These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.
4. Injection of recombinant human sulfamidase into the CSF via the cerebellomedullary cistern in MPS IIIA mice. Hemsley KM; King B; Hopwood JJ Mol Genet Metab; 2007 Mar; 90(3):313-28. PubMed ID: 17166757 [TBL] [Abstract][Full Text] [Related]
5. Determination of the role of injection site on the efficacy of intra-CSF enzyme replacement therapy in MPS IIIA mice. Beard H; Luck AJ; Hassiotis S; King B; Trim PJ; Snel MF; Hopwood JJ; Hemsley KM Mol Genet Metab; 2015 May; 115(1):33-40. PubMed ID: 25795516 [TBL] [Abstract][Full Text] [Related]
6. Low-dose, continuous enzyme replacement therapy ameliorates brain pathology in the neurodegenerative lysosomal disorder mucopolysaccharidosis type IIIA. King B; Hassiotis S; Rozaklis T; Beard H; Trim PJ; Snel MF; Hopwood JJ; Hemsley KM J Neurochem; 2016 May; 137(3):409-22. PubMed ID: 26762778 [TBL] [Abstract][Full Text] [Related]
7. Slow, continuous enzyme replacement via spinal CSF in dogs with the paediatric-onset neurodegenerative disease, MPS IIIA. King B; Marshall NR; Hassiotis S; Trim PJ; Tucker J; Hattersley K; Snel MF; Jolly RD; Hopwood JJ; Hemsley KM J Inherit Metab Dis; 2017 May; 40(3):443-453. PubMed ID: 27832416 [TBL] [Abstract][Full Text] [Related]
8. Novel treatments and future perspectives: outcomes of intrathecal drug delivery. Dickson PI Int J Clin Pharmacol Ther; 2009; 47 Suppl 1():S124-7. PubMed ID: 20040323 [TBL] [Abstract][Full Text] [Related]
14. Intrathecal enzyme replacement therapy reduces lysosomal storage in the brain and meninges of the canine model of MPS I. Kakkis E; McEntee M; Vogler C; Le S; Levy B; Belichenko P; Mobley W; Dickson P; Hanson S; Passage M Mol Genet Metab; 2004; 83(1-2):163-74. PubMed ID: 15464431 [TBL] [Abstract][Full Text] [Related]
15. Disease stage determines the efficacy of treatment of a paediatric neurodegenerative disease. Hassiotis S; Beard H; Luck A; Trim PJ; King B; Snel MF; Hopwood JJ; Hemsley KM Eur J Neurosci; 2014 Jun; 39(12):2139-50. PubMed ID: 25068161 [TBL] [Abstract][Full Text] [Related]
16. Enzyme-replacement therapy from birth delays the development of behavior and learning problems in mucopolysaccharidosis type IIIA mice. Gliddon BL; Hopwood JJ Pediatr Res; 2004 Jul; 56(1):65-72. PubMed ID: 15128919 [TBL] [Abstract][Full Text] [Related]
17. CNS penetration of intrathecal-lumbar idursulfase in the monkey, dog and mouse: implications for neurological outcomes of lysosomal storage disorder. Calias P; Papisov M; Pan J; Savioli N; Belov V; Huang Y; Lotterhand J; Alessandrini M; Liu N; Fischman AJ; Powell JL; Heartlein MW PLoS One; 2012; 7(1):e30341. PubMed ID: 22279584 [TBL] [Abstract][Full Text] [Related]
18. Intracerebral injection of sulfamidase delays neuropathology in murine MPS-IIIA. Savas PS; Hemsley KM; Hopwood JJ Mol Genet Metab; 2004 Aug; 82(4):273-85. PubMed ID: 15308125 [TBL] [Abstract][Full Text] [Related]
19. Impact of high-dose, chemically modified sulfamidase on pathology in a murine model of MPS IIIA. Rozaklis T; Beard H; Hassiotis S; Garcia AR; Tonini M; Luck A; Pan J; Lamsa JC; Hopwood JJ; Hemsley KM Exp Neurol; 2011 Jul; 230(1):123-30. PubMed ID: 21515264 [TBL] [Abstract][Full Text] [Related]
20. Widespread gene transduction to the central nervous system by adenovirus in utero: implication for prenatal gene therapy to brain involvement of lysosomal storage disease. Shen JS; Meng XL; Maeda H; Ohashi T; Eto Y J Gene Med; 2004 Nov; 6(11):1206-15. PubMed ID: 15459963 [TBL] [Abstract][Full Text] [Related] [Next] [New Search]