173 related articles for article (PubMed ID: 21620910)
41. Surface modified poly(β amino ester)-containing nanoparticles for plasmid DNA delivery.
Fields RJ; Cheng CJ; Quijano E; Weller C; Kristofik N; Duong N; Hoimes C; Egan ME; Saltzman WM
J Control Release; 2012 Nov; 164(1):41-8. PubMed ID: 23041278
[TBL] [Abstract][Full Text] [Related]
42. Efficient modification of CCR5 in primary human hematopoietic cells using a megaTAL nuclease and AAV donor template.
Sather BD; Romano Ibarra GS; Sommer K; Curinga G; Hale M; Khan IF; Singh S; Song Y; Gwiazda K; Sahni J; Jarjour J; Astrakhan A; Wagner TA; Scharenberg AM; Rawlings DJ
Sci Transl Med; 2015 Sep; 7(307):307ra156. PubMed ID: 26424571
[TBL] [Abstract][Full Text] [Related]
43. Polymer-based siRNA delivery: perspectives on the fundamental and phenomenological distinctions from polymer-based DNA delivery.
Gary DJ; Puri N; Won YY
J Control Release; 2007 Aug; 121(1-2):64-73. PubMed ID: 17588702
[TBL] [Abstract][Full Text] [Related]
44. Long-term multilineage engraftment of autologous genome-edited hematopoietic stem cells in nonhuman primates.
Peterson CW; Wang J; Norman KK; Norgaard ZK; Humbert O; Tse CK; Yan JJ; Trimble RG; Shivak DA; Rebar EJ; Gregory PD; Holmes MC; Kiem HP
Blood; 2016 May; 127(20):2416-26. PubMed ID: 26980728
[TBL] [Abstract][Full Text] [Related]
45. Homology-driven genome editing in hematopoietic stem and progenitor cells using ZFN mRNA and AAV6 donors.
Wang J; Exline CM; DeClercq JJ; Llewellyn GN; Hayward SB; Li PW; Shivak DA; Surosky RT; Gregory PD; Holmes MC; Cannon PM
Nat Biotechnol; 2015 Dec; 33(12):1256-1263. PubMed ID: 26551060
[TBL] [Abstract][Full Text] [Related]
46. Preclinical modeling highlights the therapeutic potential of hematopoietic stem cell gene editing for correction of SCID-X1.
Schiroli G; Ferrari S; Conway A; Jacob A; Capo V; Albano L; Plati T; Castiello MC; Sanvito F; Gennery AR; Bovolenta C; Palchaudhuri R; Scadden DT; Holmes MC; Villa A; Sitia G; Lombardo A; Genovese P; Naldini L
Sci Transl Med; 2017 Oct; 9(411):. PubMed ID: 29021165
[TBL] [Abstract][Full Text] [Related]
47. Current approaches and potential challenges in the delivery of gene editing cargos into hematopoietic stem and progenitor cells.
Murugesan R; Karuppusamy KV; Marepally S; Thangavel S
Front Genome Ed; 2023; 5():1148693. PubMed ID: 37780116
[TBL] [Abstract][Full Text] [Related]
48. Delivery of Genome Editing Reagents to Hematopoietic Stem/Progenitor Cells.
Hoban MD; Romero Z; Cost GJ; Mendel M; Holmes M; Kohn DB
Curr Protoc Stem Cell Biol; 2016 Feb; 36():5B.4.1-5B.4.10. PubMed ID: 26840227
[TBL] [Abstract][Full Text] [Related]
49. Comb-type copolymers for controlled DNA delivery.
Maruyama A; Ferdous A; Ishihara T; Asayama S; Park JU; Nogawa M; Watanabe H; Takei Y; Akaike T
Nucleosides Nucleotides; 1999; 18(6-7):1681-2. PubMed ID: 10474245
[TBL] [Abstract][Full Text] [Related]
50. Poly(β-amino ester)-based gene delivery systems: From discovery to therapeutic applications.
Cordeiro RA; Serra A; Coelho JFJ; Faneca H
J Control Release; 2019 Sep; 310():155-187. PubMed ID: 31454533
[TBL] [Abstract][Full Text] [Related]
51. A New Era for Hemoglobinopathies: More Than One Curative Option.
Psatha N; Papayanni PG; Yannaki E
Curr Gene Ther; 2017; 17(5):364-378. PubMed ID: 29357790
[TBL] [Abstract][Full Text] [Related]
52. Nanoparticles that deliver triplex-forming peptide nucleic acid molecules correct F508del CFTR in airway epithelium.
McNeer NA; Anandalingam K; Fields RJ; Caputo C; Kopic S; Gupta A; Quijano E; Polikoff L; Kong Y; Bahal R; Geibel JP; Glazer PM; Saltzman WM; Egan ME
Nat Commun; 2015 Apr; 6():6952. PubMed ID: 25914116
[TBL] [Abstract][Full Text] [Related]
53. Highly biocompatible, hollow coordination polymer nanoparticles as cisplatin carriers for efficient intracellular drug delivery.
Lian HY; Hu M; Liu CH; Yamauchi Y; Wu KC
Chem Commun (Camb); 2012 May; 48(42):5151-3. PubMed ID: 22514015
[TBL] [Abstract][Full Text] [Related]
54. Delivery of Peptide Nucleic Acids Using an Argininocalix[4]arene as Vector.
Finotti A; Gasparello J; Casnati A; Corradini R; Gambari R; Sansone F
Methods Mol Biol; 2021; 2211():123-143. PubMed ID: 33336275
[TBL] [Abstract][Full Text] [Related]
55. Debugging the genetic code: non-viral
Piotrowski-Daspit AS; Glaze PM; Saltzman WM
Curr Opin Biomed Eng; 2018 Sep; 7():24-32. PubMed ID: 30984891
[TBL] [Abstract][Full Text] [Related]
56. Cationic Polymer-Mediated CRISPR/Cas9 Plasmid Delivery for Genome Editing.
Zhang Z; Wan T; Chen Y; Chen Y; Sun H; Cao T; Songyang Z; Tang G; Wu C; Ping Y; Xu FJ; Huang J
Macromol Rapid Commun; 2019 Mar; 40(5):e1800068. PubMed ID: 29708298
[TBL] [Abstract][Full Text] [Related]
57. Engineering HIV-1-resistant T-cells from short-hairpin RNA-expressing hematopoietic stem/progenitor cells in humanized BLT mice.
Ringpis GE; Shimizu S; Arokium H; Camba-Colón J; Carroll MV; Cortado R; Xie Y; Kim PY; Sahakyan A; Lowe EL; Narukawa M; Kandarian FN; Burke BP; Symonds GP; An DS; Chen IS; Kamata M
PLoS One; 2012; 7(12):e53492. PubMed ID: 23300932
[TBL] [Abstract][Full Text] [Related]
58. Combined lentiviral- and RNA-mediated CRISPR/Cas9 delivery for efficient and traceable gene editing in human hematopoietic stem and progenitor cells.
Yudovich D; Bäckström A; Schmiderer L; Žemaitis K; Subramaniam A; Larsson J
Sci Rep; 2020 Dec; 10(1):22393. PubMed ID: 33372184
[TBL] [Abstract][Full Text] [Related]
59. Lentivector Knockdown of CCR5 in Hematopoietic Stem and Progenitor Cells Confers Functional and Persistent HIV-1 Resistance in Humanized Mice.
Myburgh R; Ivic S; Pepper MS; Gers-Huber G; Li D; Audigé A; Rochat MA; Jaquet V; Regenass S; Manz MG; Salmon P; Krause KH; Speck RF
J Virol; 2015 Jul; 89(13):6761-72. PubMed ID: 25903342
[TBL] [Abstract][Full Text] [Related]
60. Modulation of Gene Expression by Polymer Nanocapsule Delivery of DNA Cassettes Encoding Small RNAs.
Yan M; Wen J; Liang M; Lu Y; Kamata M; Chen IS
PLoS One; 2015; 10(6):e0127986. PubMed ID: 26035832
[TBL] [Abstract][Full Text] [Related]
[Previous] [Next] [New Search]