These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.


BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

293 related articles for article (PubMed ID: 22704480)

  • 1. Bone marrow transplantation increases efficacy of central nervous system-directed enzyme replacement therapy in the murine model of globoid cell leukodystrophy.
    Qin EY; Hawkins-Salsbury JA; Jiang X; Reddy AS; Farber NB; Ory DS; Sands MS
    Mol Genet Metab; 2012 Sep; 107(1-2):186-96. PubMed ID: 22704480
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Mechanism-based combination treatment dramatically increases therapeutic efficacy in murine globoid cell leukodystrophy.
    Hawkins-Salsbury JA; Shea L; Jiang X; Hunter DA; Guzman AM; Reddy AS; Qin EY; Li Y; Gray SJ; Ory DS; Sands MS
    J Neurosci; 2015 Apr; 35(16):6495-505. PubMed ID: 25904800
    [TBL] [Abstract][Full Text] [Related]  

  • 3. CNS-targeted AAV5 gene transfer results in global dispersal of vector and prevention of morphological and function deterioration in CNS of globoid cell leukodystrophy mouse model.
    Lin DS; Hsiao CD; Liau I; Lin SP; Chiang MF; Chuang CK; Wang TJ; Wu TY; Jian YR; Huang SF; Liu HL
    Mol Genet Metab; 2011 Aug; 103(4):367-77. PubMed ID: 21620749
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Bone marrow transplantation augments the effect of brain- and spinal cord-directed adeno-associated virus 2/5 gene therapy by altering inflammation in the murine model of globoid-cell leukodystrophy.
    Reddy AS; Kim JH; Hawkins-Salsbury JA; Macauley SL; Tracy ET; Vogler CA; Han X; Song SK; Wozniak DF; Fowler SC; Klein RS; Sands MS
    J Neurosci; 2011 Jul; 31(27):9945-57. PubMed ID: 21734286
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Enzyme replacement therapy of a novel humanized mouse model of globoid cell leukodystrophy.
    Matthes F; Andersson C; Stein A; Eistrup C; Fogh J; Gieselmann V; Wenger DA; Matzner U
    Exp Neurol; 2015 Sep; 271():36-45. PubMed ID: 25956830
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Central nervous system-directed AAV2/5-mediated gene therapy synergizes with bone marrow transplantation in the murine model of globoid-cell leukodystrophy.
    Lin D; Donsante A; Macauley S; Levy B; Vogler C; Sands MS
    Mol Ther; 2007 Jan; 15(1):44-52. PubMed ID: 17164774
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Intrathecal administration of AAV/GALC vectors in 10-11-day-old twitcher mice improves survival and is enhanced by bone marrow transplant.
    Karumuthil-Melethil S; Marshall MS; Heindel C; Jakubauskas B; Bongarzone ER; Gray SJ
    J Neurosci Res; 2016 Nov; 94(11):1138-51. PubMed ID: 27638599
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Transplantation of mouse embryonic stem cell-derived oligodendrocytes in the murine model of globoid cell leukodystrophy.
    Kuai XL; Ni RZ; Zhou GX; Mao ZB; Zhang JF; Yi N; Liu ZX; Shao N; Ni WK; Wang ZW
    Stem Cell Res Ther; 2015 Mar; 6(1):30. PubMed ID: 25888852
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Multipotent stromal cells alleviate inflammation, neuropathology, and symptoms associated with globoid cell leukodystrophy in the twitcher mouse.
    Scruggs BA; Zhang X; Bowles AC; Gold PA; Semon JA; Fisher-Perkins JM; Zhang S; Bonvillain RW; Myers L; Li SC; Kalueff AV; Bunnell BA
    Stem Cells; 2013 Aug; 31(8):1523-34. PubMed ID: 23606584
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Hematopoietic cell transplantation in murine globoid cell leukodystrophy (the twitcher mouse): effects on levels of galactosylceramidase, psychosine, and galactocerebrosides.
    Ichioka T; Kishimoto Y; Brennan S; Santos GW; Yeager AM
    Proc Natl Acad Sci U S A; 1987 Jun; 84(12):4259-63. PubMed ID: 2884662
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Mitigation of cerebellar neuropathy in globoid cell leukodystrophy mice by AAV-mediated gene therapy.
    Lin DS; Hsiao CD; Lee AY; Ho CS; Liu HL; Wang TJ; Jian YR; Hsu JC; Huang ZD; Lee TH; Chiang MF
    Gene; 2015 Oct; 571(1):81-90. PubMed ID: 26115766
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Characterization and application of a disease-cell model for a neurodegenerative lysosomal disease.
    Ribbens JJ; Moser AB; Hubbard WC; Bongarzone ER; Maegawa GH
    Mol Genet Metab; 2014 Feb; 111(2):172-83. PubMed ID: 24094551
    [TBL] [Abstract][Full Text] [Related]  

  • 13. β-Galactosylceramidase Deficiency Causes Upregulation of Long Pentraxin-3 in the Central Nervous System of Krabbe Patients and
    Coltrini D; Chandran AMK; Belleri M; Poliani PL; Cominelli M; Pagani F; Capra M; Calza S; Prioni S; Mauri L; Prinetti A; Kofler JK; Escolar ML; Presta M
    Int J Mol Sci; 2022 Aug; 23(16):. PubMed ID: 36012705
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Long-term Improvements in Lifespan and Pathology in CNS and PNS After BMT Plus One Intravenous Injection of AAVrh10-GALC in Twitcher Mice.
    Rafi MA; Rao HZ; Luzi P; Wenger DA
    Mol Ther; 2015 Nov; 23(11):1681-1690. PubMed ID: 26329589
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Central nervous system pathology progresses independently of KC and CXCR2 in globoid-cell leukodystrophy.
    Reddy AS; Patel JR; Vogler C; Klein RS; Sands MS
    PLoS One; 2014; 8(6):e64647. PubMed ID: 23755134
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Combined gene/cell therapies provide long-term and pervasive rescue of multiple pathological symptoms in a murine model of globoid cell leukodystrophy.
    Ricca A; Rufo N; Ungari S; Morena F; Martino S; Kulik W; Alberizzi V; Bolino A; Bianchi F; Del Carro U; Biffi A; Gritti A
    Hum Mol Genet; 2015 Jun; 24(12):3372-89. PubMed ID: 25749991
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Intravenous injection of AAVrh10-GALC after the neonatal period in twitcher mice results in significant expression in the central and peripheral nervous systems and improvement of clinical features.
    Rafi MA; Rao HZ; Luzi P; Luddi A; Curtis MT; Wenger DA
    Mol Genet Metab; 2015 Mar; 114(3):459-66. PubMed ID: 25533112
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Insights into the Pathogenesis and Treatment of Krabbe Disease.
    Bongarzone ER; Escolar ML; Gray SJ; Kafri T; Vite CH; Sands MS
    Pediatr Endocrinol Rev; 2016 Jun; 13 Suppl 1():689-96. PubMed ID: 27491217
    [TBL] [Abstract][Full Text] [Related]  

  • 19. AAVrh10 Gene Therapy Ameliorates Central and Peripheral Nervous System Disease in Canine Globoid Cell Leukodystrophy (Krabbe Disease).
    Bradbury AM; Rafi MA; Bagel JH; Brisson BK; Marshall MS; Pesayco Salvador J; Jiang X; Swain GP; Prociuk ML; ODonnell PA; Fitzgerald C; Ory DS; Bongarzone ER; Shelton GD; Wenger DA; Vite CH
    Hum Gene Ther; 2018 Jul; 29(7):785-801. PubMed ID: 29316812
    [TBL] [Abstract][Full Text] [Related]  

  • 20. The twitcher mouse. Central nervous system pathology after bone marrow transplantation.
    Suzuki K; Hoogerbrugge PM; Poorthuis BJ; Bekkum DW; Suzuki K
    Lab Invest; 1988 Mar; 58(3):302-9. PubMed ID: 3279262
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 15.