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6. Novel compound heterozygous GFPT1 mutations in a family with limb-girdle myasthenia with tubular aggregates. Luo HY; Zhao L; Mao CY; Yang ZH; Yang J; Wang YL; Niu HX; Liu YT; Shi CH; Xu YM Neuromuscul Disord; 2019 Jul; 29(7):549-553. PubMed ID: 31255525 [TBL] [Abstract][Full Text] [Related]
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