These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.
3. Adopting orphan drugs--two dozen years of treating rare diseases. Haffner ME N Engl J Med; 2006 Feb; 354(5):445-7. PubMed ID: 16452556 [No Abstract] [Full Text] [Related]
4. Orphan drugs and orphan tests in the USA. Thoene JG Community Genet; 2004; 7(4):169-72. PubMed ID: 15692190 [No Abstract] [Full Text] [Related]
5. Should off-label drug use be off-the-table? Rivkees SA J Pediatr Endocrinol Metab; 2007 Feb; 20(2):171-2. PubMed ID: 17396432 [No Abstract] [Full Text] [Related]
6. Lucrative niches: how drugs for rare diseases became lifeline for companies. Anand G Wall St J (East Ed); 2005 Nov; ():A1, A18. PubMed ID: 16502531 [No Abstract] [Full Text] [Related]
8. "Creating hope" and other incentives for drug development for children. Connor E; Cure P Sci Transl Med; 2011 Jan; 3(66):66cm1. PubMed ID: 21248312 [TBL] [Abstract][Full Text] [Related]
9. The Minor Use and Minor Species Animal Health Act: past, present, and future. Haley CJ Food Drug Law J; 2006; 61(1):13-43. PubMed ID: 16838456 [No Abstract] [Full Text] [Related]
10. Law and research could add up to profitable niche drugs. Haefner B Nature; 2007 Apr; 446(7138):856. PubMed ID: 17443162 [No Abstract] [Full Text] [Related]
11. Regulators adopt more orphan drugs. Reardon S Nature; 2014 Apr; 508(7494):16-7. PubMed ID: 24695293 [No Abstract] [Full Text] [Related]
12. The routes to orphan drug designation--our recent experience at the FDA. Lev D; Thorat C; Phillips I; Thomas M; Imoisili MA Drug Discov Today; 2012 Feb; 17(3-4):97-9. PubMed ID: 22210120 [No Abstract] [Full Text] [Related]
13. Health care policy. Reforming off-label promotion to enhance orphan disease treatment. Liang BA; Mackey T Science; 2010 Jan; 327(5963):273-4. PubMed ID: 20075234 [No Abstract] [Full Text] [Related]
15. A cross-national comparative study of orphan drug policies in the United States, the European Union, and Japan: towards a made-in-China orphan drug policy. Liu BC; He L; He G; He Y J Public Health Policy; 2010 Dec; 31(4):407-20; discussion 420-1. PubMed ID: 21119648 [TBL] [Abstract][Full Text] [Related]
16. Developing treatments for inborn errors: incentives available to the clinician. Haffner ME Mol Genet Metab; 2004 Apr; 81 Suppl 1():S63-6. PubMed ID: 15050976 [TBL] [Abstract][Full Text] [Related]
17. Big pharma moves from 'blockbusters' to 'niche busters'. Dolgin E Nat Med; 2010 Aug; 16(8):837. PubMed ID: 20689537 [No Abstract] [Full Text] [Related]
18. The US Orphan Drug Act: rare disease research stimulator or commercial opportunity? Wellman-Labadie O; Zhou Y Health Policy; 2010 May; 95(2-3):216-28. PubMed ID: 20036435 [TBL] [Abstract][Full Text] [Related]
19. The orphan drug backlash. Maeder T Sci Am; 2003 May; 288(5):80-7. PubMed ID: 12701333 [No Abstract] [Full Text] [Related]
20. The Orphan Drug Act Revisited. Thomas S; Caplan A JAMA; 2019 Mar; 321(9):833-834. PubMed ID: 30768155 [No Abstract] [Full Text] [Related] [Next] [New Search]