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3. Characteristics of clinical trials to support approval of orphan vs nonorphan drugs for cancer. Kesselheim AS; Myers JA; Avorn J JAMA; 2011 Jun; 305(22):2320-6. PubMed ID: 21642684 [TBL] [Abstract][Full Text] [Related]
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14. Regulators adopt more orphan drugs. Reardon S Nature; 2014 Apr; 508(7494):16-7. PubMed ID: 24695293 [No Abstract] [Full Text] [Related]
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