310 related articles for article (PubMed ID: 22509403)
1. AAV-mediated cone rescue in a naturally occurring mouse model of CNGA3-achromatopsia.
Pang JJ; Deng WT; Dai X; Lei B; Everhart D; Umino Y; Li J; Zhang K; Mao S; Boye SL; Liu L; Chiodo VA; Liu X; Shi W; Tao Y; Chang B; Hauswirth WW
PLoS One; 2012; 7(4):e35250. PubMed ID: 22509403
[TBL] [Abstract][Full Text] [Related]
2. Long-term retinal cone rescue using a capsid mutant AAV8 vector in a mouse model of CNGA3-achromatopsia.
Dai X; He Y; Zhang H; Zhang Y; Liu Y; Wang M; Chen H; Pang JJ
PLoS One; 2017; 12(11):e0188032. PubMed ID: 29131863
[TBL] [Abstract][Full Text] [Related]
3. Six Years and Counting: Restoration of Photopic Retinal Function and Visual Behavior Following Gene Augmentation Therapy in a Sheep Model of
Ofri R; Averbukh E; Ezra-Elia R; Ross M; Honig H; Obolensky A; Rosov A; Hauswirth WW; Gootwine E; Banin E
Hum Gene Ther; 2018 Dec; 29(12):1376-1386. PubMed ID: 29926749
[TBL] [Abstract][Full Text] [Related]
4. Vitreal delivery of AAV vectored Cnga3 restores cone function in CNGA3-/-/Nrl-/- mice, an all-cone model of CNGA3 achromatopsia.
Du W; Tao Y; Deng WT; Zhu P; Li J; Dai X; Zhang Y; Shi W; Liu X; Chiodo VA; Ding XQ; Zhao C; Michalakis S; Biel M; Zhang Z; Qu J; Hauswirth WW; Pang JJ
Hum Mol Genet; 2015 Jul; 24(13):3699-707. PubMed ID: 25855802
[TBL] [Abstract][Full Text] [Related]
5. Gene Augmentation Therapy Restores Retinal Function and Visual Behavior in a Sheep Model of CNGA3 Achromatopsia.
Banin E; Gootwine E; Obolensky A; Ezra-Elia R; Ejzenberg A; Zelinger L; Honig H; Rosov A; Yamin E; Sharon D; Averbukh E; Hauswirth WW; Ofri R
Mol Ther; 2015 Sep; 23(9):1423-33. PubMed ID: 26087757
[TBL] [Abstract][Full Text] [Related]
6. Safety and Efficacy Evaluation of rAAV2tYF-PR1.7-hCNGA3 Vector Delivered by Subretinal Injection in CNGA3 Mutant Achromatopsia Sheep.
Gootwine E; Ofri R; Banin E; Obolensky A; Averbukh E; Ezra-Elia R; Ross M; Honig H; Rosov A; Yamin E; Ye GJ; Knop DR; Robinson PM; Chulay JD; Shearman MS
Hum Gene Ther Clin Dev; 2017 Jun; 28(2):96-107. PubMed ID: 28478700
[TBL] [Abstract][Full Text] [Related]
7. Safety and Vision Outcomes of Subretinal Gene Therapy Targeting Cone Photoreceptors in Achromatopsia: A Nonrandomized Controlled Trial.
Fischer MD; Michalakis S; Wilhelm B; Zobor D; Muehlfriedel R; Kohl S; Weisschuh N; Ochakovski GA; Klein R; Schoen C; Sothilingam V; Garcia-Garrido M; Kuehlewein L; Kahle N; Werner A; Dauletbekov D; Paquet-Durand F; Tsang S; Martus P; Peters T; Seeliger M; Bartz-Schmidt KU; Ueffing M; Zrenner E; Biel M; Wissinger B
JAMA Ophthalmol; 2020 Jun; 138(6):643-651. PubMed ID: 32352493
[TBL] [Abstract][Full Text] [Related]
8. Long-term and age-dependent restoration of visual function in a mouse model of CNGB3-associated achromatopsia following gene therapy.
Carvalho LS; Xu J; Pearson RA; Smith AJ; Bainbridge JW; Morris LM; Fliesler SJ; Ding XQ; Ali RR
Hum Mol Genet; 2011 Aug; 20(16):3161-75. PubMed ID: 21576125
[TBL] [Abstract][Full Text] [Related]
9. Achromatopsia as a potential candidate for gene therapy.
Pang JJ; Alexander J; Lei B; Deng W; Zhang K; Li Q; Chang B; Hauswirth WW
Adv Exp Med Biol; 2010; 664():639-46. PubMed ID: 20238068
[TBL] [Abstract][Full Text] [Related]
10. Gene therapy restores missing cone-mediated vision in the CNGA3-/- mouse model of achromatopsia.
Michalakis S; Mühlfriedel R; Tanimoto N; Krishnamoorthy V; Koch S; Fischer MD; Becirovic E; Bai L; Huber G; Beck SC; Fahl E; Büning H; Schmidt J; Zong X; Gollisch T; Biel M; Seeliger MW
Adv Exp Med Biol; 2012; 723():183-9. PubMed ID: 22183332
[No Abstract] [Full Text] [Related]
11. Safety and Efficacy of AAV5 Vectors Expressing Human or Canine CNGB3 in CNGB3-Mutant Dogs.
Ye GJ; Komáromy AM; Zeiss C; Calcedo R; Harman CD; Koehl KL; Stewart GA; Iwabe S; Chiodo VA; Hauswirth WW; Aguirre GD; Chulay JD
Hum Gene Ther Clin Dev; 2017 Dec; 28(4):197-207. PubMed ID: 29020838
[TBL] [Abstract][Full Text] [Related]
12. Gene Therapy for Color Blindness.
Hassall MM; Barnard AR; MacLaren RE
Yale J Biol Med; 2017 Dec; 90(4):543-551. PubMed ID: 29259520
[TBL] [Abstract][Full Text] [Related]
13. Mouse Models of Achromatopsia in Addressing Temporal "Point of No Return" in Gene-Therapy.
Wang NK; Liu PK; Kong Y; Levi SR; Huang WC; Hsu CW; Wang HH; Chen N; Tseng YJ; Quinn PMJ; Tai MH; Lin CS; Tsang SH
Int J Mol Sci; 2021 Jul; 22(15):. PubMed ID: 34360834
[TBL] [Abstract][Full Text] [Related]
14. Loss of cone cyclic nucleotide-gated channel leads to alterations in light response modulating system and cellular stress response pathways: a gene expression profiling study.
Ma H; Thapa A; Morris LM; Michalakis S; Biel M; Frank MB; Bebak M; Ding XQ
Hum Mol Genet; 2013 Oct; 22(19):3906-19. PubMed ID: 23740940
[TBL] [Abstract][Full Text] [Related]
15. Restoration of cone vision in the CNGA3-/- mouse model of congenital complete lack of cone photoreceptor function.
Michalakis S; Mühlfriedel R; Tanimoto N; Krishnamoorthy V; Koch S; Fischer MD; Becirovic E; Bai L; Huber G; Beck SC; Fahl E; Büning H; Paquet-Durand F; Zong X; Gollisch T; Biel M; Seeliger MW
Mol Ther; 2010 Dec; 18(12):2057-63. PubMed ID: 20628362
[TBL] [Abstract][Full Text] [Related]
16. Genetics and Disease Expression in the CNGA3 Form of Achromatopsia: Steps on the Path to Gene Therapy.
Zelinger L; Cideciyan AV; Kohl S; Schwartz SB; Rosenmann A; Eli D; Sumaroka A; Roman AJ; Luo X; Brown C; Rosin B; Blumenfeld A; Wissinger B; Jacobson SG; Banin E; Sharon D
Ophthalmology; 2015 May; 122(5):997-1007. PubMed ID: 25616768
[TBL] [Abstract][Full Text] [Related]
17. Cortical Visual Mapping following Ocular Gene Augmentation Therapy for Achromatopsia.
McKyton A; Averbukh E; Marks Ohana D; Levin N; Banin E
J Neurosci; 2021 Sep; 41(35):7363-7371. PubMed ID: 34349002
[TBL] [Abstract][Full Text] [Related]
18. Gene therapy rescues cone function in congenital achromatopsia.
Komáromy AM; Alexander JJ; Rowlan JS; Garcia MM; Chiodo VA; Kaya A; Tanaka JC; Acland GM; Hauswirth WW; Aguirre GD
Hum Mol Genet; 2010 Jul; 19(13):2581-93. PubMed ID: 20378608
[TBL] [Abstract][Full Text] [Related]
19. A demonstration of cone function plasticity after gene therapy in achromatopsia.
Farahbakhsh M; Anderson EJ; Maimon-Mor RO; Rider A; Greenwood JA; Hirji N; Zaman S; Jones PR; Schwarzkopf DS; Rees G; Michaelides M; Dekker TM
Brain; 2022 Nov; 145(11):3803-3815. PubMed ID: 35998912
[TBL] [Abstract][Full Text] [Related]
20. Outer retinal transduction by AAV2-7m8 following intravitreal injection in a sheep model of CNGA3 achromatopsia.
Ross M; Obolensky A; Averbukh E; Desrosiers M; Ezra-Elia R; Honig H; Yamin E; Rosov A; Dvir H; Gootwine E; Banin E; Dalkara D; Ofri R
Gene Ther; 2022 Nov; 29(10-11):624-635. PubMed ID: 34853444
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]