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2. [Clinical characterization and mutation identification for multiple sulfatase deficiency patients in China]. Meng Y; Zhang WM; Shi HP; Yao FX; Qiu ZQ; Yang T; Zhao SM; Huang SZ Zhonghua Er Ke Za Zhi; 2013 Nov; 51(11):836-41. PubMed ID: 24484558 [TBL] [Abstract][Full Text] [Related]
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5. Late infantile form of multiple sulfatase deficiency with a novel missense variant in the SUMF1 gene: case report and review. Sheth J; Shah S; Datar C; Bhatt K; Raval P; Nair A; Jain D; Shah J; Sheth F; Sheth H BMC Pediatr; 2023 Mar; 23(1):133. PubMed ID: 36959582 [TBL] [Abstract][Full Text] [Related]
6. A systematic review and meta-analysis of published cases reveals the natural disease history in multiple sulfatase deficiency. Schlotawa L; Preiskorn J; Ahrens-Nicklas R; Schiller S; Adang LA; Gärtner J; Friede T J Inherit Metab Dis; 2020 Nov; 43(6):1288-1297. PubMed ID: 32621519 [TBL] [Abstract][Full Text] [Related]
7. Molecular and functional analysis of SUMF1 mutations in multiple sulfatase deficiency. Cosma MP; Pepe S; Parenti G; Settembre C; Annunziata I; Wade-Martins R; Di Domenico C; Di Natale P; Mankad A; Cox B; Uziel G; Mancini GM; Zammarchi E; Donati MA; Kleijer WJ; Filocamo M; Carrozzo R; Carella M; Ballabio A Hum Mutat; 2004 Jun; 23(6):576-81. PubMed ID: 15146462 [TBL] [Abstract][Full Text] [Related]
8. SUMF1 enhances sulfatase activities in vivo in five sulfatase deficiencies. Fraldi A; Biffi A; Lombardi A; Visigalli I; Pepe S; Settembre C; Nusco E; Auricchio A; Naldini L; Ballabio A; Cosma MP Biochem J; 2007 Apr; 403(2):305-12. PubMed ID: 17206939 [TBL] [Abstract][Full Text] [Related]
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11. Complex care of individuals with multiple sulfatase deficiency: Clinical cases and consensus statement. Ahrens-Nicklas R; Schlotawa L; Ballabio A; Brunetti-Pierri N; De Castro M; Dierks T; Eichler F; Ficicioglu C; Finglas A; Gaertner J; Kirmse B; Klepper J; Lee M; Olsen A; Parenti G; Vossough A; Vanderver A; Adang LA Mol Genet Metab; 2018 Mar; 123(3):337-346. PubMed ID: 29397290 [TBL] [Abstract][Full Text] [Related]
12. New mouse models with hypomorphic SUMF1 variants mimic attenuated forms of multiple sulfatase deficiency. Sorrentino NC; Presa M; Attanasio S; Cacace V; Sofia M; Zuberi A; Ryan J; Ray S; Petkovic I; Radhakrishnan K; Schlotawa L; Ballabio A; Lutz C; Brunetti-Pierri N J Inherit Metab Dis; 2023 Mar; 46(2):335-347. PubMed ID: 36433920 [TBL] [Abstract][Full Text] [Related]
13. Genetic analysis of a novel SUMF1 variation associated with a late infantile form of multiple sulfatase deficiency. Zhang J; Ma D; Liu G; Zeng H; Wang Y; Luo C; Hu P; Xu Z J Clin Lab Anal; 2022 Dec; 36(12):e24786. PubMed ID: 36441600 [TBL] [Abstract][Full Text] [Related]
14. Multiple sulfatase deficiency: A case series of four children. Incecik F; Ozbek MN; Gungor S; Pepe S; Herguner OM; Mungan NO; Gungor S; Altunbasak S Ann Indian Acad Neurol; 2013 Oct; 16(4):720-2. PubMed ID: 24339620 [TBL] [Abstract][Full Text] [Related]
15. A novel iPSC model reveals selective vulnerability of neurons in multiple sulfatase deficiency. Pham V; Sertori Finoti L; Cassidy MM; Maguire JA; Gagne AL; Waxman EA; French DL; King K; Zhou Z; Gelb MH; Wongkittichote P; Hong X; Schlotawa L; Davidson BL; Ahrens-Nicklas RC Mol Genet Metab; 2024 Feb; 141(2):108116. PubMed ID: 38161139 [TBL] [Abstract][Full Text] [Related]
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20. Multiple sulfatase deficiency in a Turkish family resulting from a novel mutation. Yiş U; Pepe S; Kurul SH; Ballabio A; Cosma MP; Dirik E Brain Dev; 2008 May; 30(5):374-7. PubMed ID: 18509892 [TBL] [Abstract][Full Text] [Related] [Next] [New Search]