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3. Quantitative Antisense Screening and Optimization for Exon 51 Skipping in Duchenne Muscular Dystrophy. Echigoya Y; Lim KRQ; Trieu N; Bao B; Miskew Nichols B; Vila MC; Novak JS; Hara Y; Lee J; Touznik A; Mamchaoui K; Aoki Y; Takeda S; Nagaraju K; Mouly V; Maruyama R; Duddy W; Yokota T Mol Ther; 2017 Nov; 25(11):2561-2572. PubMed ID: 28865998 [TBL] [Abstract][Full Text] [Related]
4. Direct Reprogramming of Human DMD Fibroblasts into Myotubes for In Vitro Evaluation of Antisense-Mediated Exon Skipping and Exons 45-55 Skipping Accompanied by Rescue of Dystrophin Expression. Lee JJA; Saito T; Duddy W; Takeda S; Yokota T Methods Mol Biol; 2018; 1828():141-150. PubMed ID: 30171539 [TBL] [Abstract][Full Text] [Related]
5. In Vitro Multiexon Skipping by Antisense PMOs in Dystrophic Dog and Exon 7-Deleted DMD Patient. Nakamura A; Aoki Y; Tsoumpra M; Yokota T; Takeda S Methods Mol Biol; 2018; 1828():151-163. PubMed ID: 30171540 [TBL] [Abstract][Full Text] [Related]
6. Exon Skipping Therapy Using Phosphorodiamidate Morpholino Oligomers in the mdx52 Mouse Model of Duchenne Muscular Dystrophy. Miyatake S; Mizobe Y; Takizawa H; Hara Y; Yokota T; Takeda S; Aoki Y Methods Mol Biol; 2018; 1687():123-141. PubMed ID: 29067660 [TBL] [Abstract][Full Text] [Related]
7. Antisense-induced exon skipping for duplications in Duchenne muscular dystrophy. Aartsma-Rus A; Janson AA; van Ommen GJ; van Deutekom JC BMC Med Genet; 2007 Jul; 8():43. PubMed ID: 17612397 [TBL] [Abstract][Full Text] [Related]
8. Multiexon skipping leading to an artificial DMD protein lacking amino acids from exons 45 through 55 could rescue up to 63% of patients with Duchenne muscular dystrophy. Béroud C; Tuffery-Giraud S; Matsuo M; Hamroun D; Humbertclaude V; Monnier N; Moizard MP; Voelckel MA; Calemard LM; Boisseau P; Blayau M; Philippe C; Cossée M; Pagès M; Rivier F; Danos O; Garcia L; Claustres M Hum Mutat; 2007 Feb; 28(2):196-202. PubMed ID: 17041910 [TBL] [Abstract][Full Text] [Related]
9. Contributions of Japanese patients to development of antisense therapy for DMD. Matsuo M; Takeshima Y; Nishio H Brain Dev; 2016 Jan; 38(1):4-9. PubMed ID: 26094594 [TBL] [Abstract][Full Text] [Related]
11. Exons 45-55 Skipping Using Mutation-Tailored Cocktails of Antisense Morpholinos in the DMD Gene. Echigoya Y; Lim KRQ; Melo D; Bao B; Trieu N; Mizobe Y; Maruyama R; Mamchaoui K; Tanihata J; Aoki Y; Takeda S; Mouly V; Duddy W; Yokota T Mol Ther; 2019 Nov; 27(11):2005-2017. PubMed ID: 31416775 [TBL] [Abstract][Full Text] [Related]
12. Skipping multiple exons of dystrophin transcripts using cocktail antisense oligonucleotides. Echigoya Y; Yokota T Nucleic Acid Ther; 2014 Feb; 24(1):57-68. PubMed ID: 24380394 [TBL] [Abstract][Full Text] [Related]
13. Bioinformatic and functional optimization of antisense phosphorodiamidate morpholino oligomers (PMOs) for therapeutic modulation of RNA splicing in muscle. Popplewell LJ; Graham IR; Malerba A; Dickson G Methods Mol Biol; 2011; 709():153-78. PubMed ID: 21194027 [TBL] [Abstract][Full Text] [Related]
14. Biochemical characterization of patients with in-frame or out-of-frame DMD deletions pertinent to exon 44 or 45 skipping. Anthony K; Arechavala-Gomeza V; Ricotti V; Torelli S; Feng L; Janghra N; Tasca G; Guglieri M; Barresi R; Armaroli A; Ferlini A; Bushby K; Straub V; Ricci E; Sewry C; Morgan J; Muntoni F JAMA Neurol; 2014 Jan; 71(1):32-40. PubMed ID: 24217213 [TBL] [Abstract][Full Text] [Related]
15. Exons 45-55 Skipping Using Antisense Oligonucleotides in Immortalized Human DMD Muscle Cells. He M; Yokota T Methods Mol Biol; 2023; 2640():313-325. PubMed ID: 36995604 [TBL] [Abstract][Full Text] [Related]
16. Systemic Delivery of Morpholinos to Skip Multiple Exons in a Dog Model of Duchenne Muscular Dystrophy. Maruyama R; Echigoya Y; Caluseriu O; Aoki Y; Takeda S; Yokota T Methods Mol Biol; 2017; 1565():201-213. PubMed ID: 28364245 [TBL] [Abstract][Full Text] [Related]
17. Theoretic applicability of antisense-mediated exon skipping for Duchenne muscular dystrophy mutations. Aartsma-Rus A; Fokkema I; Verschuuren J; Ginjaar I; van Deutekom J; van Ommen GJ; den Dunnen JT Hum Mutat; 2009 Mar; 30(3):293-9. PubMed ID: 19156838 [TBL] [Abstract][Full Text] [Related]
18. Antisense oligonucleotide-induced exon skipping restores dystrophin expression in vitro in a canine model of DMD. McClorey G; Moulton HM; Iversen PL; Fletcher S; Wilton SD Gene Ther; 2006 Oct; 13(19):1373-81. PubMed ID: 16724091 [TBL] [Abstract][Full Text] [Related]
19. [Exon skipping therapy for Duchenne muscular dystrophy by using antisense Morpholino]. Takeda S Rinsho Shinkeigaku; 2009 Nov; 49(11):856-8. PubMed ID: 20030230 [TBL] [Abstract][Full Text] [Related]
20. Comparative analysis of antisense oligonucleotide analogs for targeted DMD exon 46 skipping in muscle cells. Aartsma-Rus A; Kaman WE; Bremmer-Bout M; Janson AA; den Dunnen JT; van Ommen GJ; van Deutekom JC Gene Ther; 2004 Sep; 11(18):1391-8. PubMed ID: 15229633 [TBL] [Abstract][Full Text] [Related] [Next] [New Search]