208 related articles for article (PubMed ID: 21944884)
1. Pathogenesis of aortic dilatation in mucopolysaccharidosis VII mice may involve complement activation.
Baldo G; Wu S; Howe RA; Ramamoothy M; Knutsen RH; Fang J; Mecham RP; Liu Y; Wu X; Atkinson JP; Ponder KP
Mol Genet Metab; 2011 Dec; 104(4):608-19. PubMed ID: 21944884
[TBL] [Abstract][Full Text] [Related]
2. Upregulation of elastase activity in aorta in mucopolysaccharidosis I and VII dogs may be due to increased cytokine expression.
Metcalf JA; Linders B; Wu S; Bigg P; O'Donnell P; Sleeper MM; Whyte MP; Haskins M; Ponder KP
Mol Genet Metab; 2010 Apr; 99(4):396-407. PubMed ID: 20044292
[TBL] [Abstract][Full Text] [Related]
3. Upregulation of elastase proteins results in aortic dilatation in mucopolysaccharidosis I mice.
Ma X; Tittiger M; Knutsen RH; Kovacs A; Schaller L; Mecham RP; Ponder KP
Mol Genet Metab; 2008 Jul; 94(3):298-304. PubMed ID: 18479957
[TBL] [Abstract][Full Text] [Related]
4. Pathogenesis of mitral valve disease in mucopolysaccharidosis VII dogs.
Bigg PW; Baldo G; Sleeper MM; O'Donnell PA; Bai H; Rokkam VR; Liu Y; Wu S; Giugliani R; Casal ML; Haskins ME; Ponder KP
Mol Genet Metab; 2013 Nov; 110(3):319-28. PubMed ID: 23856419
[TBL] [Abstract][Full Text] [Related]
5. Gene therapy ameliorates cardiovascular disease in dogs with mucopolysaccharidosis VII.
Sleeper MM; Fornasari B; Ellinwood NM; Weil MA; Melniczek J; O'Malley TM; Sammarco CD; Xu L; Ponder KP; Haskins ME
Circulation; 2004 Aug; 110(7):815-20. PubMed ID: 15289379
[TBL] [Abstract][Full Text] [Related]
6. The effect of neonatal gene therapy with a gamma retroviral vector on cardiac valve disease in mucopolysaccharidosis VII dogs after a decade.
Bigg PW; Sleeper MM; O'Donnell PA; Liu Y; Wu S; Casal ML; Haskins ME; Ponder KP
Mol Genet Metab; 2013 Nov; 110(3):311-8. PubMed ID: 23860311
[TBL] [Abstract][Full Text] [Related]
7. Vestronidase alfa: Recombinant human β-glucuronidase as an enzyme replacement therapy for MPS VII.
Cadaoas J; Boyle G; Jungles S; Cullen S; Vellard M; Grubb JH; Jurecka A; Sly W; Kakkis E
Mol Genet Metab; 2020 May; 130(1):65-76. PubMed ID: 32192868
[TBL] [Abstract][Full Text] [Related]
8. Evaluation of pathological manifestations of disease in mucopolysaccharidosis VII mice after neonatal hepatic gene therapy.
Xu L; Mango RL; Sands MS; Haskins ME; Ellinwood NM; Ponder KP
Mol Ther; 2002 Dec; 6(6):745-58. PubMed ID: 12498771
[TBL] [Abstract][Full Text] [Related]
9. Neonatal retroviral vector-mediated hepatic gene therapy reduces bone, joint, and cartilage disease in mucopolysaccharidosis VII mice and dogs.
Mango RL; Xu L; Sands MS; Vogler C; Seiler G; Schwarz T; Haskins ME; Ponder KP
Mol Genet Metab; 2004 May; 82(1):4-19. PubMed ID: 15110316
[TBL] [Abstract][Full Text] [Related]
10. Effect of neonatal gene therapy on lumbar spine disease in mucopolysaccharidosis VII dogs.
Smith LJ; Martin JT; O'Donnell P; Wang P; Elliott DM; Haskins ME; Ponder KP
Mol Genet Metab; 2012 Sep; 107(1-2):145-52. PubMed ID: 22510705
[TBL] [Abstract][Full Text] [Related]
11. The effect of Tlr4 and/or C3 deficiency and of neonatal gene therapy on skeletal disease in mucopolysaccharidosis VII mice.
Xing EM; Wu S; Ponder KP
Mol Genet Metab; 2015 Feb; 114(2):209-16. PubMed ID: 25559179
[TBL] [Abstract][Full Text] [Related]
12. AAV-mediated intravitreal gene therapy reduces lysosomal storage in the retinal pigmented epithelium and improves retinal function in adult MPS VII mice.
Hennig AK; Ogilvie JM; Ohlemiller KK; Timmers AM; Hauswirth WW; Sands MS
Mol Ther; 2004 Jul; 10(1):106-16. PubMed ID: 15233947
[TBL] [Abstract][Full Text] [Related]
13. Transgene produces massive overexpression of human beta -glucuronidase in mice, lysosomal storage of enzyme, and strain-dependent tumors.
Vogler C; Galvin N; Levy B; Grubb J; Jiang J; Zhou XY; Sly WS
Proc Natl Acad Sci U S A; 2003 Mar; 100(5):2669-73. PubMed ID: 12591953
[TBL] [Abstract][Full Text] [Related]
14. Murine mucopolysaccharidosis type VII: the impact of therapies on the clinical course and pathology in a murine model of lysosomal storage disease.
Vogler C; Sands MS; Galvin N; Levy B; Thorpe C; Barker J; Sly WS
J Inherit Metab Dis; 1998 Aug; 21(5):575-86. PubMed ID: 9728337
[TBL] [Abstract][Full Text] [Related]
15. Clinical response to persistent, low-level beta-glucuronidase expression in the murine model of mucopolysaccharidosis type VII.
Donsante A; Levy B; Vogler C; Sands MS
J Inherit Metab Dis; 2007 Apr; 30(2):227-38. PubMed ID: 17308887
[TBL] [Abstract][Full Text] [Related]
16. Pathogenesis of lumbar spine disease in mucopolysaccharidosis VII.
Smith LJ; Baldo G; Wu S; Liu Y; Whyte MP; Giugliani R; Elliott DM; Haskins ME; Ponder KP
Mol Genet Metab; 2012 Sep; 107(1-2):153-60. PubMed ID: 22513347
[TBL] [Abstract][Full Text] [Related]
17. Lentiviral-mediated gene therapy results in sustained expression of β-glucuronidase for up to 12 months in the gus(mps/mps) and up to 18 months in the gus(tm(L175F)Sly) mouse models of mucopolysaccharidosis type VII.
Derrick-Roberts AL; Pyragius CE; Kaidonis XM; Jackson MR; Anson DS; Byers S
Hum Gene Ther; 2014 Sep; 25(9):798-810. PubMed ID: 25003807
[TBL] [Abstract][Full Text] [Related]
18. Treatment of a lysosomal storage disease, mucopolysaccharidosis VII, with microencapsulated recombinant cells.
Ross CJ; Bastedo L; Maier SA; Sands MS; Chang PL
Hum Gene Ther; 2000 Oct; 11(15):2117-27. PubMed ID: 11044913
[TBL] [Abstract][Full Text] [Related]
19. Widespread correction of lysosomal storage following intrahepatic injection of a recombinant adeno-associated virus in the adult MPS VII mouse.
Sferra TJ; Backstrom K; Wang C; Rennard R; Miller M; Hu Y
Mol Ther; 2004 Sep; 10(3):478-91. PubMed ID: 15336648
[TBL] [Abstract][Full Text] [Related]
20. Accumulation of abnormal amounts of glycosaminoglycans in murine mucopolysaccharidosis type VII neural progenitor cells does not alter the growth rate or efficiency of differentiation into neurons.
Heuer GG; Skorupa AF; Prasad Alur RK; Jiang K; Wolfe JH
Mol Cell Neurosci; 2001 Jan; 17(1):167-78. PubMed ID: 11161477
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]
