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4. Merits of combination cortical, subcortical, and cerebellar injections for the treatment of Niemann-Pick disease type A. Bu J; Ashe KM; Bringas J; Marshall J; Dodge JC; Cabrera-Salazar MA; Forsayeth J; Schuchman EH; Bankiewicz KS; Cheng SH; Shihabuddin LS; Passini MA Mol Ther; 2012 Oct; 20(10):1893-901. PubMed ID: 22828503 [TBL] [Abstract][Full Text] [Related]
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