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2. Ocular lesions in canine mucopolysaccharidosis I and response to enzyme replacement therapy. Newkirk KM; Atkins RM; Dickson PI; Rohrbach BW; McEntee MF Invest Ophthalmol Vis Sci; 2011 Jul; 52(8):5130-5. PubMed ID: 21436264 [TBL] [Abstract][Full Text] [Related]
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7. Intrathecal enzyme replacement therapy reduces lysosomal storage in the brain and meninges of the canine model of MPS I. Kakkis E; McEntee M; Vogler C; Le S; Levy B; Belichenko P; Mobley W; Dickson P; Hanson S; Passage M Mol Genet Metab; 2004; 83(1-2):163-74. PubMed ID: 15464431 [TBL] [Abstract][Full Text] [Related]
8. Glycosaminoglycan storage in neuroanatomical regions of mucopolysaccharidosis I dogs following intrathecal recombinant human iduronidase. Chen A; Vogler C; McEntee M; Hanson S; Ellinwood NM; Jens J; Snella E; Passage M; Le S; Guerra C; Dickson P APMIS; 2011 Aug; 119(8):513-21. PubMed ID: 21749451 [TBL] [Abstract][Full Text] [Related]
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10. Gene therapy for a mucopolysaccharidosis type I murine model with lentiviral-IDUA vector. Di Domenico C; Villani GR; Di Napoli D; Reyero EG; Lombardo A; Naldini L; Di Natale P Hum Gene Ther; 2005 Jan; 16(1):81-90. PubMed ID: 15703491 [TBL] [Abstract][Full Text] [Related]
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13. Neonatal tolerance induction enables accurate evaluation of gene therapy for MPS I in a canine model. Hinderer C; Bell P; Louboutin JP; Katz N; Zhu Y; Lin G; Choa R; Bagel J; O'Donnell P; Fitzgerald CA; Langan T; Wang P; Casal ML; Haskins ME; Wilson JM Mol Genet Metab; 2016 Sep; 119(1-2):124-30. PubMed ID: 27386755 [TBL] [Abstract][Full Text] [Related]
14. Limited transgene immune response and long-term expression of human alpha-L-iduronidase in young adult mice with mucopolysaccharidosis type I by liver-directed gene therapy. Di Domenico C; Di Napoli D; Gonzalez Y Reyero E; Lombardo A; Naldini L; Di Natale P Hum Gene Ther; 2006 Nov; 17(11):1112-21. PubMed ID: 17044753 [TBL] [Abstract][Full Text] [Related]
15. Enzyme replacement therapy in feline mucopolysaccharidosis I. Kakkis ED; Schuchman E; He X; Wan Q; Kania S; Wiemelt S; Hasson CW; O'Malley T; Weil MA; Aguirre GA; Brown DE; Haskins ME Mol Genet Metab; 2001 Mar; 72(3):199-208. PubMed ID: 11243725 [TBL] [Abstract][Full Text] [Related]
16. Morphologic and biochemical studies of canine mucopolysaccharidosis I. Shull RM; Helman RG; Spellacy E; Constantopoulos G; Munger RJ; Neufeld EF Am J Pathol; 1984 Mar; 114(3):487-95. PubMed ID: 6320652 [TBL] [Abstract][Full Text] [Related]