These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.
6. Recombinant adeno-associated virus delivers human factor IX in mice. Stewart A Mol Med Today; 1997 Sep; 3(9):368. PubMed ID: 9302683 [No Abstract] [Full Text] [Related]
7. Adeno-associated virus-mediated gene transfer of factor IX for treatment of hemophilia B by gene therapy. Herzog RW; High KA Thromb Haemost; 1999 Aug; 82(2):540-6. PubMed ID: 10605748 [No Abstract] [Full Text] [Related]
9. Moving forward toward a cure for hemophilia B. VandenDriessche T; Chuah MK Mol Ther; 2015 May; 23(5):809-811. PubMed ID: 25943496 [No Abstract] [Full Text] [Related]
10. Functions of AAV-CMV-F.IX And AAV-EF1alpha-F.IX in gene therapy for hemophilia B. Wiwanitkit V Hum Gene Ther; 2007 Feb; 18(2):89-92. PubMed ID: 17266422 [TBL] [Abstract][Full Text] [Related]
11. Gene therapy for hemophilia: are viral vectors really feasible? Walsh C J Thromb Haemost; 2003 Feb; 1(2):218-9. PubMed ID: 12871491 [No Abstract] [Full Text] [Related]
12. Hemophilia. After a setback, gene therapy progresses...gingerly. Gura T Science; 2001 Mar; 291(5509):1692-7. PubMed ID: 11253191 [No Abstract] [Full Text] [Related]
13. Direct intramuscular injection with recombinant AAV vectors results in sustained expression in a dog model of hemophilia. Monahan PE; Samulski RJ; Tazelaar J; Xiao X; Nichols TC; Bellinger DA; Read MS; Walsh CE Gene Ther; 1998 Jan; 5(1):40-9. PubMed ID: 9536263 [TBL] [Abstract][Full Text] [Related]
14. Our journey to successful gene therapy for hemophilia B. Nathwani AC; Nienhuis AW; Davidoff AM Hum Gene Ther; 2014 Nov; 25(11):923-6. PubMed ID: 25397929 [No Abstract] [Full Text] [Related]
15. Genetic Targeting of the Albumin Locus to Treat Hemophilia. Davidoff AM; Nathwani AC N Engl J Med; 2016 Mar; 374(13):1288-90. PubMed ID: 27028920 [No Abstract] [Full Text] [Related]
16. FIX It in One Go: Enhanced Factor IX Gene Therapy for Hemophilia B. Lillicrap D Cell; 2017 Dec; 171(7):1478-1480. PubMed ID: 29245009 [TBL] [Abstract][Full Text] [Related]
17. Gene therapy, an ongoing revolution. Benveniste O Blood; 2012 Mar; 119(13):2973-4. PubMed ID: 22461470 [TBL] [Abstract][Full Text] [Related]
18. Immune responses to AAV capsid: are mice not humans after all? Herzog RW Mol Ther; 2007 Apr; 15(4):649-50. PubMed ID: 17372595 [No Abstract] [Full Text] [Related]
19. A first step toward gene therapy for hemophilia B? Marx J Science; 1993 Oct; 262(5130):29-30. PubMed ID: 8211125 [No Abstract] [Full Text] [Related]