168 related articles for article (PubMed ID: 18667806)
1. Multipotential neural precursors transplanted into the metachromatic leukodystrophy brain fail to generate oligodendrocytes but contribute to limit brain dysfunction.
Givogri MI; Bottai D; Zhu HL; Fasano S; Lamorte G; Brambilla R; Vescovi A; Wrabetz L; Bongarzone E
Dev Neurosci; 2008; 30(5):340-57. PubMed ID: 18667806
[TBL] [Abstract][Full Text] [Related]
2. Oligodendroglial progenitor cell therapy limits central neurological deficits in mice with metachromatic leukodystrophy.
Givogri MI; Galbiati F; Fasano S; Amadio S; Perani L; Superchi D; Morana P; Del Carro U; Marchesini S; Brambilla R; Wrabetz L; Bongarzone E
J Neurosci; 2006 Mar; 26(12):3109-19. PubMed ID: 16554462
[TBL] [Abstract][Full Text] [Related]
3. Ex vivo cell-mediated gene therapy for metachromatic leukodystrophy using neurospheres.
Kawabata K; Migita M; Mochizuki H; Miyake K; Igarashi T; Fukunaga Y; Shimada T
Brain Res; 2006 Jun; 1094(1):13-23. PubMed ID: 16729983
[TBL] [Abstract][Full Text] [Related]
4. Arylsulfatase A Overexpressing Human iPSC-derived Neural Cells Reduce CNS Sulfatide Storage in a Mouse Model of Metachromatic Leukodystrophy.
Doerr J; Böckenhoff A; Ewald B; Ladewig J; Eckhardt M; Gieselmann V; Matzner U; Brüstle O; Koch P
Mol Ther; 2015 Sep; 23(9):1519-31. PubMed ID: 26061647
[TBL] [Abstract][Full Text] [Related]
5. Generation of Human Induced Pluripotent Stem Cell-Derived Bona Fide Neural Stem Cells for Ex Vivo Gene Therapy of Metachromatic Leukodystrophy.
Meneghini V; Frati G; Sala D; De Cicco S; Luciani M; Cavazzin C; Paulis M; Mentzen W; Morena F; Giannelli S; Sanvito F; Villa A; Bulfone A; Broccoli V; Martino S; Gritti A
Stem Cells Transl Med; 2017 Feb; 6(2):352-368. PubMed ID: 28191778
[TBL] [Abstract][Full Text] [Related]
6. Dysfunction of platelet-derived growth factor receptor α (PDGFRα) represses the production of oligodendrocytes from arylsulfatase A-deficient multipotential neural precursor cells.
Pituch KC; Moyano AL; Lopez-Rosas A; Marottoli FM; Li G; Hu C; van Breemen R; Månsson JE; Givogri MI
J Biol Chem; 2015 Mar; 290(11):7040-53. PubMed ID: 25605750
[TBL] [Abstract][Full Text] [Related]
7. Correction of brain oligodendrocytes by AAVrh.10 intracerebral gene therapy in metachromatic leukodystrophy mice.
Piguet F; Sondhi D; Piraud M; Fouquet F; Hackett NR; Ahouansou O; Vanier MT; Bieche I; Aubourg P; Crystal RG; Cartier N; Sevin C
Hum Gene Ther; 2012 Aug; 23(8):903-14. PubMed ID: 22642214
[TBL] [Abstract][Full Text] [Related]
8. Embryonic stem cell-based reduction of central nervous system sulfatide storage in an animal model of metachromatic leukodystrophy.
Klein D; Schmandt T; Muth-Köhne E; Perez-Bouza A; Segschneider M; Gieselmann V; Brüstle O
Gene Ther; 2006 Dec; 13(24):1686-95. PubMed ID: 16871228
[TBL] [Abstract][Full Text] [Related]
9. Gene therapy of metachromatic leukodystrophy reverses neurological damage and deficits in mice.
Biffi A; Capotondo A; Fasano S; del Carro U; Marchesini S; Azuma H; Malaguti MC; Amadio S; Brambilla R; Grompe M; Bordignon C; Quattrini A; Naldini L
J Clin Invest; 2006 Nov; 116(11):3070-82. PubMed ID: 17080200
[TBL] [Abstract][Full Text] [Related]
10. Treatment of adult metachromatic leukodystrophy model mice using intrathecal administration of type 9 AAV vector encoding arylsulfatase A.
Miyake N; Miyake K; Sakai A; Yamamoto M; Suzuki H; Shimada T
Sci Rep; 2021 Oct; 11(1):20513. PubMed ID: 34654893
[TBL] [Abstract][Full Text] [Related]
11. Metabolic correction in oligodendrocytes derived from metachromatic leukodystrophy mouse model by using encapsulated recombinant myoblasts.
Consiglio A; Martino S; Dolcetta D; Cusella G; Conese M; Marchesini S; Benaglia G; Wrabetz L; Orlacchio A; Déglon N; Aebischer P; Severini GM; Bordignon C
J Neurol Sci; 2007 Apr; 255(1-2):7-16. PubMed ID: 17341424
[TBL] [Abstract][Full Text] [Related]
12. Gene therapy in metachromatic leukodystrophy.
Sevin C; Cartier-Lacave N; Aubourg P
Int J Clin Pharmacol Ther; 2009; 47 Suppl 1():S128-31. PubMed ID: 20040324
[TBL] [Abstract][Full Text] [Related]
13. Intracerebral adeno-associated virus-mediated gene transfer in rapidly progressive forms of metachromatic leukodystrophy.
Sevin C; Benraiss A; Van Dam D; Bonnin D; Nagels G; Verot L; Laurendeau I; Vidaud M; Gieselmann V; Vanier M; De Deyn PP; Aubourg P; Cartier N
Hum Mol Genet; 2006 Jan; 15(1):53-64. PubMed ID: 16311251
[TBL] [Abstract][Full Text] [Related]
14. High residual arylsulfatase A (ARSA) activity in a patient with late-infantile metachromatic leukodystrophy.
Kreysing J; Bohne W; Bösenberg C; Marchesini S; Turpin JC; Baumann N; von Figura K; Gieselmann V
Am J Hum Genet; 1993 Aug; 53(2):339-46. PubMed ID: 8101038
[TBL] [Abstract][Full Text] [Related]
15. Metachromatic leukodystrophy and transplantation: remyelination, no cross-correction.
Wolf NI; Breur M; Plug B; Beerepoot S; Westerveld ASR; van Rappard DF; de Vries SI; Kole MHP; Vanderver A; van der Knaap MS; Lindemans CA; van Hasselt PM; Boelens JJ; Matzner U; Gieselmann V; Bugiani M
Ann Clin Transl Neurol; 2020 Feb; 7(2):169-180. PubMed ID: 31967741
[TBL] [Abstract][Full Text] [Related]
16. Elucidating the Therapeutic Utility of Olaparib in Sulfatide-Induced Human Astrocyte Toxicity and Neuroinflammation.
Mekhaeil M; Conroy MJ; Dev KK
J Neuroimmune Pharmacol; 2023 Dec; 18(4):592-609. PubMed ID: 37924373
[TBL] [Abstract][Full Text] [Related]
17. [Pathophysiology of sulfatide metabolism in metachromatic leukodystrophy].
Wiesmann UN
Bull Schweiz Akad Med Wiss; 1978 Mar; 34(1-3):33-47. PubMed ID: 27269
[TBL] [Abstract][Full Text] [Related]
18. Human iPSC-based models highlight defective glial and neuronal differentiation from neural progenitor cells in metachromatic leukodystrophy.
Frati G; Luciani M; Meneghini V; De Cicco S; Ståhlman M; Blomqvist M; Grossi S; Filocamo M; Morena F; Menegon A; Martino S; Gritti A
Cell Death Dis; 2018 Jun; 9(6):698. PubMed ID: 29899471
[TBL] [Abstract][Full Text] [Related]
19. Lentiviral haematopoietic stem-cell gene therapy for early-onset metachromatic leukodystrophy: long-term results from a non-randomised, open-label, phase 1/2 trial and expanded access.
Fumagalli F; Calbi V; Natali Sora MG; Sessa M; Baldoli C; Rancoita PMV; Ciotti F; Sarzana M; Fraschini M; Zambon AA; Acquati S; Redaelli D; Attanasio V; Miglietta S; De Mattia F; Barzaghi F; Ferrua F; Migliavacca M; Tucci F; Gallo V; Del Carro U; Canale S; Spiga I; Lorioli L; Recupero S; Fratini ES; Morena F; Silvani P; Calvi MR; Facchini M; Locatelli S; Corti A; Zancan S; Antonioli G; Farinelli G; Gabaldo M; Garcia-Segovia J; Schwab LC; Downey GF; Filippi M; Cicalese MP; Martino S; Di Serio C; Ciceri F; Bernardo ME; Naldini L; Biffi A; Aiuti A
Lancet; 2022 Jan; 399(10322):372-383. PubMed ID: 35065785
[TBL] [Abstract][Full Text] [Related]
20. Olaparib Attenuates Demyelination and Neuroinflammation in an Organotypic Slice Culture Model of Metachromatic Leukodystrophy.
Mekhaeil M; Conroy MJ; Dev KK
Neurotherapeutics; 2023 Sep; 20(5):1347-1368. PubMed ID: 37525026
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]
