacy and safety of an improved lentiviral vector for the treatment of β-thalassemia and sickle cell disease.
    Negre O; Bartholomae C; Beuzard Y; Cavazzana M; Christiansen L; Courne C; Deichmann A; Denaro M; de Dreuzy E; Finer M; Fronza R; Gillet-Legrand B; Joubert C; Kutner R; Leboulch P; Maouche L; Paulard A; Pierciey FJ; Rothe M; Ryu B; Schmidt M; von Kalle C; Payen E; Veres G
    Curr Gene Ther; 2015; 15(1):64-81. PubMed ID: 25429463
    [TBL] [Abstract][Full Text] [Related]  

  • 44. Lentiviral globin gene therapy with reduced-intensity conditioning in adults with β-thalassemia: a phase 1 trial.
    Boulad F; Maggio A; Wang X; Moi P; Acuto S; Kogel F; Takpradit C; Prockop S; Mansilla-Soto J; Cabriolu A; Odak A; Qu J; Thummar K; Du F; Shen L; Raso S; Barone R; Di Maggio R; Pitrolo L; Giambona A; Mingoia M; Everett JK; Hokama P; Roche AM; Cantu VA; Adhikari H; Reddy S; Bouhassira E; Mohandas N; Bushman FD; Rivière I; Sadelain M
    Nat Med; 2022 Jan; 28(1):63-70. PubMed ID: 34980909
    [TBL] [Abstract][Full Text] [Related]  

  • 45. Recombinant AAV2-mediated β-globin expression in human fetal hematopoietic cells from the aborted fetuses with β-thalassemia major.
    Tian J; Wang F; Xue JF; Zhao F; Song LJ; Tan MQ
    Int J Hematol; 2011 Jun; 93(6):691-699. PubMed ID: 21617888
    [TBL] [Abstract][Full Text] [Related]  

  • 46. Production of genetically stable high-titer retroviral vectors that carry a human gamma-globin gene under the control of the alpha-globin locus control region.
    Ren S; Wong BY; Li J; Luo XN; Wong PM; Atweh GF
    Blood; 1996 Mar; 87(6):2518-24. PubMed ID: 8630419
    [TBL] [Abstract][Full Text] [Related]  

  • 47. The GATA1-HS2 enhancer allows persistent and position-independent expression of a β-globin transgene.
    Miccio A; Poletti V; Tiboni F; Rossi C; Antonelli A; Mavilio F; Ferrari G
    PLoS One; 2011; 6(12):e27955. PubMed ID: 22164220
    [TBL] [Abstract][Full Text] [Related]  

  • 48. Adeno-associated virus 2-mediated transduction and erythroid lineage-restricted expression from parvovirus B19p6 promoter in primary human hematopoietic progenitor cells.
    Kurpad C; Mukherjee P; Wang XS; Ponnazhagan S; Li L; Yoder MC; Srivastava A
    J Hematother Stem Cell Res; 1999 Dec; 8(6):585-92. PubMed ID: 10645765
    [TBL] [Abstract][Full Text] [Related]  

  • 49. Engineered U7 snRNA mediates sustained splicing correction in erythroid cells from β-thalassemia/HbE patients.
    Preedagasamzin S; Nualkaew T; Pongrujikorn T; Jinawath N; Kole R; Fucharoen S; Jearawiriyapaisarn N; Svasti S
    Biochem Biophys Res Commun; 2018 Apr; 499(1):86-92. PubMed ID: 29550480
    [TBL] [Abstract][Full Text] [Related]  

  • 50. Safe mobilization of CD34+ cells in adults with β-thalassemia and validation of effective globin gene transfer for clinical investigation.
    Boulad F; Wang X; Qu J; Taylor C; Ferro L; Karponi G; Bartido S; Giardina P; Heller G; Prockop SE; Maggio A; Sadelain M; Rivière I
    Blood; 2014 Mar; 123(10):1483-6. PubMed ID: 24429337
    [TBL] [Abstract][Full Text] [Related]  

  • 51. Enhancement of β-Globin Gene Expression in Thalassemic IVS2-654 Induced Pluripotent Stem Cell-Derived Erythroid Cells by Modified U7 snRNA.
    Phanthong P; Borwornpinyo S; Kitiyanant N; Jearawiriyapaisarn N; Nuntakarn L; Saetan J; Nualkaew T; Sa-Ngiamsuntorn K; Anurathapan U; Dinnyes A; Kitiyanant Y; Hongeng S
    Stem Cells Transl Med; 2017 Apr; 6(4):1059-1069. PubMed ID: 28213976
    [TBL] [Abstract][Full Text] [Related]  

  • 52. A novel transgenic mouse model produced from lentiviral germline integration for the study of beta-thalassemia gene therapy.
    Li W; Xie S; Guo X; Gong X; Wang S; Lin D; Zhang J; Ren Z; Huang S; Zeng F; Zeng Y
    Haematologica; 2008 Mar; 93(3):356-62. PubMed ID: 18268280
    [TBL] [Abstract][Full Text] [Related]  

  • 53. Development of gene therapy for hemoglobin disorders.
    Nienhuis AW; Hanawa H; Sawai N; Sorrentino BP; Persons DA
    Ann N Y Acad Sci; 2003 May; 996():101-11. PubMed ID: 12799288
    [TBL] [Abstract][Full Text] [Related]  

  • 54. Hematopoietic stem cell gene transfer for the treatment of hemoglobin disorders.
    Persons DA
    Hematology Am Soc Hematol Educ Program; 2009; ():690-7. PubMed ID: 20008255
    [TBL] [Abstract][Full Text] [Related]  

  • 55. Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia.
    Marktel S; Scaramuzza S; Cicalese MP; Giglio F; Galimberti S; Lidonnici MR; Calbi V; Assanelli A; Bernardo ME; Rossi C; Calabria A; Milani R; Gattillo S; Benedicenti F; Spinozzi G; Aprile A; Bergami A; Casiraghi M; Consiglieri G; Masera N; D'Angelo E; Mirra N; Origa R; Tartaglione I; Perrotta S; Winter R; Coppola M; Viarengo G; Santoleri L; Graziadei G; Gabaldo M; Valsecchi MG; Montini E; Naldini L; Cappellini MD; Ciceri F; Aiuti A; Ferrari G
    Nat Med; 2019 Feb; 25(2):234-241. PubMed ID: 30664781
    [TBL] [Abstract][Full Text] [Related]  

  • 56. Advances in stem cell transplantation and gene therapy in the β-hemoglobinopathies.
    Payen E; Leboulch P
    Hematology Am Soc Hematol Educ Program; 2012; 2012():276-83. PubMed ID: 23233592
    [TBL] [Abstract][Full Text] [Related]  

  • 57. Curative in vivo hematopoietic stem cell gene therapy of murine thalassemia using large regulatory elements.
    Wang H; Georgakopoulou A; Li C; Liu Z; Gil S; Bashyam A; Yannaki E; Anagnostopoulos A; Pande A; Izsvák Z; Papayannopoulou T; Lieber A
    JCI Insight; 2020 Aug; 5(16):. PubMed ID: 32814708
    [TBL] [Abstract][Full Text] [Related]  

  • 58. Abnormal assembly of membrane proteins in erythroid progenitors of patients with beta-thalassemia major.
    Aljurf M; Ma L; Angelucci E; Lucarelli G; Snyder LM; Kiefer CR; Yuan J; Schrier SL
    Blood; 1996 Mar; 87(5):2049-56. PubMed ID: 8634456
    [TBL] [Abstract][Full Text] [Related]  

  • 59. [Optimization of β-globin Stable Expression Using the Third Generation Lentiviral Vector for β-thalassemia Therapy].
    Yu Z; Tong S; Bai Y; Zhong XS
    Zhongguo Shi Yan Xue Ye Xue Za Zhi; 2022 Jun; 30(3):844-850. PubMed ID: 35680815
    [TBL] [Abstract][Full Text] [Related]  

  • 60. Development of viral vectors for gene therapy of beta-chain hemoglobinopathies: optimization of a gamma-globin gene expression cassette.
    Li Q; Emery DW; Fernandez M; Han H; Stamatoyannopoulos G
    Blood; 1999 Apr; 93(7):2208-16. PubMed ID: 10090929
    [TBL] [Abstract][Full Text] [Related]  

    [Previous]   [Next]    [New Search]
    of 15.