BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

146 related articles for article (PubMed ID: 18812474)

  • 1. In vivo proliferation advantage of genetically corrected hematopoietic stem cells in a mouse model of Fanconi anemia FA-D1.
    Río P; Meza NW; González-Murillo A; Navarro S; Alvarez L; Surrallés J; Castella M; Guenechea G; Segovia JC; Hanenberg H; Bueren JA
    Blood; 2008 Dec; 112(13):4853-61. PubMed ID: 18812474
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Hematopoietic dysfunction in a mouse model for Fanconi anemia group D1.
    Navarro S; Meza NW; Quintana-Bustamante O; Casado JA; Jacome A; McAllister K; Puerto S; Surrallés J; Segovia JC; Bueren JA
    Mol Ther; 2006 Oct; 14(4):525-35. PubMed ID: 16859999
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Generation of iPSCs from genetically corrected Brca2 hypomorphic cells: implications in cell reprogramming and stem cell therapy.
    Navarro S; Moleiro V; Molina-Estevez FJ; Lozano ML; Chinchon R; Almarza E; Quintana-Bustamante O; Mostoslavsky G; Maetzig T; Galla M; Heinz N; Schiedlmeier B; Torres Y; Modlich U; Samper E; Río P; Segovia JC; Raya A; Güenechea G; Izpisua-Belmonte JC; Bueren JA
    Stem Cells; 2014 Feb; 32(2):436-46. PubMed ID: 24420904
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Stem Cell Genetic Therapy for Fanconi Anemia - A New Hope.
    Hanenberg H; Roellecke K; Wiek C
    Curr Gene Ther; 2017; 16(5):309-320. PubMed ID: 28067166
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Advances in Gene Therapy for Fanconi Anemia.
    Río P; Navarro S; Bueren JA
    Hum Gene Ther; 2018 Oct; 29(10):1114-1123. PubMed ID: 30117331
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemia.
    Río P; Navarro S; Wang W; Sánchez-Domínguez R; Pujol RM; Segovia JC; Bogliolo M; Merino E; Wu N; Salgado R; Lamana ML; Yañez RM; Casado JA; Giménez Y; Román-Rodríguez FJ; Álvarez L; Alberquilla O; Raimbault A; Guenechea G; Lozano ML; Cerrato L; Hernando M; Gálvez E; Hladun R; Giralt I; Barquinero J; Galy A; García de Andoín N; López R; Catalá A; Schwartz JD; Surrallés J; Soulier J; Schmidt M; Díaz de Heredia C; Sevilla J; Bueren JA
    Nat Med; 2019 Sep; 25(9):1396-1401. PubMed ID: 31501599
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Engraftment and in vivo proliferation advantage of gene-corrected mobilized CD34
    Río P; Navarro S; Guenechea G; Sánchez-Domínguez R; Lamana ML; Yañez R; Casado JA; Mehta PA; Pujol MR; Surrallés J; Charrier S; Galy A; Segovia JC; Díaz de Heredia C; Sevilla J; Bueren JA
    Blood; 2017 Sep; 130(13):1535-1542. PubMed ID: 28801449
    [TBL] [Abstract][Full Text] [Related]  

  • 8. In vitro phenotypic correction of hematopoietic progenitors from Fanconi anemia group A knockout mice.
    Río P; Segovia JC; Hanenberg H; Casado JA; Martínez J; Göttsche K; Cheng NC; Van de Vrugt HJ; Arwert F; Joenje H; Bueren JA
    Blood; 2002 Sep; 100(6):2032-9. PubMed ID: 12200363
    [TBL] [Abstract][Full Text] [Related]  

  • 9. NHEJ-Mediated Repair of CRISPR-Cas9-Induced DNA Breaks Efficiently Corrects Mutations in HSPCs from Patients with Fanconi Anemia.
    Román-Rodríguez FJ; Ugalde L; Álvarez L; Díez B; Ramírez MJ; Risueño C; Cortón M; Bogliolo M; Bernal S; March F; Ayuso C; Hanenberg H; Sevilla J; Rodríguez-Perales S; Torres-Ruiz R; Surrallés J; Bueren JA; Río P
    Cell Stem Cell; 2019 Nov; 25(5):607-621.e7. PubMed ID: 31543367
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Lentiviral-Mediated Gene Therapy in Fanconi Anemia-A Mice Reveals Long-Term Engraftment and Continuous Turnover of Corrected HSCs.
    Molina-Estevez FJ; Nowrouzi A; Lozano ML; Galy A; Charrier S; von Kalle C; Guenechea G; Bueren JA; Schmidt M
    Curr Gene Ther; 2015; 15(6):550-62. PubMed ID: 26415575
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Minimal conditioning in Fanconi anemia promotes multi-lineage marrow engraftment at 10-fold lower cell doses.
    Haworth KG; Ironside C; Ramirez MA; Weitz S; Beard BC; Schwartz JD; Adair JE; Kiem HP
    J Gene Med; 2018 Oct; 20(10-11):e3050. PubMed ID: 30129972
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Rapid lentiviral transduction preserves the engraftment potential of Fanca(-/-) hematopoietic stem cells.
    Müller LU; Milsom MD; Kim MO; Schambach A; Schuesler T; Williams DA
    Mol Ther; 2008 Jun; 16(6):1154-60. PubMed ID: 18398427
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Phenotypic correction of Fanconi anemia cells in the murine bone marrow after carrier cell mediated delivery of lentiviral vector.
    Chakkaramakkil Verghese S; Goloviznina NA; Kurre P
    Stem Cell Res Ther; 2016 Nov; 7(1):170. PubMed ID: 27865213
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Gene Therapy in Fanconi Anemia: A Matter of Time, Safety and Gene Transfer Tool Efficiency.
    Verhoeyen E; Roman-Rodriguez FJ; Cosset FL; Levy C; Rio P
    Curr Gene Ther; 2017; 16(5):297-308. PubMed ID: 28067165
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Retroviral-mediated expression of recombinant Fancc enhances the repopulating ability of Fancc-/- hematopoietic stem cells and decreases the risk of clonal evolution.
    Haneline LS; Li X; Ciccone SL; Hong P; Yang Y; Broxmeyer HE; Lee SH; Orazi A; Srour EF; Clapp DW
    Blood; 2003 Feb; 101(4):1299-307. PubMed ID: 12393504
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Gene therapy of Fanconi anemia: preclinical efficacy using lentiviral vectors.
    Galimi F; Noll M; Kanazawa Y; Lax T; Chen C; Grompe M; Verma IM
    Blood; 2002 Oct; 100(8):2732-6. PubMed ID: 12351379
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Retroviral mediated gene transfer of the Fanconi anemia complementation group C gene to hematopoietic progenitors of group C patients.
    Liu JM; Young NS; Walsh CE; Cottler-Fox M; Carter C; Dunbar C; Barrett AJ; Emmons R
    Hum Gene Ther; 1997 Sep; 8(14):1715-30. PubMed ID: 9322874
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Phenotypic correction of Fanconi anemia in human hematopoietic cells with a recombinant adeno-associated virus vector.
    Walsh CE; Nienhuis AW; Samulski RJ; Brown MG; Miller JL; Young NS; Liu JM
    J Clin Invest; 1994 Oct; 94(4):1440-8. PubMed ID: 7929819
    [TBL] [Abstract][Full Text] [Related]  

  • 19. p53-TP53-Induced Glycolysis Regulator Mediated Glycolytic Suppression Attenuates DNA Damage and Genomic Instability in Fanconi Anemia Hematopoietic Stem Cells.
    Li X; Wu L; Zopp M; Kopelov S; Du W
    Stem Cells; 2019 Jul; 37(7):937-947. PubMed ID: 30977208
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Preclinical protocol for in vivo selection of hematopoietic stem cells corrected by gene therapy in Fanconi anemia group C.
    Noll M; Bateman RL; D'Andrea AD; Grompe M
    Mol Ther; 2001 Jan; 3(1):14-23. PubMed ID: 11162306
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 8.