These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.


BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

188 related articles for article (PubMed ID: 21959273)

  • 1. Gene therapies advance towards finish line.
    Mullard A
    Nat Rev Drug Discov; 2011 Sep; 10(10):719-20. PubMed ID: 21959273
    [No Abstract]   [Full Text] [Related]  

  • 2. Gene therapy: Industrial strength.
    Bender E
    Nature; 2016 Sep; 537(7619):S57-9. PubMed ID: 27602741
    [No Abstract]   [Full Text] [Related]  

  • 3. [Gene therapy and rare diseases].
    Cohen-Haguenauer O
    Rev Med Interne; 2011 Dec; 32 Suppl 2():S210-2. PubMed ID: 22037347
    [No Abstract]   [Full Text] [Related]  

  • 4. The Platform Vector Gene Therapies Project: Increasing the Efficiency of Adeno-Associated Virus Gene Therapy Clinical Trial Startup.
    Brooks PJ; Ottinger EA; Portero D; Lomash RM; Alimardanov A; Terse P; Xu X; Chandler RJ; Geist Hauserman J; Esposito E; Bönnemann CG; Venditti CP; Austin CP; Pariser A; Lo DC
    Hum Gene Ther; 2020 Oct; 31(19-20):1034-1042. PubMed ID: 32993373
    [No Abstract]   [Full Text] [Related]  

  • 5. Gene therapies need new development models.
    Mavilio F
    Nature; 2012 Oct; 490(7418):7. PubMed ID: 23038429
    [No Abstract]   [Full Text] [Related]  

  • 6. Glybera and the future of gene therapy in the European Union.
    Miller N
    Nat Rev Drug Discov; 2012 May; 11(5):419. PubMed ID: 22679644
    [No Abstract]   [Full Text] [Related]  

  • 7. Gene therapy of inherited diseases.
    Fischer A; Cavazzana-Calvo M
    Lancet; 2008 Jun; 371(9629):2044-7. PubMed ID: 18555917
    [No Abstract]   [Full Text] [Related]  

  • 8. Gene therapy enters the pharma market: the short story of a long journey.
    Büning H
    EMBO Mol Med; 2013 Jan; 5(1):1-3. PubMed ID: 23283747
    [No Abstract]   [Full Text] [Related]  

  • 9. Bumps in the Road for Commercial Gene Therapy for Rare Diseases.
    Ylä-Herttuala S
    Mol Ther; 2017 Oct; 25(10):2225. PubMed ID: 28939088
    [No Abstract]   [Full Text] [Related]  

  • 10. Dual Purpose Vectors for Rare Neurological Diseases.
    Bigger BW
    Mol Ther; 2020 Oct; 28(10):2104-2105. PubMed ID: 32949496
    [No Abstract]   [Full Text] [Related]  

  • 11. Gene-therapy trials must proceed with caution.
    Nature; 2016 Jun; 534(7609):590. PubMed ID: 27357758
    [No Abstract]   [Full Text] [Related]  

  • 12. Designer viruses could be the secret to cheaper and better gene therapy.
    Savage N
    Nature; 2018 Dec; 564(7735):S18-S19. PubMed ID: 30542181
    [No Abstract]   [Full Text] [Related]  

  • 13. The Bespoke Gene Therapy Consortium: facilitating development of AAV gene therapies for rare diseases.
    Brooks PJ; Miller TM; Revah F; Suh J; Garrison BR; Starke LC; MacLachlan TK; Neilan EG; Raychaudhuri G; Kassim SH; Dehdashti J; Rutter JL
    Nat Rev Drug Discov; 2024 Mar; 23(3):157-158. PubMed ID: 38321319
    [No Abstract]   [Full Text] [Related]  

  • 14. A patient and family perspective on gene therapy for rare diseases.
    Kent A; Oosterwijk C
    J Gene Med; 2007 Oct; 9(10):922-3. PubMed ID: 17880044
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Streamlined collaboration can boost CRISPR gene therapies for rare diseases.
    He W; Zeng S; Xu C
    Nature; 2024 Jul; 631(8019):28. PubMed ID: 38956334
    [No Abstract]   [Full Text] [Related]  

  • 16. [The time has come of a therapeutic (re)positioning of the ultra-rare diseases].
    Martinat C; Peschanski M
    Med Sci (Paris); 2018 Dec; 34(12):1019-1021. PubMed ID: 30623755
    [No Abstract]   [Full Text] [Related]  

  • 17. [Rare diseases and the CRISPR technology...].
    Carayon P; Cler E; By Y
    Ann Biol Clin (Paris); 2016; 74(2):125-9. PubMed ID: 27029719
    [No Abstract]   [Full Text] [Related]  

  • 18. "Profoundly Saddened" Lysogene Discloses Child's Death in Phase II/III Trial.
    Philippidis A
    Hum Gene Ther; 2020 Nov; 31(21-22):1141-1143. PubMed ID: 33200963
    [No Abstract]   [Full Text] [Related]  

  • 19. 'Bespoke Gene Therapy Consortium' sets out to enable gene therapies for ultra-rare diseases.
    Kingwell K
    Nat Rev Drug Discov; 2021 Dec; 20(12):886-887. PubMed ID: 34773079
    [No Abstract]   [Full Text] [Related]  

  • 20. The consortium project to treat RPE65 deficiency in humans.
    Hauswirth WW
    Retina; 2005 Dec; 25(8 Suppl):S60. PubMed ID: 16374340
    [No Abstract]   [Full Text] [Related]  

    [Next]    [New Search]
    of 10.