BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

202 related articles for article (PubMed ID: 21254403)

  • 1. Parachuting in the epigenome: the biology of gene vector insertion profiles in the context of clinical trials.
    Baum C
    EMBO Mol Med; 2011 Feb; 3(2):75-7. PubMed ID: 21254403
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Integration profile of retroviral vector in gene therapy treated patients is cell-specific according to gene expression and chromatin conformation of target cell.
    Biasco L; Ambrosi A; Pellin D; Bartholomae C; Brigida I; Roncarolo MG; Di Serio C; von Kalle C; Schmidt M; Aiuti A
    EMBO Mol Med; 2011 Feb; 3(2):89-101. PubMed ID: 21243617
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Gene therapy for PIDs: progress, pitfalls and prospects.
    Mukherjee S; Thrasher AJ
    Gene; 2013 Aug; 525(2):174-81. PubMed ID: 23566838
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Gene therapy of primary T cell immunodeficiencies.
    Fischer A; Hacein-Bey-Abina S; Cavazzana-Calvo M
    Gene; 2013 Aug; 525(2):170-3. PubMed ID: 23583799
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Integration of retroviral vectors induces minor changes in the transcriptional activity of T cells from ADA-SCID patients treated with gene therapy.
    Cassani B; Montini E; Maruggi G; Ambrosi A; Mirolo M; Selleri S; Biral E; Frugnoli I; Hernandez-Trujillo V; Di Serio C; Roncarolo MG; Naldini L; Mavilio F; Aiuti A
    Blood; 2009 Oct; 114(17):3546-56. PubMed ID: 19652199
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Strategies for retrovirus-based correction of severe, combined immunodeficiency (SCID).
    Fischer A; Hacein-Bey-Abina S; Cavazzana-Calvo M
    Methods Enzymol; 2012; 507():15-27. PubMed ID: 22365767
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Gene therapy for severe combined immunodeficiency caused by adenosine deaminase deficiency: improved retroviral vectors for clinical trials.
    Onodera M; Nelson DM; Sakiyama Y; Candotti F; Blaese RM
    Acta Haematol; 1999; 101(2):89-96. PubMed ID: 10202239
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Recombinant adeno-associated virus-mediated gene transfer for the potential therapy of adenosine deaminase-deficient severe combined immune deficiency.
    Silver JN; Elder M; Conlon T; Cruz P; Wright AJ; Srivastava A; Flotte TR
    Hum Gene Ther; 2011 Aug; 22(8):935-49. PubMed ID: 21142972
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Gene therapy for severe combined immunodeficiencies.
    Gaspar HB; Thrasher AJ
    Expert Opin Biol Ther; 2005 Sep; 5(9):1175-82. PubMed ID: 16120048
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Stem cell gene therapy: the risks of insertional mutagenesis and approaches to minimize genotoxicity.
    Wu C; Dunbar CE
    Front Med; 2011 Dec; 5(4):356-71. PubMed ID: 22198747
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Genotoxicity of retroviral hematopoietic stem cell gene therapy.
    Trobridge GD
    Expert Opin Biol Ther; 2011 May; 11(5):581-93. PubMed ID: 21375467
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Cytoreductive conditioning intensity predicts clonal diversity in ADA-SCID retroviral gene therapy patients.
    Cooper AR; Lill GR; Shaw K; Carbonaro-Sarracino DA; Davila A; Sokolic R; Candotti F; Pellegrini M; Kohn DB
    Blood; 2017 May; 129(19):2624-2635. PubMed ID: 28351939
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Ten years of gene therapy for primary immune deficiencies.
    Aiuti A; Roncarolo MG
    Hematology Am Soc Hematol Educ Program; 2009; ():682-9. PubMed ID: 20008254
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Gene therapy for severe combined immunodeficiencies and beyond.
    Fischer A; Hacein-Bey-Abina S
    J Exp Med; 2020 Jan; 217(2):. PubMed ID: 31826240
    [TBL] [Abstract][Full Text] [Related]  

  • 15. LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1.
    Hacein-Bey-Abina S; Von Kalle C; Schmidt M; McCormack MP; Wulffraat N; Leboulch P; Lim A; Osborne CS; Pawliuk R; Morillon E; Sorensen R; Forster A; Fraser P; Cohen JI; de Saint Basile G; Alexander I; Wintergerst U; Frebourg T; Aurias A; Stoppa-Lyonnet D; Romana S; Radford-Weiss I; Gross F; Valensi F; Delabesse E; Macintyre E; Sigaux F; Soulier J; Leiva LE; Wissler M; Prinz C; Rabbitts TH; Le Deist F; Fischer A; Cavazzana-Calvo M
    Science; 2003 Oct; 302(5644):415-9. PubMed ID: 14564000
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Dynamics of gene-modified progenitor cells analyzed by tracking retroviral integration sites in a human SCID-X1 gene therapy trial.
    Wang GP; Berry CC; Malani N; Leboulch P; Fischer A; Hacein-Bey-Abina S; Cavazzana-Calvo M; Bushman FD
    Blood; 2010 Jun; 115(22):4356-66. PubMed ID: 20228274
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Twenty-Five Years of Gene Therapy for ADA-SCID: From Bubble Babies to an Approved Drug.
    Ferrua F; Aiuti A
    Hum Gene Ther; 2017 Nov; 28(11):972-981. PubMed ID: 28847159
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Multilineage hematopoietic reconstitution without clonal selection in ADA-SCID patients treated with stem cell gene therapy.
    Aiuti A; Cassani B; Andolfi G; Mirolo M; Biasco L; Recchia A; Urbinati F; Valacca C; Scaramuzza S; Aker M; Slavin S; Cazzola M; Sartori D; Ambrosi A; Di Serio C; Roncarolo MG; Mavilio F; Bordignon C
    J Clin Invest; 2007 Aug; 117(8):2233-40. PubMed ID: 17671653
    [TBL] [Abstract][Full Text] [Related]  

  • 19. [Gene therapy for adenosine deaminase deficiency].
    Sakiyama Y
    Hokkaido Igaku Zasshi; 1996 Jan; 71(1):27-32. PubMed ID: 8727372
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Towards a rAAV-based gene therapy for ADA-SCID: from ADA deficiency to current and future treatment strategies.
    Silver JN; Flotte TR
    Pharmacogenomics; 2008 Jul; 9(7):947-68. PubMed ID: 18597656
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 11.