255 related articles for article (PubMed ID: 18805722)
21. Long-term engraftment of nonobese diabetic/severe combined immunodeficient mice with human CD34+ cells transduced by a self-inactivating human immunodeficiency virus type 1 vector.
Gatlin J; Padgett A; Melkus MW; Kelly PF; Garcia JV
Hum Gene Ther; 2001 Jun; 12(9):1079-89. PubMed ID: 11399229
[TBL] [Abstract][Full Text] [Related]
22. [The observation of engraftment of human umbilical cord blood-derived hematopoietic stem/progenitor cells in xenotransplanted NOD/SCID mouse model by intra-bone marrow injection].
Gao JT; Lu SH; Li YH; Yang Z; Xu J; Zheng YZ
Zhonghua Xue Ye Xue Za Zhi; 2008 Jun; 29(6):361-5. PubMed ID: 19031735
[TBL] [Abstract][Full Text] [Related]
23. Targeted gene therapy to antigen-presenting cells in the central nervous system using hematopoietic stem cells.
Lesniak MS; Kelleher E; Pardoll D; Cui Y
Neurol Res; 2005 Dec; 27(8):820-6. PubMed ID: 16354542
[TBL] [Abstract][Full Text] [Related]
24. Comparison of three retroviral vector systems for transduction of nonobese diabetic/severe combined immunodeficiency mice repopulating human CD34+ cord blood cells.
Leurs C; Jansen M; Pollok KE; Heinkelein M; Schmidt M; Wissler M; Lindemann D; Von Kalle C; Rethwilm A; Williams DA; Hanenberg H
Hum Gene Ther; 2003 Apr; 14(6):509-19. PubMed ID: 12718762
[TBL] [Abstract][Full Text] [Related]
25. Acid Ceramidase Depletion Impairs Neuronal Survival and Induces Morphological Defects in Neurites Associated with Altered Gene Transcription and Sphingolipid Content.
Kyriakou K; Lederer CW; Kleanthous M; Drousiotou A; Malekkou A
Int J Mol Sci; 2020 Feb; 21(5):. PubMed ID: 32111095
[TBL] [Abstract][Full Text] [Related]
26. [Intra-bone marrow infusion of human cord blood hematopoietic stem/progenitor cells improves hematopoietic reconstitution in NOD-SCID mice].
Meng ZT; Gao JT; Lu SH; Yan X; Li YH; Yang Z; Zheng YZ
Zhongguo Shi Yan Xue Ye Xue Za Zhi; 2009 Aug; 17(4):1010-5. PubMed ID: 19698249
[TBL] [Abstract][Full Text] [Related]
27. Transduction of human NOD/SCID-repopulating cells with both lymphoid and myeloid potential by foamy virus vectors.
Josephson NC; Vassilopoulos G; Trobridge GD; Priestley GV; Wood BL; Papayannopoulou T; Russell DW
Proc Natl Acad Sci U S A; 2002 Jun; 99(12):8295-300. PubMed ID: 12060773
[TBL] [Abstract][Full Text] [Related]
28. Glycoprotein Ibalpha promoter drives megakaryocytic lineage-restricted expression after hematopoietic stem cell transduction using a self-inactivating lentiviral vector.
Lavenu-Bombled C; Izac B; Legrand F; Cambot M; Vigier A; Massé JM; Dubart-Kupperschmitt A
Stem Cells; 2007 Jun; 25(6):1571-7. PubMed ID: 17379771
[TBL] [Abstract][Full Text] [Related]
29. Enhanced transgene expression in cord blood CD34(+)-derived hematopoietic cells, including developing T cells and NOD/SCID mouse repopulating cells, following transduction with modified trip lentiviral vectors.
Sirven A; Ravet E; Charneau P; Zennou V; Coulombel L; Guétard D; Pflumio F; Dubart-Kupperschmitt A
Mol Ther; 2001 Apr; 3(4):438-48. PubMed ID: 11319904
[TBL] [Abstract][Full Text] [Related]
30. Anti-CD25 targeted killing of bicistronically transduced cells: a novel safety mechanism against retroviral genotoxicity.
Ramsubir S; Yoshimitsu M; Medin JA
Mol Ther; 2007 Jun; 15(6):1174-81. PubMed ID: 17387334
[TBL] [Abstract][Full Text] [Related]
31. Transduction of human CD34+ CD38- bone marrow and cord blood-derived SCID-repopulating cells with third-generation lentiviral vectors.
Guenechea G; Gan OI; Inamitsu T; Dorrell C; Pereira DS; Kelly M; Naldini L; Dick JE
Mol Ther; 2000 Jun; 1(6):566-73. PubMed ID: 10933981
[TBL] [Abstract][Full Text] [Related]
32. Pathological manifestations of Farber disease in a new mouse model.
Beckmann N; Kadow S; Schumacher F; Göthert JR; Kesper S; Draeger A; Schulz-Schaeffer WJ; Wang J; Becker JU; Kramer M; Kühn C; Kleuser B; Becker KA; Gulbins E; Carpinteiro A
Biol Chem; 2018 Sep; 399(10):1183-1202. PubMed ID: 29908121
[TBL] [Abstract][Full Text] [Related]
33. Sustained transgene expression by human cord blood derived CD34+ cells transduced with simian immunodeficiency virus agmTYO1-based vectors carrying the human coagulation factor VIII gene in NOD/SCID mice.
Kikuchi J; Mimuro J; Ogata K; Tabata T; Ueda Y; Ishiwata A; Kimura K; Takano K; Madoiwa S; Mizukami H; Hanazono Y; Kume A; Hasegawa M; Ozawa K; Sakata Y
J Gene Med; 2004 Oct; 6(10):1049-60. PubMed ID: 15386735
[TBL] [Abstract][Full Text] [Related]
34. The molecular medicine of acid ceramidase.
Frohbergh M; He X; Schuchman EH
Biol Chem; 2015 Jun; 396(6-7):759-65. PubMed ID: 25938220
[TBL] [Abstract][Full Text] [Related]
35. Development of gene therapy for hematopoietic stem cells using lentiviral vectors.
Woods NB; Ooka A; Karlsson S
Leukemia; 2002 Apr; 16(4):563-9. PubMed ID: 11960333
[TBL] [Abstract][Full Text] [Related]
36. Novel V97G ASAH1 mutation found in Farber disease patients: unique appearance of the disease with an intermediate severity, and marked early involvement of central and peripheral nervous system.
Chedrawi AK; Al-Hassnan ZN; Al-Muhaizea M; Colak D; Al-Younes B; Albakheet A; Tulba S; Kaya N
Brain Dev; 2012 May; 34(5):400-4. PubMed ID: 21893389
[TBL] [Abstract][Full Text] [Related]
37. Ceramide accumulation is associated with increased apoptotic cell death in cultured fibroblasts of sphingolipid activator protein-deficient mouse but not in fibroblasts of patients with Farber disease.
Tohyama J; Oya Y; Ezoe T; Vanier MT; Nakayasu H; Fujita N; Suzuki K
J Inherit Metab Dis; 1999 Jun; 22(5):649-62. PubMed ID: 10399097
[TBL] [Abstract][Full Text] [Related]
38. Exclusive Transduction of Human CD4+ T Cells upon Systemic Delivery of CD4-Targeted Lentiviral Vectors.
Zhou Q; Uhlig KM; Muth A; Kimpel J; Lévy C; Münch RC; Seifried J; Pfeiffer A; Trkola A; Coulibaly C; von Laer D; Wels WS; Hartwig UF; Verhoeyen E; Buchholz CJ
J Immunol; 2015 Sep; 195(5):2493-501. PubMed ID: 26232436
[TBL] [Abstract][Full Text] [Related]
39. Long-term expression of the human glucocerebrosidase gene in vivo after transplantation of bone-marrow-derived cells transformed with a lentivirus vector.
Kim EY; Hong YB; Lai Z; Cho YH; Brady RO; Jung SC
J Gene Med; 2005 Jul; 7(7):878-87. PubMed ID: 15712335
[TBL] [Abstract][Full Text] [Related]
40. Molecular analyses of novel ASAH1 mutations causing Farber lipogranulomatosis: analyses of exonic splicing enhancer inactivating mutation.
Bashyam MD; Chaudhary AK; Kiran M; Reddy V; Nagarajaram HA; Dalal A; Bashyam L; Suri D; Gupta A; Gupta N; Kabra M; Puri RD; RamaDevi R; Kapoor S; Danda S
Clin Genet; 2014 Dec; 86(6):530-8. PubMed ID: 24355074
[TBL] [Abstract][Full Text] [Related]
[Previous] [Next] [New Search]
