BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

232 related articles for article (PubMed ID: 22525091)

  • 21. Gene therapy for murine mucopolysaccharidosis type VII.
    Sands MS; Wolfe JH; Birkenmeier EH; Barker JE; Vogler C; Sly WS; Okuyama T; Freeman B; Nicholes A; Muzyczka N; Chang PL; Axelrod HR
    Neuromuscul Disord; 1997 Jul; 7(5):352-60. PubMed ID: 9267850
    [TBL] [Abstract][Full Text] [Related]  

  • 22. Evaluation of AAV-mediated Gene Therapy for Central Nervous System Disease in Canine Mucopolysaccharidosis VII.
    Gurda BL; De Guilhem De Lataillade A; Bell P; Zhu Y; Yu H; Wang P; Bagel J; Vite CH; Sikora T; Hinderer C; Calcedo R; Yox AD; Steet RA; Ruane T; O'Donnell P; Gao G; Wilson JM; Casal M; Ponder KP; Haskins ME
    Mol Ther; 2016 Feb; 24(2):206-216. PubMed ID: 26447927
    [TBL] [Abstract][Full Text] [Related]  

  • 23. Recombinant adeno-associated virus-mediated correction of lysosomal storage within the central nervous system of the adult mucopolysaccharidosis type VII mouse.
    Sferra TJ; Qu G; McNeely D; Rennard R; Clark KR; Lo WD; Johnson PR
    Hum Gene Ther; 2000 Mar; 11(4):507-19. PubMed ID: 10724030
    [TBL] [Abstract][Full Text] [Related]  

  • 24. In vivo treatment of hemophilia A and mucopolysaccharidosis type VII using nonprimate lentiviral vectors.
    Stein CS; Kang Y; Sauter SL; Townsend K; Staber P; Derksen TA; Martins I; Qian J; Davidson BL; McCray PB
    Mol Ther; 2001 Jun; 3(6):850-6. PubMed ID: 11407898
    [TBL] [Abstract][Full Text] [Related]  

  • 25. Vestronidase alfa: Recombinant human β-glucuronidase as an enzyme replacement therapy for MPS VII.
    Cadaoas J; Boyle G; Jungles S; Cullen S; Vellard M; Grubb JH; Jurecka A; Sly W; Kakkis E
    Mol Genet Metab; 2020 May; 130(1):65-76. PubMed ID: 32192868
    [TBL] [Abstract][Full Text] [Related]  

  • 26. Enzyme replacement therapy for murine mucopolysaccharidosis type VII.
    Sands MS; Vogler C; Kyle JW; Grubb JH; Levy B; Galvin N; Sly WS; Birkenmeier EH
    J Clin Invest; 1994 Jun; 93(6):2324-31. PubMed ID: 8200966
    [TBL] [Abstract][Full Text] [Related]  

  • 27. Central nervous system delivery of helper-dependent canine adenovirus corrects neuropathology and behavior in mucopolysaccharidosis type VII mice.
    Ariza L; Giménez-Llort L; Cubizolle A; Pagès G; García-Lareu B; Serratrice N; Cots D; Thwaite R; Chillón M; Kremer EJ; Bosch A
    Hum Gene Ther; 2014 Mar; 25(3):199-211. PubMed ID: 24299455
    [TBL] [Abstract][Full Text] [Related]  

  • 28. Clinical response to persistent, low-level beta-glucuronidase expression in the murine model of mucopolysaccharidosis type VII.
    Donsante A; Levy B; Vogler C; Sands MS
    J Inherit Metab Dis; 2007 Apr; 30(2):227-38. PubMed ID: 17308887
    [TBL] [Abstract][Full Text] [Related]  

  • 29. Intracranial injection of recombinant adeno-associated virus improves cognitive function in a murine model of mucopolysaccharidosis type VII.
    Frisella WA; O'Connor LH; Vogler CA; Roberts M; Walkley S; Levy B; Daly TM; Sands MS
    Mol Ther; 2001 Mar; 3(3):351-8. PubMed ID: 11273777
    [TBL] [Abstract][Full Text] [Related]  

  • 30. Cloning of the canine beta-glucuronidase cDNA, mutation identification in canine MPS VII, and retroviral vector-mediated correction of MPS VII cells.
    Ray J; Bouvet A; DeSanto C; Fyfe JC; Xu D; Wolfe JH; Aguirre GD; Patterson DF; Haskins ME; Henthorn PS
    Genomics; 1998 Mar; 48(2):248-53. PubMed ID: 9521879
    [TBL] [Abstract][Full Text] [Related]  

  • 31. Transgene produces massive overexpression of human beta -glucuronidase in mice, lysosomal storage of enzyme, and strain-dependent tumors.
    Vogler C; Galvin N; Levy B; Grubb J; Jiang J; Zhou XY; Sly WS
    Proc Natl Acad Sci U S A; 2003 Mar; 100(5):2669-73. PubMed ID: 12591953
    [TBL] [Abstract][Full Text] [Related]  

  • 32. Cross-correction of beta-glucuronidase deficiency by retroviral vector-mediated gene transfer.
    Taylor RM; Wolfe JH
    Exp Cell Res; 1994 Oct; 214(2):606-13. PubMed ID: 7925654
    [TBL] [Abstract][Full Text] [Related]  

  • 33. Treatment of lysosomal storage disease in MPS VII mice using a recombinant adeno-associated virus.
    Watson GL; Sayles JN; Chen C; Elliger SS; Elliger CA; Raju NR; Kurtzman GJ; Podsakoff GM
    Gene Ther; 1998 Dec; 5(12):1642-9. PubMed ID: 10023443
    [TBL] [Abstract][Full Text] [Related]  

  • 34. Effect of neonatal gene therapy on lumbar spine disease in mucopolysaccharidosis VII dogs.
    Smith LJ; Martin JT; O'Donnell P; Wang P; Elliott DM; Haskins ME; Ponder KP
    Mol Genet Metab; 2012 Sep; 107(1-2):145-52. PubMed ID: 22510705
    [TBL] [Abstract][Full Text] [Related]  

  • 35. In utero fetal liver cell transplantation without toxic irradiation alleviates lysosomal storage in mice with mucopolysaccharidosis type VII.
    Barker JE; Deveau S; Lessard M; Hamblen N; Vogler C; Levy B
    Blood Cells Mol Dis; 2001; 27(5):861-73. PubMed ID: 11783949
    [TBL] [Abstract][Full Text] [Related]  

  • 36. The effect of neonatal gene therapy on skeletal manifestations in mucopolysaccharidosis VII dogs after a decade.
    Xing EM; Knox VW; O'Donnell PA; Sikura T; Liu Y; Wu S; Casal ML; Haskins ME; Ponder KP
    Mol Genet Metab; 2013 Jun; 109(2):183-93. PubMed ID: 23628461
    [TBL] [Abstract][Full Text] [Related]  

  • 37. Accumulation of abnormal amounts of glycosaminoglycans in murine mucopolysaccharidosis type VII neural progenitor cells does not alter the growth rate or efficiency of differentiation into neurons.
    Heuer GG; Skorupa AF; Prasad Alur RK; Jiang K; Wolfe JH
    Mol Cell Neurosci; 2001 Jan; 17(1):167-78. PubMed ID: 11161477
    [TBL] [Abstract][Full Text] [Related]  

  • 38. Decreased lysosomal storage in the adult MPS VII mouse brain in the vicinity of grafts of retroviral vector-corrected fibroblasts secreting high levels of beta-glucuronidase.
    Taylor RM; Wolfe JH
    Nat Med; 1997 Jul; 3(7):771-4. PubMed ID: 9212105
    [TBL] [Abstract][Full Text] [Related]  

  • 39. Genetic correction of the fetal brain increases the lifespan of mice with the severe multisystemic disease mucopolysaccharidosis type VII.
    Karolewski BA; Wolfe JH
    Mol Ther; 2006 Jul; 14(1):14-24. PubMed ID: 16624622
    [TBL] [Abstract][Full Text] [Related]  

  • 40. Reversal of pathology in the entire brain of mucopolysaccharidosis type VII mice after lentivirus-mediated gene transfer.
    Bosch A; Perret E; Desmaris N; Trono D; Heard JM
    Hum Gene Ther; 2000 May; 11(8):1139-50. PubMed ID: 10834616
    [TBL] [Abstract][Full Text] [Related]  

    [Previous]   [Next]    [New Search]
    of 12.