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4. Engineering multiple U7snRNA constructs to induce single and multiexon-skipping for Duchenne muscular dystrophy. Goyenvalle A; Wright J; Babbs A; Wilkins V; Garcia L; Davies KE Mol Ther; 2012 Jun; 20(6):1212-21. PubMed ID: 22354379 [TBL] [Abstract][Full Text] [Related]
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