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9. Functional amounts of dystrophin produced by skipping the mutated exon in the mdx dystrophic mouse. Lu QL; Mann CJ; Lou F; Bou-Gharios G; Morris GE; Xue SA; Fletcher S; Partridge TA; Wilton SD Nat Med; 2003 Aug; 9(8):1009-14. PubMed ID: 12847521 [TBL] [Abstract][Full Text] [Related]
10. Identification of an HLA-A*0201-restricted epitopic peptide from human dystrophin: application in duchenne muscular dystrophy gene therapy. Ginhoux F; Doucet C; Leboeuf M; Lemonnier FA; Danos O; Davoust J; Firat H Mol Ther; 2003 Aug; 8(2):274-83. PubMed ID: 12907150 [TBL] [Abstract][Full Text] [Related]
11. Gene therapy: the 'pro-sense' approach to Duchenne muscular dystrophy. van Deutekom JC Eur J Hum Genet; 2005 May; 13(5):518-9. PubMed ID: 15714219 [No Abstract] [Full Text] [Related]
12. In vivo targeted repair of a point mutation in the canine dystrophin gene by a chimeric RNA/DNA oligonucleotide. Bartlett RJ; Stockinger S; Denis MM; Bartlett WT; Inverardi L; Le TT; thi Man N; Morris GE; Bogan DJ; Metcalf-Bogan J; Kornegay JN Nat Biotechnol; 2000 Jun; 18(6):615-22. PubMed ID: 10835598 [TBL] [Abstract][Full Text] [Related]
13. Restoration of all dystrophin protein interactions by functional domains in trans does not rescue dystrophy. Gardner KL; Kearney JA; Edwards JD; Rafael-Fortney JA Gene Ther; 2006 May; 13(9):744-51. PubMed ID: 16307000 [TBL] [Abstract][Full Text] [Related]
14. Long-term expression of full-length human dystrophin in transgenic mdx mice expressing internally deleted human dystrophins. Ferrer A; Foster H; Wells KE; Dickson G; Wells DJ Gene Ther; 2004 Jun; 11(11):884-93. PubMed ID: 14985788 [TBL] [Abstract][Full Text] [Related]
15. Genetics. Hopping to a better protein. Pennisi E Science; 2008 Dec; 322(5907):1454-5. PubMed ID: 19056949 [No Abstract] [Full Text] [Related]
17. Therapeutic strategies for Duchenne and Becker dystrophies. Voisin V; de la Porte S Int Rev Cytol; 2004; 240():1-30. PubMed ID: 15548414 [TBL] [Abstract][Full Text] [Related]
18. Gene therapy for duchenne muscular dystrophy: expectations and challenges. Rodino-Klapac LR; Chicoine LG; Kaspar BK; Mendell JR Arch Neurol; 2007 Sep; 64(9):1236-41. PubMed ID: 17846262 [TBL] [Abstract][Full Text] [Related]
19. Exon skipping with morpholino oligomers: new treatment option for cardiomyopathy in Duchenne muscular dystrophy? Bauer R; Katus HA; Müller OJ Cardiovasc Res; 2010 Feb; 85(3):409-10. PubMed ID: 20008475 [No Abstract] [Full Text] [Related]